未登录 A critical analysis on ENaC inhibitors, unravelling molecular medicinal insights and promising research roadmap in the treatment of cystic fibrosis 对ENaC抑制剂的批判性分析,揭示分子药物学见解和治疗囊性纤维化研究的可行路线图 Lo Mascolo, Fabiana; Lipani, Alessandra; Giuffrida, Stefano; Barreca, Marilia; Bivacqua, Roberta; Spano, Virginia; Raimondi, Maria Valeria; Montalbano, Alessandra; Borrelli, Anna; Venturini, Arianna; Guidone, Daniela; Genovese, Michele; Galietta, Luis J. V.; Barraja, Paola 分享 收藏
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Esc peptides and derivatives potentiate the activity of CFTR with gating defects and display antipseudomonal activity in cystic fibrosis-like lung disease Esc肽及其衍生物能够增强具有门控缺陷的CFTR的活性,并在类囊性纤维化肺病中显示出抗铜绿假单胞菌活性。 Ferrera, Loretta; Cappiello, Floriana; Venturini, Arianna; Lu, Hexin; Casciaro, Bruno; Cappella, Giacomo; Bontempi, Giulio; Corrente, Alessandra; Strippoli, Raffaele; Zara, Federico; Di, Y. Peter; Galietta, Luis J. V.; Mori, Mattia; Mangoni, Maria Luisa 分享 收藏
Functional rescue of F508del-CFTR through revertant mutations introduced by CRISPR base editing 通过CRISPR碱基编辑引入的返突变对F508del-CFTR的功能拯救 Carrozzo, Irene; Maule, Giulia; Gentile, Carmelo; Umbach, Alessandro; Ciciani, Matteo; Guidone, Daniela; De Santis, Martina; Petris, Gianluca; Galietta, Luis Juan Vicente; Arosio, Daniele; Cereseto, Anna 分享 收藏
Identification of 6,9-dihydro-5H-pyrrolo[3,2-h]quinazolines as a new class of F508del-CFTR correctors for the treatment of cystic fibrosis Barreca, Marilia; Renda, Mario; Spano, Virginia; Montalbano, Alessandra; Raimondi, Maria Valeria; Giuffrida, Stefano; Bivacqua, Roberta; Bandiera, Tiziano; Galietta, Luis J. V.; Barraja, Paola 分享 收藏
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Functional restoration of a CFTR splicing mutation through RNA delivery of CRISPR adenine base editor Amistadi, Simone; Maule, Giulia; Ciciani, Matteo; Ensinck, Marjolein M.; De Keersmaecker, Liesbeth; Ramalho, Anabela S.; Guidone, Daniela; Buccirossi, Martina; Galietta, Luis J. V.; Carlon, Marianne S.; Cereseto, Anna 分享 收藏
Novel tricyclic pyrrolo-quinolines as pharmacological correctors of the mutant CFTR chloride channel Renda, Mario; Barreca, Marilia; Borrelli, Anna; Spano, Virginia; Montalbano, Alessandra; Raimondi, Maria Valeria; Bivacqua, Roberta; Musante, Ilaria; Scudieri, Paolo; Guidone, Daniela; Buccirossi, Martina; Genovese, Michele; Venturini, Arianna; Bandiera, Tiziano; Barraja, Paola; Galietta, Luis J. V. 分享 收藏
Rescue by elexacaf tor-tezacaf tor-ivacaf tor of the G1244E cystic fibrosis mutation's stability and gating defects are dependent on cell background G1244E囊性纤维化突变的稳定性和门控缺陷依赖于细胞背景 Tomati, Valeria; Costa, Stefano; Capurro, Valeria; Pesce, Emanuela; Pastorino, Cristina; Lena, Mariateresa; Sondo, Elvira; Di Duca, Marco; Cresta, Federico; Cristadoro, Simona; Zara, Federico; Galietta, Luis J. V.; Bocciardi, Renata; Castellani, Carlo; Lucanto, Maria Cristina; Pedemonte, Nicoletta 分享 收藏
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Airway surface hyperviscosity and defective mucociliary transport by IL-17/TNF-? are corrected by ?-adrenergic stimulus br Guidone, Daniela; Buccirossi, Martina; Scudieri, Paolo; Genovese, Michele; Sarnataro, Sergio; De Cegli, Rossella; Cresta, Federico; Terlizzi, Vito; Planelles, Gabrielle; Crambert, Gilles; Sermet, Isabelle; Galietta, Luis J. V. 分享 收藏
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Esc peptides as novel potentiators of defective cystic fibrosis transmembrane conductance regulator: an unprecedented property of antimicrobial peptides Ferrera, Loretta; Cappiello, Floriana; Loffredo, Maria Rosa; Puglisi, Elena; Casciaro, Bruno; Botta, Bruno; Galietta, Luis J., V; Mori, Mattia; Mangoni, Maria Luisa 分享 收藏