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Equal outcomes after human leukocyte antigen-matched unrelated versus sibling donor transplants-Results of the AML SCT-BFM 2007 trial and consecutive 'real-world routine' Sauer, Martin G.; Lang, Peter J.; Albert, Michael H.; Bader, Peter; Eyrich, Matthias; Gruhn, Bernd; Klingebiel, Thomas; Mauz-korholz, Christine; Meisel, Roland; Muller, Ingo; Niemeyer, Charlotte M.; Peters, Christina; Burkhardt, Birgit; Reinhardt, Dirk; Sedlacek, Petr; Strahm, Brigitte; Woessmann, Wilhelm; Handgretinger, Rupert; Zimmermann, Martin; Borkhardt, Arndt 分享 收藏
Impact of minimal residual disease on the outcome of hematopoietic stem cell transplantation for childhood acute lymphoblastic leukemia within the FORUM trial FORUM试验中微量残留病对儿童急性淋巴细胞白血病造血干细胞移植结局的影响 Balduzzi, Adriana; Glogova, Evgenia; Peters, Christina; Sedlacek, Petr; Dalle, Jean-Hugues; Locatelli, Franco; Meisel, Roland; Burkhardt, Birgit; Buechner, Jochen; Wachowiak, Jacek; Bierings, Marc; Staciuk, Raquel; Graphakos, Stelios; Gungor, Tayfun; Yesilipek, Akif; Svec, Peter; Palma, Julia; Krivan, Gergely; Diaz-de-Heredia, Cristina; Limido, Francesca; Ansari, Marc; Kalwak, Krzysztof; Bader, Peter; Ifversen, Marianne 分享 收藏
Beyond TREC: Pivotal role of tandem TREC/KREC assay in Czech SCID NBS pilot programme 超越TREC:串联TREC/KREC检测在捷克SCID新生儿筛查试点项目中的关键作用 Bloomfield, Marketa; Hlavackova, Eva; Schneiderova, Helena; Turnovec, Marek; Tichy, Lukas; Cech, Zbynek; Chrastina, Petr; Dvorakova, Lenka; Peskova, Karolina; Formankova, Renata; Riha, Petr; Vlkova, Marcela; Bejdak, Petr; Havlisova, Magdalena; Fronkova, Eva; Kalina, Tomas; Bily, Viktor; Ricna, Dita; Grombirikova, Hana; Sedlacek, Petr; Litzman, Jiri; Freiberger, Tomas; Sediva, Anna; Klocperk, Adam 分享 收藏
NGS-MRD negativity in post-HSCT ALL spares unnecessary therapeutic interventions triggered by borderline qPCR results without an increase in relapse risk HSCT后ALL患者中NGS-MRD阴性可避免因临界qPCR结果触发的非必要治疗干预,且不增加复发风险。 Seferna, Krystof; Svaton, Michael; Rennerova, Andrea; Skotnicova, Aneta; Reznickova, Leona; Valova, Tatana; Sedlacek, Petr; Riha, Petr; Formankova, Renata; Keslova, Petra; Sramkova, Lucie; Stary, Jan; Zuna, Jan; Kolenova, Alexandra; Salek, Cyril; Trka, Jan; Fronkova, Eva 分享 收藏
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Anti-T-lymphocyte globulin exposure is associated with acute graft- versus-host disease and relapse in pediatric acute lymphoblastic leukemia patients undergoing hematopoietic stem cell transplantation: amultinational prospective study Oostenbrink, Lisa V. E.; von Asmuth, Erik G. J.; Jol-van der Zijde, Cornelia M.; Jansen-Hoogendijk, Anja M.; Vervat, Carly; Bredius, Robbert G. M.; van Tol, Maarten J. D.; Schilham, Marco W.; Sedlacek, Petr; Ifversen, Marianne; Balduzzi, Adriana; Bader, Peter; Peters, Christina; Moes, Dirk Jan A. R.; Lankester, Arjan C. 分享 收藏
