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Long-Term Safety and Tolerability of Beremagene Geperpavec-svdt (B-VEC) in an Open-Label Extension Study of Patients with Dystrophic Epidermolysis Bullosa 贝雷玛基因·格佩尔帕韦西-svdt(B-VEC)在营养不良性大疱性表皮松解症患者开放标签扩展研究中的长期安全性与耐受性 Marinkovich, MP; Paller, AS; Guide, SV; Gonzalez, ME; Lucky, AW; Bagci, IS; Agostini, B; Fitzgerald, K; Chen, SJ; Chen, HB; Conner, MM; Krishnan, SM 分享 收藏
Repurposing an epithelial sodium channel inhibitor as a therapy for murine and human skin inflammation Winge, Marten C. G.; Nasrallah, Mazen; Jackrazi, Leandra V.; Guo, Konnie Q.; Fuhriman, Jessica M.; Szafran, Rebecca; Ramanathan, Muthukumar; Gurevich, Irina; Nguyen, Ngon T.; Siprashvili, Zurab; Inayathullah, Mohammed; Rajadas, Jayakumar; Porter, Douglas F.; Khavari, Paul A.; Butte, Atul J.; Marinkovich, M. Peter 分享 收藏
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Functional genotype-phenotype associations in recessive dystrophic epidermolysis bullosa 隐性营养不良性大疱性表皮松解症的功能基因型-表型关联 So, Jodi Y.; Nazaroff, Jaron; Yenamandra, Vamsi K.; Gorell, Emily S.; Harris, Nicki; Fulchand, Shivali; Eid, Edward; Dolorito, John A.; Marinkovich, M. Peter; Tang, Jean Y. 分享 收藏
Anti-NC16A IgA from Patients with Linear IgA Bullous Dermatosis Induce Neutrophil-Dependent Subepidermal Blistering in Mice Jing, Ke; Jordan, Tyler J. M.; Li, Ning; Burette, Susan; Yang, Baoqi; Marinkovich, M. Peter; Diaz, Luis A.; Googe, Paul; Thomas, Nancy E.; Feng, Suying; Liu, Zhi 分享 收藏
Cell volume expansion and local contractility drive collective invasion of the basement membrane in breast cancer Chang, Julie; Saraswathibhatla, Aashrith; Song, Zhaoqiang; Varma, Sushama; Sanchez, Colline; Alyafei, Naomi Hassan Kahtan; Indana, Dhiraj; Slyman, Raleigh; Srivastava, Sucheta; Liu, Katherine; Bassik, Michael C.; Marinkovich, M. Peter; Hodgson, Louis; Shenoy, Vivek; West, Robert B.; Chaudhuri, Ovijit 分享 收藏
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Trial of Beremagene Geperpavec (B-VEC) for Dystrophic Epidermolysis Bullosa Guide, Shireen V. V.; Gonzalez, Mercedes E. E.; Bagci, I. Sinem; Agostini, Brittani; Chen, Hubert; Feeney, Gloria; Steimer, Molly; Kapadia, Binoy; Sridhar, Kunju; Sanchez, Lori Quesada; Gonzalez, Franshesca; Van Ligten, Matthew; Parry, Trevor J. J.; Chitra, Surya; Kammerman, Lisa A. A.; Krishnan, Suma; Marinkovich, M. Peter 分享 收藏
Long-term safety and efficacy of gene-corrected autologous keratinocyte grafts for recessive dystrophic epidermolysis bullosa 基因校正的自体角质形成细胞移植治疗隐性营养不良性大疱性表皮松解症的长期安全性和有效性 So, Jodi Y.; Nazaroff, Jaron; Iwummadu, Chinonso, V; Harris, Nicki; Gorell, Emily S.; Fulchand, Shivali; Bailey, Irene; McCarthy, Daniel; Siprashvili, Zurab; Marinkovich, M. Peter; Tang, Jean Y.; Chiou, Albert S. 分享 收藏
In vivo topical gene therapy for recessive dystrophic epidermolysis bullosa: a phase 1 and 2 trial Gurevich, Irina; Agarwal, Pooja; Zhang, PeiPei; Dolorito, John A.; Oliver, Stacie; Liu, Henry; Reitze, Nicholas; Sarma, Nikhil; Bagci, Isin Sinem; Sridhar, Kunju; Kakarla, Visesha; Yenamandra, Vamsi K.; O'Malley, Mark; Prisco, Marco; Tufa, Sara F.; Keene, Douglas R.; South, Andrew P.; Krishnan, Suma M.; Marinkovich, M. Peter 分享 收藏
Classification of 2 distinct wound types in recessive dystrophic epidermolysis bullosa: A retrospective and cohort natural history study Solis, Daniel C.; Teng, Claudia; Gorell, Emily S.; Barriga, Melissa; Nazaroff, Jaron; Li, Shufeng; Lu, Ying; Bruckner, Anna; Marinkovich, M. Peter; Tang, Jean Y. 分享 收藏
Patient-reported outcomes and quality of life in recessive dystrophic epidermolysis bullosa: A global cross-sectional survey Eng, Victor A.; Solis, Daniel C.; Gorell, Emily S.; Choi, Sara; Nazaroff, Jaron; Li, Shufeng; de Souza, Mark P.; Murrell, Dedee F.; Marinkovich, M. Peter; Tang, Jean Y. 分享 收藏
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QR-313, an Antisense Oligonucleotide, Shows Therapeutic Efficacy for Treatment of Dominant and Recessive Dystrophic Epidermolysis Bullosa: A Preclinical Study Bornert, Olivier; Hogervorst, Marieke; Nauroy, Pauline; Bischof, Johannes; Swildens, Jim; Athanasiou, Ioannis; Tufa, Sara F.; Keene, Douglas R.; Kiritsi, Dimitra; Hainzl, Stefan; Murauer, Eva M.; Marinkovich, M. Peter; Platenburg, Gerard; Hausser, Ingrid; Wally, Verena; Ritsema, Tita; Koller, Ulrich; Haisma, Elisabeth M.; Nystroem, Alexander 分享 收藏
Multidisciplinary care of epidermolysis bullosa during the COVID-19 pandemic-Consensus: Recommendations by an international panel of experts Murrell, Dedee F.; Lucky, Anne W.; Salas-Alanis, Julio C.; Woodley, David T.; Palisson, Francis; Natsuga, Ken; Nikolic, Milos; Ramirez-Quizon, Mae; Paller, Amy S.; Lara-Corrales, Irene; Barzegar, Mohammadreza Amir; Sprecher, Eli; Has, Cristina; Laimer, Martin; Bruckner, Anna L.; Bilgic, Asli; Nanda, Arti; Purvis, Diana; Hovnanian, Alain; Murat-Susic, Slobodna; Bauer, Johannes; Kern, Johannes S.; Bodemer, Christine; Martin, Linda K.; Mellerio, Jemima; Kowaleski, Cezary; Robertson, Susan J.; Bruckner-Tuderman, Leena; Pope, Elena; Marinkovich, M. Peter; Tang, Jean Y.; Su, John; Uitto, Jouni; Eichenfield, Lawrence F.; Teng, Joyce; Koh, Mark Jean Aan; Lee, Sang Eun; Phuong Khuu; Rishel, Heather I.; Sommerlund, Mette; Wiss, Karen; Hsu, Chao-Kai; Chiu, Tor Wo; Martinez, Anna E. 分享 收藏