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Endothelial and neuronal engagement by AAV-BR1 gene therapy alleviates neurological symptoms and lipid deposition in a mouse model of Niemann-Pick type C2 Rasmussen, Charlotte Laurfelt Munch; Frederiksen, Signe Frost; Heegaard, Christian Wurtz; Thomsen, Maj Schneider; Hede, Eva; Laczek, Bartosz; Koerbelin, Jakob; Wustner, Daniel; Thomsen, Louiza Bohn; Schwaninger, Markus; Jensen, Ole N.; Moos, Torben; Burkhart, Annette 分享 收藏
The impact of acyl-CoA:cholesterol transferase (ACAT) inhibitors on biophysical membrane properties depends on membrane lipid composition To, Huong; Reinholdt, Peter; Bashawat, Mohammad; Luck, Meike; Lauritsen, Line; Akkerman, Vibeke; Kroiss, Matthias; Wustner, Daniel; Kongsted, Jacob; Mueller, Peter; Scheidt, Holger A. 分享 收藏
Stereospecific Properties and Intracellular Transport of Novel Intrinsically Fluorescent Neurosteroids Akkerman, Vibeke; Reinholdt, Peter; Schnoor-Madsen, Rasmus; Lauritsen, Line; Bader, Jad; Qian, Minxing; Xu, Yuanjiang; Akk, Gustav; Scheidt, Holger A.; Mueller, Peter; Covey, Douglas F.; Evers, Alex S.; Kongsted, Jacob; Wustner, Daniel 分享 收藏
Synthesis and Characterization of a Novel Intrinsically Fluorescent Analog of Cholesterol with Improved Photophysical Properties Lehmann, Max; Halder, Senjuti; Reinholdt, Peter; Bashawat, Mohammad; Scheidt, Holger A.; Leopold, Jenny; Schiller, Jurgen; di Prima, Duccio; Akkerman, Vibeke; Szomek, Maria; Lauritsen, Line; Kongsted, Jacob; Mueller, Peter; Wessig, Pablo; Wuestner, Daniel 分享 收藏
Structural and biochemical analysis of ligand binding in yeast Niemann-Pick type C1-related protein Nel, Lynette; Thaysen, Katja; Jamecna, Denisa; Olesen, Esben; Szomek, Maria; Langer, Julia; Frain, Kelly M.; Hoeglinger, Doris; Wustner, Daniel; Pedersen, Bjorn P. 分享 收藏
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Automated quantification of vacuole fusion and lipophagy in Saccharomyces cerevisiae from fluorescence and cryo-soft X-ray microscopy data using deep learning Egebjerg, Jacob Marcus; Szomek, Maria; Thaysen, Katja; Juhl, Alice Dupont; Kozakijevic, Suzana; Werner, Stephan; Pratsch, Christoph; Schneider, Gerd; Kapishnikov, Sergey; Ekman, Axel; Rottger, Richard; Wustner, Daniel 分享 收藏
Dynamic switching of transcriptional regulators between two distinct low-mobility chromatin states Wagh, Kaustubh; Stavreva, Diana A.; Jensen, Rikke A. M.; Paakinaho, Ville; Fettweis, Gregory; Schiltz, R. Louis; Wustner, Daniel; Mandrup, Susanne; Presman, Diego M.; Upadhyaya, Arpita; Hager, Gordon L. 分享 收藏
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Niemann Pick C2 protein enables cholesterol transfer from endo-lysosomes to the plasma membrane for efflux by shedding of extracellular vesicles Juhl, Alice Dupont; Lund, Frederik W.; Jensen, Maria Louise, V; Szomek, Maria; Heegaard, Christian W.; Guttmann, Peter; Werner, Stephan; McNally, James; Schneider, Gerd; Kapishnikov, Sergey; Wustner, Daniel 分享 收藏
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Design, Synthesis, and Evaluation of a Luminescent Cholesterol Mimic Work, Emily M.; Ferraudi, Guillermo; Kiefer, Luke; Liu, Gang; Grigalunas, Michael; Bhardwaj, Atul; Kaur, Rasmin; Dempsey, Janel M.; Wuestner, Daniel; Helquist, Paul; Wiest, Olaf 分享 收藏
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