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Boost and Increased Antibody Breadth Following a Second Dose of PARVAX for SARS-CoV-2 in Mice and Nonhuman Primates Bhatt, Urja; Herate, Cecile; Estelien, Reynette; Relouzat, Francis; Dereuddre-Bosquet, Nathalie; Maciorowski, Dawid; Diop, Cheikh; Couto, Emma; Staiti, Jillian; Cavarelli, Mariangela; Bossevot, Laetitia; Sconosciuti, Quentin; Bouchard, Page; Le Grand, Roger; Vandenberghe, Luk H.; Zabaleta, Nerea 分享 收藏
Subretinal gene therapy delays vision loss in a Bardet-Biedl Syndrome type 10 mouse model 视网膜下基因治疗可延迟bardet-biedl综合征10型小鼠模型的视力丧失 Hsu, Ying; Bhattarai, Sajag; Thompson, Jacob M.; Mahoney, Angela; Thomas, Jacintha; Mayer, Sara K.; Datta, Poppy; Garrison, Janelle; Searby, Charles C.; Vandenberghe, Luk H.; Seo, Seongjin; Eld, Val C. Shef fi; V. Drack, Arlene 分享 收藏
Efficient in vivo genome editing prevents hypertrophic cardiomyopathy in mice Reichart, Daniel; Newby, Gregory A.; Wakimoto, Hiroko; Lun, Mingyue; Gorham, Joshua M.; Curran, Justin J.; Raguram, Aditya; DeLaughter, Daniel M.; Conner, David A.; Marsiglia, Julia D. C.; Kohli, Sajeev; Chmatal, Lukas; Page, David C.; Zabaleta, Nerea; Vandenberghe, Luk; Liu, David R.; Seidman, Jonathan G.; Seidman, Christine 分享 收藏
Ancestral library identifies conserved reprogrammable liver motif on AAV capsid Zinn, Eric; Unzu, Carmen; Schmit, Pauline F.; Turunen, Heikki T.; Zabaleta, Nerea; Sanmiguel, Julio; Fieldsend, Allegra; Bhatt, Urja; Diop, Cheikh; Merkel, Erin; Gurrala, Rakesh; Peacker, Bryan; Rios, Christopher; Messemer, Kathleen; Santos, Jennifer; Estelien, Reynette; Andres-Mateos, Eva; Wagers, Amy J.; Tipper, Christopher; Vandenberghe, Luk H. 分享 收藏
Gene therapy with a synthetic adeno-associated viral vector improves audiovestibular phenotypes in Pjvk- mutant mice Lu, Ying-Chang; Tsai, Yi-Hsiu; Chan, Yen-Huei; Hu, Chin-Ju; Huang, Chun-Ying; Xiao, Ru; Hsu, Chuan-Jen; Vandenberghe, Luk H.; Wu, Chen-Chi; Cheng, Yen-Fu 分享 收藏
Durable immunogenicity, adaptation to emerging variants, and low-dose efficacy of an AAV-based COVID-19 vaccine platform in macaques Zabaleta, Nerea; Bhatt, Urja; Herate, Cecile; Maisonnasse, Pauline; Sanmiguel, Julio; Diop, Cheikh; Castore, Sofia; Estelien, Reynette; Li, Dan; Dereuddre-Bosquet, Nathalie; Cavarelli, Mariangela; Gallouet, Anne-Sophie; Pascal, Quentin; Naninck, Thibaut; Kahlaoui, Nidhal; Lemaitre, Julien; Relouzat, Francis; Ronzitti, Giuseppe; Thibaut, Hendrik Jan; Montomoli, Emanuele; Wilson, James M.; Le Grand, Roger; Vandenberghe, Luk H. 分享 收藏
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Choice of vector and surgical approach enables efficient cochlear gene transfer in nonhuman primate Andres-Mateos, Eva; Landegger, Lukas D.; Unzu, Carmen; Phillips, Jean; Lin, Brian M.; Dewyer, Nicholas A.; Sanmiguel, Julio; Nicolaou, Fotini; Valero, Michelle D.; Bourdeu, Kathrin, I; Sewell, William F.; Beiler, Rudolph J.; McKenna, Michael J.; Stankovic, Konstantina M.; Vandenberghe, Luk H. 分享 收藏
