未登录Inhibitor development upon switching from plasma-derived to recombinant factor VIII in previously untreated patients with severe hemophilia A: the PUP-SWITCH study既往未接受治疗的重度A型血友病患者从血浆来源凝血因子VIII转换为重组凝血因子VIII时抑制物的产生:PUP-SWITCH研究
Miri, Syna; Rosendaal, Frits R.; Kavakli, Kaan; Eshghi, Peyman; Moghaddam, Soha Mohammadi; Scardo, Sara; Habibpanah, Behnaz; Elalfy, Mohsen; Halimeh, Susan; Nicolo, Gabriella; Gokcebay, Dilek; Ozbek, Namik; Celkan, Tiraje; Mohammadi, Ahmad; Karimi, Mehran; Shahsavani, Amin; Yilmaz, Baris; Albayrak, Canan; Gunes, Burcak; Kaya, Zuehre; Ay, Yilmaz; Akbayram, Sinan; Sarper, Nazan; Mannucci, Pier Mannuccio; Peyvandi, Flora
分享
收藏Predicting inhibitor development using a random peptide phage-display library approach in the SIPPET cohort
Hassan, Shermarke; Baselli, Guido; Mollica, Luca; Rossi, Riccardo L.; Chand, Himani; El-Beshlawy, Amal; Elalfy, Mohsen; Ramanan, Vijay; Eshghi, Peyman; Karimi, Mehran; Palla, Roberta; Rosendaal, Frits R.; Peyvandi, Flora
分享
收藏Efficacy and safety of early-start deferiprone in infants and young children with transfusion-dependent beta thalassemia: Evidence for iron shuttling to transferrin in a randomized, double-blind, placebo-controlled, clinical trial (START)
Elalfy, Mohsen S.; Hamdy, Mona; Adly, Amira; Ebeid, Fatma S. E.; Temin, Noemi Toiber; Rozova, Anna; Lee, David; Fradette, Caroline; Tricta, Fernando
分享
收藏Adolescents and young adults with newly diagnosed primary immune thrombocytopenia
Schifferli, Alexandra; Moulis, Guillaume; Godeau, Bertrand; Leblanc, Thierry; Aladjidi, Nathalie; Michel, Marc; Leverger, Guy; Elalfy, Mohsen; Grainger, John; Chitlur, Meera; Heiri, Andrea; Holzhauer, Susanne; le Gavrian, Gautier; Imbach, Paul; Kuhne, Thomas
分享
收藏Deferiprone for transfusional iron overload in sickle cell disease and other anemias: open-label study of up to 3 years
Elalfy, Mohsen S.; Hamdy, Mona; El-Beshlawy, Amal; Ebeid, Fatma S. E.; Badr, Mohamed; Kanter, Julie; Inusa, Baba; Adly, Amira A. M.; Williams, Suzan; Kilinc, Yurdanur; Lee, David; Fradette, Caroline; Rozova, Anna; Temin, Noemi Toiber; Tricta, Fernando; Kwiatkowski, Janet L.
分享
收藏
分享
收藏Deferiprone vs deferoxamine for transfusional iron overload in SCD and other anemias: a randomized, open-label noninferiority study
Kwiatkowski, Janet L.; Hamdy, Mona; El-Beshlawy, Amal; Ebeid, Fatma S. E.; Badr, Mohammed; Alshehri, Abdulrahman; Kanter, Julie; Inusa, Baba; Adly, Amira A. M.; Williams, Suzan; Kilinc, Yurdanur; Lee, David; Tricta, Fernando; Elalfy, Mohsen S.
分享
收藏
分享
收藏
分享
收藏
分享
收藏Performance of a clinical risk prediction model for inhibitor formation in severe haemophilia A
Hassan, Shermarke; Palla, Roberta; Valsecchi, Carla; Garagiola, Isabella; El-Beshlawy, Amal; Elalfy, Mohsen; Ramanan, Vijay; Eshghi, Peyman; Karimi, Mehran; Gouw, Samantha Claudia; Mannucci, Pier Mannuccio; Rosendaal, Frits Richard; Peyvandi, Flora
分享
收藏Intracranial hemorrhage in primary immune thrombocytopenia (ITP): 20 years' experience in pediatrics
Elalfy, Mohsen Saleh; Eltonbary, Khadiga Yehia Elsayed Mousa; El Ghamry, Islam R.; Elalfy, Omar; Wahid, Marwa; Badr, Mohamed; Hassan, Tamer; Mansour, Ahmed; Meabed, Mohamed; El-Hawy, Mahmoud; Youssry, Ilham; Abd Elhady, Marwa; Elshanshory, Mohamed; Elsayh, Khalid; Hassab, Hoda M.
