未登录 Subretinal injection in the USH1CR31*pig model leads to chorioretinal atrophy that limits evaluation of efficacy of an AAV-mediated gene therapy 在美国H1CR31*pig模型中,视网膜下注射导致脉络膜视网膜萎缩,限制了AAV介导的基因治疗效果的评估 Nyshchuk, Ruslan; Klein, Joshua; Seitz, Immanuel P.; Peters, Tobias; Mai, Matthias; Ardan, Taras; Drutovic, Saskia; Bohuslavova, Bozena Levinska; Juhas, Stefan; Juhasova, Jana; Tutuncu, Yesim; Nemesh, Yaroslav; Reifferscheid, Lienne M.; DeMott, Kathryn Post; Klein, Jennifer J.; Nagel-Wolfrum, Kerstin; Klymiuk, Nikolai; Winslow, Ashley R.; Motlik, Jan; Ellederova, Zdenka; Fischer, M. Dominik; Wolfrum, Uwe 分享 收藏
Subretinal Injection Volume Correlates to Persistent Outer Retinal Thinning in the Pig Eye Seitz, Immanuel P.; Nyshchuk, Ruslan; Ellederova, Zdenka; Ardan, Taras; Juhasova, Jana; Nemesh, Yaroslav; Juhas, Stefan; Drutovic, Saskia; Susskind, Daniela; Schnichels, Sven; Motlik, Jan; Klymiuk, Nikolai; Wolfrum, Uwe; DeMott, Kathryn Post; Klein, Jennifer J.; Winslow, Ashley; Fischer, M. Dominik 分享 收藏
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Delivery of Human iPSC-Derived RPE Cells in Healthy Minipig Retina Results in Interaction Between Photoreceptors and Transplanted Cells 向健康迷你猪视网膜内输送人诱导多能干细胞来源的RPE细胞会导致感光细胞与移植细胞之间的相互作用 Brymová, AM; Rodriguez-Jimenez, FJ; Konrad, A; Nemesh, Y; Thottappali, MA; Artero-Castro, A; Nyshchuk, R; Kolesnikova, A; Müller, B; Studenovska, H; Juhasova, J; Juhas, S; Valekova, I; Lukovic, D; Aleman, C; Ardan, T; Drutovic, S; Motlik, J; Ellederova, Z; Stranák, Z; Veith, M; Lytvynchuk, L; Sharma, R; Bharti, K; Petrovski, G; Jendelova, P; Stieger, K; Erceg, S 分享 收藏
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Safety of Human USH1C Transgene Expression Following Subretinal Injection in Wild-Type Pigs Kiraly, Peter; Klein, Joshua; Seitz, Immanuel P.; Reichel, Felix F.; Peters, Tobias; Ardan, Taras; Juhasova, Jana; Juhas, Stefan; Ellederova, Zdenka; Nemesh, Yaroslav; Nyshchuk, Ruslan; Klymiuk, Nikolai; Nagel-Wolfrum, Kerstin; Winslow, Ashley R.; Wolfrum, Uwe; Motlik, Jan; Fischer, M. Dominik 分享 收藏
Human iPSC-derived RPE cells implantation into minipig eye - Six weeks follow-up study 人源诱导多能干细胞(iPSC)来源的RPE细胞移植入微型猪眼 - 六周随访研究 Ardan, T; Erceg, S; Brymová, A; Studenovska, H; Mueller, B; Stieger, K; Petrovski, G; Lytvynchuk, L; Stranák, Z; Veith, M; Juhás, S; Juhasova, J; Nemesh, Y; Ellederová, Z; Motlik, J 分享 收藏
Optimizing Subretinal Bleb Formation for Visual Streak Involvement in a Porcine Model for Retinal Gene Therapy 优化视网膜下滤过泡形成以使视觉条纹参与视网膜基因治疗的猪模型 Seitz, Immanuel P.; Peters, Tobias; Reichel, Felix; Baehr, Andrea; Auch, Hanna; Motlik, Jan; Ardan, Taras; Juhasova, Jana; Nemesh, Yaroslav; Juhas, Stefan; Klymiuk, Nikolai; Fischer, Manuel Dominik 分享 收藏
Human iPSC-derived RPE cells implantation into minipig eye: Two weeks follow-up study Ardan, Taras; Erceg, Slaven; Artero-Castro, Ana; Studenovska, Hana; Mueller, Brigitte; Stieger, Knut; Lytvynchuk, Lyubomyr; Stranak, Zbynek; Ellederova, Zdenka; Juhas, Stefan; Motlik, Jan; Petrovski, Goran 分享 收藏
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In vitro and in vivo evaluation of genetically corrected RPE cells for autologous cell therapy of hereditary retinal dystrophies Rodriguez-Jimenez, F. J.; Brymova, A.; Mueller, B.; Stieger, K.; Jendelova, P.; Ardan, T.; Studenovska, H.; Lytvynchuk, L.; Stranak, Z.; Ellederova, Z.; Juhas, J.; Motlik, J.; Petrovski, G.; Erceg, Lukovic D. 分享 收藏