Early disruption of photoreceptor cell architecture and loss of vision in a humanized pig model of usher syndromes Grotz, Sophia; Schaefer, Jessica; Wunderlich, Kirsten A.; Ellederova, Zdenka; Auch, Hannah; Baehr, Andrea; Runa-Vochozkova, Petra; Fadl, Janet; Arnold, Vanessa; Ardan, Taras; Veith, Miroslav; Santamaria, Gianluca; Dhom, Georg; Hitzl, Wolfgang; Kessler, Barbara; Eckardt, Christian; Klein, Joshua; Brymova, Anna; Linnert, Joshua; Kurome, Mayuko; Zakharchenko, Valeri; Fischer, Andrea; Blutke, Andreas; Doering, Anna; Suchankova, Stepanka; Popelar, Jiri; Rodriguez-Bocanegra, Eduardo; Dlugaiczyk, Julia; Straka, Hans; May-Simera, Helen; Wang, Weiwei; Laugwitz, Karl-Ludwig; Vandenberghe, Luk H.; Wolf, Eckhard; Nagel-Wolfrum, Kerstin; Peters, Tobias; Motlik, Jan; Fischer, M. Dominik; Wolfrum, Uwe; Klymiuk, Nikolai 分享 收藏
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Selective retinal ganglion cell loss and optic neuropathy in a humanized mouse model of familial dysautonomia Chekuri, Anil; Logan, Emily M.; Krauson, Aram J.; Salani, Monica; Ackerman, Sophie; Kirchner, Emily G.; Bolduc, Jessica M.; Wang, Xia; Dietrich, Paula; Dragatsis, Ioannis; Vandenberghe, Luk H.; Slaugenhaupt, Susan A.; Morini, Elisabetta 分享 收藏
MCOLN1 gene therapy corrects neurologic dysfunction in the mouse model of mucolipidosis IV DeRosa, Samantha; Salani, Monica; Smith, Sierra; Sangster, Madison; Miller-Browne, Victoria; Wassmer, Sarah; Xiao, Ru; Vandenberghe, Luk; Slaugenhaupt, Susan; Misko, Albert; Grishchuk, Yulia 分享 收藏
Voices of biotech research Annabi, Nasim; Baker, Matthew; Boettiger, Alistair; Chakraborty, Debojyoti; Chen, Yvonne; Corbett, Kizzmekia S.; Correia, Bruno; Dahlman, James; de Oliveira, Tulio; Ertuerk, Ali; Yanik, Mehmet Fatih; Henaff, Elizabeth; Huch, Meritxell; Iliev, Iliyan D.; Jacobs, Thomas; Junca, Howard; Keung, Albert; Kolodkin-Gal, Ilana; Krishnaswamy, Smita; Lancaster, Madeline; Macosko, Evan; Martinez-Nunez, Mario Alberto; Miura, Kyoko; Molloy, Jenny; Cruz, Andres Ochoa; Platt, Randall J.; Posey, Avery D., Jr.; Shao, Huilin; Simunovic, Mijo; Slavov, Nikolai; Takebe, Takanori; Vandenberghe, Luk H.; Varshney, Rajeev K.; Wang, Jianbin 分享 收藏
Homologous Recombination Offers Advantages over Transposition-Based Systems to Generate Recombinant Baculovirus for Adeno-Associated Viral Vector Production 同源重组提供了优于基于转座的系统的优势，以产生用于腺相关病毒载体生产的重组杆状病毒 Jacob, Aurelien; Brun, Laurie; Jimenez Gil, Paloma; Menard, Lucie; Bouzelha, Mohammed; Broucque, Frederic; Roblin, Aline; Vandenberghe, Luk H.; Adjali, Oumeya; Robin, Cecile; Francois, Achille; Blouin, Veronique; Penaud-Budloo, Magalie; Ayuso, Eduard 分享 收藏
GPR108 Is a Highly Conserved AAV Entry Factor Dudek, Amanda M.; Zabaleta, Nerea; Zinn, Eric; Pillay, Sirika; Zengel, James; Porter, Caryn; Franceschini, Jennifer Santos; Estelien, Reynette; Carette, Jan E.; Zhou, Guo Ling; Vandenberghe, Luk H. 分享 收藏
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In Situ Modification of Tissue Stem and Progenitor Cell Genomes Goldstein, Jill M.; Tabebordbar, Mohammadsharif; Zhu, Kexian; Wang, Leo D.; Messemer, Kathleen A.; Peacker, Bryan; Kakhki, Sara Ashrafi; Gonzalez-Celeiro, Meryem; Shwartz, Yulia; Cheng, Jason K. W.; Xiao, Ru; Barungi, Trisha; Albright, Charles; Hsu, Ya-Chieh; Vandenberghe, Luk H.; Wagers, Amy J. 分享 收藏
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