Low rate of nonrelapse mortality in under-4-year-olds with ALL given chemotherapeutic conditioning for HSCT: a phase 3 FORUM study Bader, Peter; Poetschger, Ulrike; Dalle, Jean-Hugues; Moser, Laura M.; Balduzzi, Adriana; Ansari, Marc; Buechner, Jochen; Gungor, Tayfun; Ifversen, Marianne; Krivan, Gergely; Pichler, Herbert; Renard, Marleen; Staciuk, Raquel; Sedlacek, Petr; Stein, Jerry; Heusel, Jan Robert; Truong, Tony; Wachowiak, Jacek; Yesilipek, Akif; Locatelli, Franco; Peters, Christina 分享 收藏
Matched unrelated donor transplantation versus haploidentical transplantation with post-transplant cyclophosphamide in children with acute myeloid leukemia: a PDWP-EBMT study Ruggeri, Annalisa; Santoro, Nicole; Galimard, Jacques-Emmanuel; Kalwak, Krzysztof; Algeri, Mattia; Zubarovskaya, Ludmila; Czyzewski, Krzysztof; Skorobogatova, Elena; Sedlacek, Petr; Besley, Caroline; Balduzzi, Adriana; Bertrand, Yves; Peristeri, Julia; Fagioli, Franca; Ifversen, Mariane; Gozdzik, Jolanta; Peters, Christina; Versluijs, Birgitta; Biffi, Alessandra; Prete, Arcangelo; Faraci, Maura; Ghemlas, Ibrahim; Bodova, Ivana; Aleinikova, Olga; Dalissier, Arnaud; Rocha, Vanderson; Corbacioglu, Selim 分享 收藏
Management of children and adolescents with chronic myeloid leukemia in blast phase: International pediatric CML expert panel recommendations Sembill, Stephanie; Ampatzidou, Maria; Chaudhury, Sonali; Dworzak, Michael; Kalwak, Krzysztof; Karow, Axel; Kiani, Alexander; Krumbholz, Manuela; Luesink, Maaike; Naumann-Bartsch, Nora; De Moerloose, Barbara; Osborn, Michael; Schultz, Kirk R.; Sedlacek, Petr; Giona, Fiorina; Zwaan, Christian Michel; Shimada, Hiroyuki; Versluijs, Birgitta; Millot, Frederic; Hijiya, Nobuko; Suttorp, Meinolf; Metzler, Markus 分享 收藏
The Importance of New EBMT Criteria on the Diagnosis of Veno-Occlusive Liver Disease in Children Fussiova, Maria; Svec, Peter; Horakova, Julia; Sedlacek, Petr; Rohon, Peter; Celec, Peter; Bod'ova, Ivana; Adamcakova, Jaroslava; Sykora, Tomas; Dobsinska, Veronika; Pozdechova, Miroslava; Doczyova, Dominika; Vargova, Santia; Kolenova, Alexandra 分享 收藏
Prevalence of anemia at diagnosis of pediatric chronic myeloid leukemia and prognostic impact on the disease course 小儿慢性粒细胞白血病诊断中贫血的患病率及其对病程的预后影响 Delehaye, Fanny; Rouger, Jeremie; Brossier, David; Suttorp, Meinolf; Gunes, Adalet Meral; Sedlacek, Petr; Versluys, Birgitta; Li, Chi Kong; Kalwak, Krzysztof; Lausen, Birgitte; Srdjana, Culic; Dworzak, Michael; Hraskova, Andrea; De Moerloose, Barbara; Roula, Farah; Briant, Anais; Parienti, Jean-Jacques; Millot, Frederic 分享 收藏
