Laure Caccavelli

centre national de la recherche scientifique (cnrs)

H指数:21

被引数:8,064

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Hydroxychloroquine sulfate: A novel treatment for lipin-1 deficiency?

BIOMEDICINE & PHARMACOTHERAPY

IF7.5

2023-07-014

OAAI

Bi-allelic loss-of-function OBSCN variants predispose individuals to severe recurrent rhabdomyolysis

BRAIN

IF11.7

2021-12-249

Cabrera-Serrano, Macarena; Caccavelli, Laure; Savarese, Marco; Vihola, Anna; Jokela, Manu; Johari, Mridul; Capiod, Thierry; Madrange, Marine; Bugiardini, Enrico; Brady, Stefen; Quinlivan, Rosaline; Merve, Ashirwad; Scalco, Renata; Hilton-Jones, David; Houlden, Henry; Aydin, Halil Ibrahim; Ceylaner, Serdar; Drewes, Sarah; Vockley, Jerry; Taylor, Rhonda L.; Folland, Chiara; Kelly, Aasta; Goullee, Hayley; Ylikallio, Emil; Auranen, Mari; Tyynismaa, Henna; Udd, Bjarne; Forrest, Alistair R. R.; Davis, Mark R.; Bratkovic, Drago; Manton, Nicholas; Robertson, Thomas; O'Gorman, Cullen; McCombe, Pamela; Laing, Nigel G.; Phillips, Liza; de Lonlay, Pascale; Ravenscroft, Gianina

Successful in utero stem cell transplantation in X-linked severe combined immunodeficiency

BLOOD ADVANCES

IF7.1

2019-01-2511

OAAI

Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia

输血依赖性 β-地中海贫血患者的基因治疗

NEW ENGLAND JOURNAL OF MEDICINE

IF78.5

2018-04-19539

OAAI

Thompson, A. A.; Walters, M. C.; Kwiatkowski, J.; Rasko, J. E. J.; Ribeil, J. -A.; Hongeng, S.; Magrin, E.; Schiller, G. J.; Payen, E.; Semeraro, M.; Moshous, D.; Lefrere, F.; Puy, H.; Bourget, P.; Magnani, A.; Caccavelli, L.; Diana, J. -S.; Suarez, F.; Monpoux, F.; Brousse, V.; Poirot, C.; Brouzes, C.; Meritet, J. -F.; Pondarre, C.; Beuzard, Y.; Chretien, S.; Lefebvre, T.; Teachey, D. T.; Anurathapan, U.; Ho, P. J.; von Kalle, C.; Kletzel, M.; Vichinsky, E.; Soni, S.; Veres, G.; Negre, O.; Ross, R. W.; Davidson, D.; Petrusich, A.; Sandler, L.; Asmal, M.; Hermine, O.; De Montalembert, M.; Hacein-Bey-Abina, S.; Blanche, S.; Leboulch, P.; Cavazzana, M.

Gene Therapy in a Patient with Sickle Cell Disease

镰状细胞病患者的基因治疗

NEW ENGLAND JOURNAL OF MEDICINE

IF78.5

2017-03-02559

OAAI

Ribeil, Jean-Antoine; Hacein-Bey-Abina, Salima; Payen, Emmanuel; Magnani, Alessandra; Semeraro, Michaela; Magrin, Elisa; Caccavelli, Laure; Neven, Benedicte; Bourget, Philippe; El Nemer, Wassim; Bartolucci, Pablo; Weber, Leslie; Puy, Herve; Meritet, Jean-Francois; Grevent, David; Beuzard, Yves; Chretien, Stany; Lefebvre, Thibaud; Ross, Robert W.; Negre, Olivier; Veres, Gabor; Sandler, Laura; Soni, Sandeep; de Montalembert, Mariane; Blanche, Stephane; Leboulch, Philippe; Cavazzana, Marina

The Content of the More Immature Hematopoietic Stem Cells (HSCs) Is Dependent from the Underlying Genetic Diseases: Consequence on Transduction Efficiencies

MOLECULAR THERAPY

IF12

2016-05-011

OAAI

Mixed Chimerism After Allogeneic Hematopoietic Stem Cell Transplantation in Sickle Cell Disease: Preliminary Results on Peripheral Blood Sorted Subpopulations and Erythroid Progenitors

