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T

Thierry VandenDriessche

Vrije Universiteit Brussel
H指数:54
被引数:1.0万

个人简介

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教育背景

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工作经历

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荣誉奖项

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Long-Term Functional Correction of Pompe Disease and Increased α-Glucosidase Expression after Gene Therapy with Novel Combinations of Muscle-Targeted Transcriptional Cis-Regulatory Elements

应用新型肌肉靶向转录顺式调控元件组合进行基因治疗后，庞贝病长期功能纠正和α-葡萄糖苷酶表达增加

gene therapy
IF4
2025-07-180
PRE
Quang Hong Pham; Venkata Anudeep Bheemsetty; Phuong Anh Nguyen; Ermira Samara-Kuko; Fangye Gao; Marinee K. Chuah; Thierry VandenDriessche
A myotropic AAV vector combined with skeletal muscle cis-regulatory elements improve glycogen clearance in mouse models of Pompe disease

一种肌动性AAV载体与骨骼肌顺式调控元件相结合，可改善庞贝病小鼠模型的糖原清除。

MOLECULAR THERAPY METHODS & CLINICAL DEVELOPMENT
IF4.7
2025-06-010
OAAI
P. Sellier; F. Collaud; Y. Krimi Benchekroun; V. Jimenez; X. Leon; N. Daniele; Q.H. Pham; J. El Andari; T. VandenDriessche; M.K. Chuah; D. Grimm; F. Bosch; F. Mingozzi; G. Ronzitti
Semirational bioengineering of AAV vectors with increased potency and specificity for systemic gene therapy of muscle disorders
SCIENCE ADVANCES
IF12.5
2022-09-2331
OAAI
El Andari, Jihad; Renaud-Gabardos, Edith; Tulalamba, Warut; Weinmann, Jonas; Mangin, Louise; Pham, Quang Hong; Hille, Susanne; Bennett, Antonette; Attebi, Esther; Bourges, Emanuele; Leborgne, Christian; Guerchet, Nicolas; Fakhiri, Julia; Kraemer, Chiara; Wiedtke, Ellen; McKenna, Robert; Guianvarc'h, Laurence; Toueille, Magali; Ronzitti, Giuseppe; Hebben, Matthias; Mingozzi, Federico; VandenDriessche, Thierry; Agbandje-McKenna, Mavis; Mueller, Oliver J.; Chuah, Marinee K.; Buj-Bello, Ana; Grimm, Dirk
Identification of a myotropic AAV by massively parallel in vivo evaluation of barcoded capsid variants

通过大规模平行体内评估条形码衣壳变体来鉴定肌性AAV

NATURE COMMUNICATIONS
IF15.7
2020-10-28151
OAAI
Weinmann, Jonas; Weis, Sabrina; Sippel, Josefine; Tulalamba, Warut; Remes, Anca; El Andari, Jihad; Herrmann, Anne-Kathrin; Pham, Quang H.; Borowski, Christopher; Hille, Susanne; Schoenberger, Tanja; Frey, Norbert; Lenter, Martin; VandenDriessche, Thierry; Mueller, Oliver J.; Chuah, Marinee K.; Lamla, Thorsten; Grimm, Dirk
Towards a global multidisciplinary consensus framework on haemophilia gene therapy: Report of the 2nd World Federation of Haemophilia Gene Therapy Round Table

关于血友病基因治疗的全球多学科共识框架: 第二届世界血友病基因治疗联合会圆桌会议的报告

HAEMOPHILIA
IF3
2020-03-2316
PREAI
Pierce, Glenn F.; Pasi, K. John; Coffin, Donna; Kaczmarek, Radoslaw; Lillicrap, David; Mahlangu, Johnny; Rottellini, Dawn; Sannie, Thomas; Srivastava, Alok; VandenDriessche, Thierry; Weill, Alain
Efficient CRISPR/Cas9-mediated editing of trinucleotide repeat expansion in myotonic dystrophy patient-derived iPS and myogenic cells
NUCLEIC ACIDS RESEARCH
IF13.1
2018-06-2772
OAAI
Dastidar, Sumitava; Ardui, Simon; Singh, Kshitiz; Majumdar, Debanjana; Nair, Nisha; Fu, Yanfang; Reyon, Deepak; Samara, Ermira; Gerli, Mattia F. M.; Klein, Arnaud F.; De Schrijver, Wito; Tipanee, Jaitip; Seneca, Sara; Tulalamba, Warut; Wang, Hui; Chai, Yoke Chin; Veld, Peter In't; Furling, Denis; Tedesco, Francesco Saverio; Vermeesch, Joris R.; Joung, J. Keith; Chuah, Marinee K.; VandenDriessche, Thierry

研究方向

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M
Marinee Chuah
H 指数:53论文数:220被引数:8,064
E
Ermira Samara-Kuko
H 指数:11论文数:37被引数:1,547
N
Nisha Nair
H 指数:19论文数:65被引数:1,338
A
Abel Acosta‐Sanchez
H 指数:10论文数:28被引数:1,880
M
Mariana Loperfido
H 指数:8论文数:25被引数:772
J
Janka Mátrai
H 指数:14论文数:56被引数:2,200
W
Warut Tulalamba
H 指数:11论文数:32被引数:788
D
David Lillicrap
H 指数:66论文数:512被引数:1.5万
M
Maurilio Sampaolesi
H 指数:51论文数:356被引数:1.2万
M
Mario Di Matteo
H 指数:19论文数:66被引数:2,512