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An RNA Editing Approach for the Treatment of Alpha-1 Antitrypsin Deficiency (AATD) Monian, Prashant; Caracta, Cynthia; Shivalila, Chikdu; Lu, Genliang; Bowman, Keith; Byrne, Michael; Xie, Lanyie; Desai, Jigar; Ghosh, Anamitra; Kawamoto, Tomomi; Kandasamy, Pachamuthu; Lamattina, Anthony; Liu, Fangjun; Paik, Ik-Hyeon; Rheinhardt, Jeanette; Shimizu, Mamoru; Singh, Kuldeep; Yang, Hailin; Narayanan, Padma; Hu, Xiao Shelley; Giangrande, Paloma; Vargeese, Chandra 分享 收藏
Rational design of base, sugar and backbone modifications improves ADAR-mediated RNA editing Lu, Genliang; Shivalila, Chikdu; Monian, Prashant; Yu, Hui; Harding, Ian; Briem, Stearne; Byrne, Michael; Faraone, Alyse; Friend, Stephen; Huth, Olivia; Iwamoto, Naoki; Kawamoto, Tomomi; Kumarasamy, Jayakanthan; Lamattina, Anthony; Longo, Kenneth; McCarthy, Leah; McGlynn, Andrew; Molski, Allison; Pan, Qianli; Pu, Tom; Purcell-Estabrook, Erin; Rossi, Jeff; Standley, Stephany; Thomas, Carina; Walen, Alexandra; Yang, Hailin; Kandasamy, Pachamuthu; Vargeese, Chandra 分享 收藏
Impact of stereopure chimeric backbone chemistries on the potency and durability of gene silencing by RNA interference Liu, Wei; Iwamoto, Naoki; Marappan, Subramanian; Luu, Khoa; Tripathi, Snehlata; Purcell-Estabrook, Erin; Shelke, Juili Dilip; Shah, Himali; Lamattina, Anthony; Pan, Qianli; Schrand, Brett; Favaloro, Frank; Bedekar, Mugdha; Chatterjee, Arindom; Desai, Jigar; Kawamoto, Tomomi; Lu, Genliang; Metterville, Jake; Samaraweera, Milinda; Prakasha, Priyanka Shiva; Yang, Hailin; Yin, Yuan; Yu, Hui; Giangrande, Paloma H.; Byrne, Michael; Kandasamy, Pachamuthu; Vargeese, Chandra 分享 收藏
Endogenous ADAR-mediated RNA editing in non-human primates using stereopure chemically modified oligonucleotides Monian, Prashant; Shivalila, Chikdu; Lu, Genliang; Shimizu, Mamoru; Boulay, David; Bussow, Karley; Byrne, Michael; Bezigian, Adam; Chatterjee, Arindom; Chew, David; Desai, Jigar; Favaloro, Frank; Godfrey, Jack; Hoss, Andrew; Iwamoto, Naoki; Kawamoto, Tomomi; Kumarasamy, Jayakanthan; Lamattina, Anthony; Lindsey, Amber; Liu, Fangjun; Looby, Richard; Marappan, Subramanian; Metterville, Jake; Murphy, Ronelle; Rossi, Jeff; Pu, Tom; Bhattarai, Bijay; Standley, Stephany; Tripathi, Snehlata; Yang, Hailin; Yin, Yuan; Yu, Hui; Zhou, Cong; Apponi, Luciano H.; Kandasamy, Pachamuthu; Vargeese, Chandra 分享 收藏
Impact of guanidine-containing backbone linkages on stereopure antisense oligonucleotides in the CNS Kandasamy, Pachamuthu; Liu, Yuanjing; Aduda, Vincent; Akare, Sandheep; Alam, Rowshon; Andreucci, Amy; Boulay, David; Bowman, Keith; Byrne, Michael; Cannon, Megan; Chivatakarn, Onanong; Shelke, Juili Dilip; Iwamoto, Naoki; Kawamoto, Tomomi; Kumarasamy, Jayakanthan; Lamore, Sarah; Lemaitre, Muriel; Lin, Xuena; Longo, Kenneth; Looby, Richard; Marappan, Subramanian; Metterville, Jake; Mohapatra, Susovan; Newman, Bridget; Paik, Ik-Hyeon; Patil, Saurabh; Purcell-Estabrook, Erin; Shimizu, Mamoru; Shum, Pochi; Standley, Stephany; Taborn, Kris; Tripathi, Snehlata; Yang, Hailin; Yin, Yuan; Zhao, Xiansi; Dale, Elena; Vargeese, Chandra 分享 收藏