Progress In Stem Cells Based Replacement Therapy for Retinal Pigment Epithelium: In Vitro Differentiation to In Vivo Delivery 基于干细胞的视网膜色素上皮替代疗法的研究进展: 体外分化为体内递送 Gupta, Santosh; Lytvynchuk, Lyubomyr; Ardan, Taras; Studenovska, Hana; Sharma, Ruchi; Faura, Georgina; Eide, Lars; Verma, Rama Shanker; Znaor, Ljubo; Erceg, Slaven; Stieger, Knut; Motlik, Jan; Petrovski, Goran; Bharti, Kapil 分享 收藏
Retinal Pigment Epithelium Cell Development: Extrapolating Basic Biology to Stem Cell Research Gupta, Santosh; Lytvynchuk, Lyubomyr; Ardan, Taras; Studenovska, Hana; Faura, Georgina; Eide, Lars; Znaor, Ljubo; Erceg, Slaven; Stieger, Knut; Motlik, Jan; Bharti, Kapil; Petrovski, Goran 分享 收藏
Nanofibrous scaffolds with ex vivo cultured human iPSC- derived RPE cells for transplantation into porcine eyes Ardan, Taras; Erceg, Slaven; Artero-Castro, Ana; Studenovska, Hana; Mueller, Brigitte; Stieger, Knut; Popelka, Stepan; Lytvynchuk, Lyubomyr; Stranak, Zbynek; Tichotova, Lucie 分享 收藏
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MINIPIG MODELS OF HUNTINGTON'S DISEASE AT PIGMOD CENTER Vochozkova, Petra Runa; Auch, Hannah; Nemesh, Kateryna; Nyguen, The Duong; Sekac, David; Kamenna, Eva; Baxa, Monika; Klima, Jiri; Ardan, Taras; Juhas, Stefan; Levinska, Bozena; Juhasova, Jana; Keller, Jiri; Klempir, Jiri; Motlik, Jan; Klymiuk, Nikolai; Ellederova, Zdenka 分享 收藏
Subretinal Implantation of Human Primary RPE Cells Cultured on Nanofibrous Membranes in Minipigs Lytvynchuk, Lyubomyr; Ebbert, Annabelle; Studenovska, Hana; Nagymihaly, Richard; Josifovska, Natasha; Rais, David; Popelka, Stepan; Tichotova, Lucie; Nemesh, Yaroslav; Cizkova, Jana; Juhasova, Jana; Juhas, Stefan; Jendelova, Pavla; Franekova, Janka; Kozak, Igor; Erceg, Slaven; Stranak, Zbynek; Mueller, Brigitte; Ellederova, Zdenka; Motlik, Jan; Stieger, Knut; Ardan, Taras; Petrovski, Goran 分享 收藏
Early disruption of photoreceptor cell architecture and loss of vision in a humanized pig model of usher syndromes Grotz, Sophia; Schaefer, Jessica; Wunderlich, Kirsten A.; Ellederova, Zdenka; Auch, Hannah; Baehr, Andrea; Runa-Vochozkova, Petra; Fadl, Janet; Arnold, Vanessa; Ardan, Taras; Veith, Miroslav; Santamaria, Gianluca; Dhom, Georg; Hitzl, Wolfgang; Kessler, Barbara; Eckardt, Christian; Klein, Joshua; Brymova, Anna; Linnert, Joshua; Kurome, Mayuko; Zakharchenko, Valeri; Fischer, Andrea; Blutke, Andreas; Doering, Anna; Suchankova, Stepanka; Popelar, Jiri; Rodriguez-Bocanegra, Eduardo; Dlugaiczyk, Julia; Straka, Hans; May-Simera, Helen; Wang, Weiwei; Laugwitz, Karl-Ludwig; Vandenberghe, Luk H.; Wolf, Eckhard; Nagel-Wolfrum, Kerstin; Peters, Tobias; Motlik, Jan; Fischer, M. Dominik; Wolfrum, Uwe; Klymiuk, Nikolai 分享 收藏
Advantages of nanofibrous membranes for culturing of primary RPE cells compared to commercial scaffolds Tichotova, Lucie; Studenovska, Hana; Petrovski, Goran; Popelka, Stepan; Nemesh, Yaroslav; Sedlackova, Miroslava; Drutovic, Saskia; Rohiwal, Sonali; Jendelova, Pavla; Erceg, Slaven; Brymova, Anna; Artero-Castro, Ana; Lytvynchuk, Lyubomyr; Stranak, Zbynek; Ellederova, Zdenka; Motlik, Jan; Ardan, Taras 分享 收藏