Hematopoietic cell transplantation in severe combined immunodeficiency: The SCETIDE 2006-2014 European cohort 严重联合免疫缺陷的造血细胞移植: SCETIDE 2006 2014的欧洲队列 Lankester, Arjan C.; Neven, Benedicte; Mahlaoui, Nizar; von Asmuth, Erik G. J.; Courteille, Virginie; Alligon, Mikael; Albert, Michael H.; Serra, Isabelle Badell; Bader, Peter; Balashov, Dmitry; Beier, Rita; Bertrand, Yves; Blanche, Stephane; Bordon, Victoria; Bredius, Robbert G.; Cant, Andrew; Cavazzana, Marina; Diaz-de-Heredia, Cristina; Dogu, Figen; Ehlert, Karoline; Entz-Werle, Natacha; Fasth, Anders; Ferrua, Francesca; Ferster, Alina; Formankova, Renata; Friedrich, Wilhelm; Gonzalez-Vicent, Marta; Gozdzik, Jolanta; Gungor, Tayfun; Hoenig, Manfred; Ikinciogullari, Aydan; Kalwak, Krzysztof; Kansoy, Savas; Kupesiz, Alphan; Lanfranchi, Arnalda; Lindemans, Caroline A.; Meisel, Roland; Michel, Gerard; Miranda, Nuno A. A.; Moraleda, Jose; Moshous, Despina; Pichler, Herbert; Rao, Kanchan; Sedlacek, Petr; Slatter, Mary; Soncini, Elena; Speckmann, Carsten; Sundin, Mikael; Toren, Amos; Vettenranta, Kim; Worth, Austen; Yesilipek, Mehmet A.; Zecca, Marco; Porta, Fulvio; Schulz, Ansgar; Veys, Paul; Fischer, Alain; Gennery, Andrew R. 分享 收藏
Early-onset pulmonary and cutaneous vasculitis driven by constitutively active SRC-family kinase HCK Kanderova, Veronika; Svobodova, Tamara; Borna, Simon; Fejtkova, Martina; Martinu, Vendula; Paderova, Jana; Svaton, Michael; Kralova, Jarmila; Fronkova, Eva; Klocperk, Adam; Pruhova, Stepanka; Lee-Kirsch, Min Ae; Hornofova, Ludmila; Koblizek, Miroslav; Novak, Petr; Zimmermannova, Olga; Parackova, Zuzana; Sediva, Anna; Kalina, Tomas; Janda, Ales; Kayserova, Jana; Dvorakova, Marcela; Macek, Milan; Pohunek, Petr; Sedlacek, Petr; Poh, Ashleigh; Ernst, Matthias; Brdicka, Tomas; Hrusak, Ondrej; Lebl, Jan 分享 收藏
TLR8/TLR7 dysregulation due to a novel TLR8 mutation causes severe autoimmune hemolytic anemia and autoinflammation in identical twins Fejtkova, Martina; Sukova, Martina; Hlozkova, Katerina; Kramarzova, Karolina Skvarova; Rackova, Marketa; Jakubec, David; Bakardjieva, Marina; Bloomfield, Marketa; Klocperk, Adam; Parackova, Zuzana; Sediva, Anna; Aluri, Jahnavi; Novakova, Michaela; Kalina, Tomas; Fronkova, Eva; Hrusak, Ondrej; Malcova, Hana; Sedlacek, Petr; Liba, Zuzana; Kudr, Martin; Stary, Jan; Cooper, Megan A.; Svaton, Michael; Kanderova, Veronika 分享 收藏
Pregnancy and pregnancy outcomes after hematopoietic stem cell transplantation in childhood: a cross-sectional survey of the EBMT Pediatric Diseases Working Party Diesch-Furlanetto, T.; Rovo, A.; Galimard, J. E.; Szinnai, G.; Dalissier, A.; Sedlacek, P.; Bodova, I; Roussou, V. K.; Gibson, B. E.; Poire, X.; Fagioli, F.; Pichler, H.; Faraci, M.; Gumy-Pause, F. G.; Dalle, J. H.; Balduzzi, A.; Bader, P.; Corbacioglu, S. 分享 收藏