MOLECULAR THERAPY

IF12

2016-05-010

OAAI

Production of Gene Corrected T Cell Precursors for Therapy of SCID X1

MOLECULAR THERAPY

IF12

2016-05-010

OAAI

Exploring the Human Hematopoietic Hierarchy Through Retroviral Integration Sites Tracking in the Wiskott Aldrich Syndrome Gene Therapy Trial

MOLECULAR THERAPY

IF12

2016-05-010

OAAI

Preserving CD4+T-Cells Phenotype and Function Upon Ex Vivo Lentiviral Transduction

MOLECULAR THERAPY

IF12

2016-05-010

OAAI

Outcomes Following Gene Therapy in Patients With Severe Wiskott-Aldrich Syndrome

JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION

IF55

2015-04-21309

OAAI

Abina, Salima Hacein-Bey; Gaspar, H. Bobby; Blondeau, Johanna; Caccavelli, Laure; Charrier, Sabine; Buckland, Karen; Picard, Capucine; Six, Emmanuelle; Himoudi, Nourredine; Gilmour, Kimberly; McNicol, Anne-Marie; Hara, Havinder; Xu-Bayford, Jinhua; Rivat, Christine; Touzot, Fabien; Mavilio, Fulvio; Lim, Annick; Treluyer, Jean-Marc; Heritier, Sebastien; Lefrere, Francois; Magalon, Jeremy; Pengue-Koyi, Isabelle; Honnet, Geraldine; Blanche, Stephane; Sherman, Eric A.; Male, Frances; Berry, Charles; Malani, Nirav; Bushman, Frederic D.; Fischer, Alain; Thrasher, Adrian J.; Galy, Anne; Cavazzana, Marina

A Modified γ-Retrovirus Vector for X-Linked Severe Combined Immunodeficiency

NEW ENGLAND JOURNAL OF MEDICINE

IF78.5

2014-10-09328

OAAI

Hacein-Bey-Abina, S.; Pai, S. -Y.; Gaspar, H. B.; Armant, M.; Berry, C. C.; Blanche, S.; Bleesing, J.; Blondeau, J.; de Boer, H.; Buckland, K. F.; Caccavelli, L.; Cros, G.; De Oliveira, S.; Fernandez, K. S.; Guo, D.; Harris, C. E.; Hopkins, G.; Lehmann, L. E.; Lim, A.; London, W. B.; van der Loo, J. C. M.; Malani, N.; Male, F.; Malik, P.; Marinovic, M. A.; McNicol, A. -M.; Moshous, D.; Neven, B.; Oleastro, M.; Picard, C.; Ritz, J.; Rivat, C.; Schambach, A.; Shaw, K. L.; Sherman, E. A.; Silberstein, L. E.; Six, E.; Touzot, F.; Tsytsykova, A.; Xu-Bayford, J.; Baum, C.; Bushman, F. D.; Fischer, A.; Kohn, D. B.; Filipovich, A. H.; Notarangelo, L. D.; Cavazzana, M.; Williams, D. A.; Thrasher, A. J.

Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1

JOURNAL OF CLINICAL INVESTIGATION

IF13.6

2008-09-021.6K

OAAI

Hacein-Bey-Abina, Salima; Garrigue, Alexandrine; Wang, Gary P.; Soulier, Jean; Lim, Annick; Morillon, Estelle; Clappier, Emmanuelle; Caccavelli, Laure; Delabesse, Eric; Beldjord, Kheira; Asnafi, Vahid; Macintyre, Elizabeth; Dal Cortivo, Liliane; Radford, Isabelle; Brousse, Nicole; Sigaux, Francois; Moshous, Despina; Hauer, Julia; Borkhardt, Arndt; Belohradsky, Bernd H.; Wintergerst, Uwe; Velez, Maria C.; Leiva, Lily; Sorensen, Ricardo; Wulffraat, Nicolas; Blanche, Stephane; Bushman, Frederic D.; Fischer, Alain; Cavazzana-Calvo, Marina

Alteration of G alpha subunits mRNA levels in bromocriptine resistant prolactinomas

溴隐亭耐药的泌乳素瘤中G α 亚基mRNA水平的变化

JOURNAL OF NEUROENDOCRINOLOGY

IF4.1

2003-10-3155

PREAI

Regulatory CD8+ T cells control neonatal tolerance to a Th2-mediated autoimmunity

JOURNAL OF IMMUNOLOGY

IF3.4

2003-03-0143

OAAI

Laure Caccavelli

个人简介

教育背景

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