分享
收藏Role of factor VIII-binding capacity of endogenous von Willebrand factor in the development of factor VIII inhibitors in patients with severe hemophilia A
Repesse, Yohann; Costa, Catherine; Palla, Roberta; Moshai, Elika Farrokhi; Borel-Derlon, Annie; D'Oiron, Roseline; Rothschild, Chantal; El-Beshlawy, Amal; Elalfy, Mohsen; Ramanan, Vijay; Eshghi, Peyman; Oldenburg, Johannes; Pavlova, Anna; Rosendaal, Frits R.; Peyvandi, Flora; Kaveri, Srinivas V.; Lacroix-Desmazes, Sebastien
分享
收藏Immunological role of CD4+CD28null T lymphocytes, natural killer cells, and interferon-gamma in pediatric patients with sickle cell disease: relation to disease severity and response to therapy
ElAlfy, Mohsen Saleh; Adly, Amira Abdel Moneam; Ebeid, Fatma Soliman ElSayed; Eissa, Deena Samir; Ismail, Eman Abdel Rahman; Mohammed, Yasser Hassan; Ahmed, Manar Elsayed; Saad, Aya Sayed
分享
收藏Renal iron deposition by magnetic resonance imaging in pediatric β-thalassemia major patients: Relation to renal biomarkers, total body iron and chelation therapy
ElAlfy, Mohsen Saleh; Elsherif, Nayera Hazaa Khalil; Ebeid, Fatma Soliman Elsayed; Ismail, Eman Abdel Rahman; Ahmed, Khaled Aboulfotouh; Darwish, Yasser Wagih; Ibrahim, Ahmed Samir; Elghamry, Islam Reda Farag; Shokrey, Nermeen Adel; Alajeil, Dunia Naser
分享
收藏A comparative prospective observational study of children and adults with immune thrombocytopenia: 2-year follow-up
Schifferli, Alexandra; Holbro, Andreas; Chitlur, Meera; Coslovsky, Michael; Imbach, Paul; Donato, Hugo; Elalfy, Mohsen; Graciela, Elena; Grainger, John; Holzhauer, Susanne; Riccheri, Cecilia; Rodeghiero, Francesco; Ruggeri, Marco; Tamary, Hannah; Uglova, Tatjana; Wu, Runhui; Kuehne, Thomas
分享
收藏
分享
收藏A Randomized Trial of Factor VIII and Neutralizing Antibodies in Hemophilia A
Peyvandi, F.; Mannucci, P. M.; Garagiola, I.; El-Beshlawy, A.; Elalfy, M.; Ramanan, V.; Eshghi, P.; Hanagavadi, S.; Varadarajan, R.; Karimi, M.; Manglani, M. V.; Ross, C.; Young, G.; Seth, T.; Apte, S.; Nayak, D. M.; Santagostino, E.; Mancuso, M. E.; Sandoval Gonzalez, A. C.; Mahlangu, J. N.; Bonanad Boix, S.; Cerqueira, M.; Ewing, N. P.; Male, C.; Owaidah, T.; Soto Arellano, V.; Kobrinsky, N. L.; Majumdar, S.; Perez Garrido, R.; Sachdeva, A.; Simpson, M.; Thomas, M.; Zanon, E.; Antmen, B.; Kavakli, K.; Manco-Johnson, M. J.; Martinez, M.; Marzouka, E.; Mazzucconi, M. G.; Neme, D.; Palomo Bravo, A.; Paredes Aguilera, R.; Prezotti, A.; Schmitt, K.; Wicklund, B. M.; Zulfikar, B.; Rosendaal, F. R.
分享
收藏
分享
收藏Sustained improvements in myocardial T2*over 2 years in severely iron-overloaded patients with beta thalassemia major treated with deferasirox or deferoxamine
Pennell, Dudley J.; Porter, John B.; Piga, Antonio; Lai, Yong-Rong; El-Beshlawy, Amal; Elalfy, Mohsen; Yesilipek, Akif; Kilinc, Yurdanur; Habr, Dany; Musallam, Khaled M.; Shen, Junwu; Aydinok, Yesim
分享
收藏