Control of backbone chemistry and chirality boost oligonucleotide splice switching activity Kandasamy, Pachamuthu; McClorey, Graham; Shimizu, Mamoru; Kothari, Nayantara; Alam, Rowshon; Iwamoto, Naoki; Kumarasamy, Jayakanthan; Bommineni, Gopal R.; Bezigian, Adam; Chivatakarn, Onanong; Butler, David C. D.; Byrne, Michael; Chwalenia, Katarzyna; Davies, Kay E.; Desai, Jigar; Shelke, Juili Dilip; Durbin, Ann F.; Ellerington, Ruth; Edwards, Ben; Godfrey, Jack; Hoss, Andrew; Liu, Fangjun; Longo, Kenneth; Lu, Genliang; Marappan, Subramanian; Oieni, Jacopo; Paik, Ik-Hyeon; Estabrook, Erin Purcell; Shivalila, Chikdu; Tischbein, Maeve; Kawamoto, Tomomi; Rinaldi, Carlo; Rajao-Saraiva, Joana; Tripathi, Snehlata; Yang, Hailin; Yin, Yuan; Zhao, Xiansi; Zhou, Cong; Zhang, Jason; Apponi, Luciano; Wood, Matthew J. A.; Vargeese, Chandra 分享 收藏
Variant-selective stereopure oligonucleotides protect against pathologies associated with C9orf72-repeat expansion in preclinical models Liu, Yuanjing; Dodart, Jean-Cosme; Tran, Helene; Berkovitch, Shaunna; Braun, Maurine; Byrne, Michael; Durbin, Ann F.; Hu, Xiao Shelley; Iwamoto, Naoki; Jang, Hyun Gyung; Kandasamy, Pachamuthu; Liu, Fangjun; Longo, Kenneth; Ruschel, Jorg; Shelke, Juili; Yang, Hailin; Yin, Yuan; Donner, Amy; Zhong, Zhong; Vargeese, Chandra; Brown, Robert H., Jr. 分享 收藏
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Inflammation modulates human HDL composition and function in vivo Moya, Margarita de la Llera; McGillicuddy, Fiona C.; Hinkle, Christine C.; Byrne, Michael; Joshi, Michelle R.; Vihn Nguyen; Tabita-Martinez, Jennifer; Wolfe, Megan L.; Badellino, Karen; Pruscino, Leticia; Mehta, Nehal N.; Asztalos, Bela F.; Reilly, Muredach P. 分享 收藏
POPULATION BASED SURVEILLANCE FOR CERVICAL INTRAEPITHELIAL NEOPLASIA GRADE 3 AND ADENOCARCINOMA IN SITU IN THREE CENTRAL CANCER REGISTRIES, USA 2009 Flagg, E. W.; Datta, S. Deblina; Lyu, C.; Nagaraja, J.; Copeland, G.; Silva, W.; Peters, E.; Cole, L.; Tucker, T.; Byrne, M. J.; Unger, E. R.; Saraiya, M.; Weinstock, H. 分享 收藏
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Early prediction of response to chemotherapy and survival in malignant pleural mesothelioma using a novel semiautomated 3-dimensional volume-based analysis of serial 18F-FDG PET scans Francis, Roslyn J.; Byrne, Michael J.; van der Schaaf, Agatha A.; Boucek, Jan A.; Nowak, Anna K.; Phillips, Michael; Price, Richard; Patrikeos, Andrew R.; Musk, A. William; Millward, Michael J. 分享 收藏
Phase II study of IV vinflunine in patients with chemotherapy native metastatic malignant melanoma Olver, I. N.; Byrne, M. J.; Walpole, E.; Vorobiof, D.; Jacobs, C.; Maart, K.; Hewitt, S.; McAdam, G.; Pouget, J. C.; Pinel, M. C. 分享 收藏
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