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Liver disease and transplantation in telomere biology disorders: An international multicenter cohort Wang, YunZu Michele; Kaj-Carbaidwala, Batul; Lane, Adam; Agarwal, Suneet; Beier, Fabian; Bertuch, Alison; Borovsky, Kristin A.; Brennan, Steven K.; Calado, Rodrigo T.; Catto, Luiz Fernando B.; Dufour, Carlo; Ebens, Christen L.; Fioredda, Francesca; Giri, Neelam; Gloude, Nicholas; Goldman, Frederick; Hertel, Paula M.; Himes, Ryan; Keel, Sioban B.; Koura, Divya T.; Kratz, Christian P.; Kulkarni, Sakil; Liou, Iris; Nakano, Taizo A.; Nastasio, Silvia; Niewisch, Marena R.; Penrice, Daniel D.; Sasa, Ghadir S.; Savage, Sharon A.; Simonetto, Douglas A.; Ziegler, David S.; Miethke, Alexander G.; Myers, Kasiani C. 分享 收藏
Infection risk in patients with autoimmune cytopenias and immune dysregulation treated with mycophenolate mofetil and sirolimus 霉酚酸酯和西罗莫司治疗自身免疫性血细胞减少和免疫失调患者的感染风险 Comella, Mattia; Palmisani, Elena; Mariani, Marcello; Dell'Orso, Gianluca; Licciardello, Maria; Giarratana, Maria Carla; Arcuri, Luca; Pestarino, Sara; Grossi, Alice; Lanciotti, Marina; Brucci, Giorgia; Guardo, Daniela; Russo, Giovanna; Dufour, Carlo; Fioredda, Francesca; Castagnola, Elio; Miano, Maurizio 分享 收藏
Late-onset and long-lasting neutropenias in the young: A new entity anticipating immune-dysregulation disorders Fioredda, F.; Beccaria, A.; Casartelli, P.; Turrini, E.; Contratto, C.; Giarratana, M. C.; Bagnasco, F.; Saettini, F.; Pillon, M.; Marzollo, A.; Zanardi, S.; Civino, A.; Onofrillo, D.; Lanciotti, M.; Ceccherini, I.; Grossi, A.; Coviello, D.; Terranova, P.; Lupia, M.; Del Borrello, G.; Uva, P.; Cangelosi, D.; Cavalca, G.; Miano, M.; Dufour, C. 分享 收藏
The long-term efficacy and safety of nilotinib in pediatric patients with CML: a 5-year update of the DIALOG study Hijiya, Nobuko; Maschan, Alexey; Rizzari, Carmelo; Shimada, Hiroyuki; Dufour, Carlo; Goto, Hiroaki; Kang, Hyoung Jin; Guinipero, Terri; Karakas, Zeynep; Bautista, Francisco; Ducassou, Stephane; Yoo, Keon Hee; Zwaan, Christian Michel; Millot, Frederic; Patterson, Briana C.; Samis, Jill; Izquierdo, Miguel; Titorenko, Ksenia; Li, Sai; Sosothikul, Darintr 分享 收藏
The role of androgen therapy in acquired aplastic anemia and other bone marrow failure syndromes Nassani, Momen; Fakih, Riad El; Passweg, Jakob; Cesaro, Simone; Alzahrani, Hazzaa; Alahmari, Ali; Bonfim, Carmem; Iftikhar, Raheel; Albeihany, Amal; Halkes, Constantijn; Ahmed, Syed Osman; Dufour, Carlo; Aljurf, Mahmoud 分享 收藏
The European Guidelines on Diagnosis and Management of Neutropenia in Adults and Children: A Consensus Between the European Hematology Association and the EuNet-INNOCHRON COST Action Fioredda, Francesca; Skokowa, Julia; Tamary, Hannah; Spanoudakis, Michail; Farruggia, Piero; Almeida, Antonio; Guardo, Daniela; Hoglund, Petter; Newburger, Peter E.; Palmblad, Jan; Touw, Ivo P.; Zeidler, Cornelia; Warren, Alan J.; Dale, David C.; Welte, Karl; Dufour, Carlo; Papadaki, Helen A. 分享 收藏
Graft-versus-host disease and relapse/rejection-free survival after allogeneic transplantation for idiopathic severe aplastic anemia: a comprehensive analysis from the SAAWP of the EBMT Devillier, Raynier; Eikema, Dirk-Jan; Dufour, Carlo; Aljurf, Mahmoud; Wu, Depei; Maschan, Alexei; Kulagin, Alexander; Halkes, Constantijn J. M.; Collin, Matthew; Snowden, John; Renard, Cecile; Ganser, Arnold; Sykora, Karl-Walter; Gibson, Brenda E.; Maertens, Johan; Itala-Remes, Maija; Corti, Paola; Cornelissen, Jan; Bornhaeuser, Martin; Colorado Araujo, Mercedes; Ozdogu, Hakan; Risitano, Antonio; Socie, Gerard; de latour, Regis Peffault 分享 收藏
Autoimmune Lymphoproliferative Syndrome (ALPS) Disease and ALPS Phenotype: Are They Two Distinct Entities? 自身免疫性淋巴增生综合征(ALPS)疾病与ALPS表型:二者是否为截然不同的实体? Palmisani, Elena; Miano, Maurizio; Grossi, Alice; Lanciotti, Marina; Lupia, Michela; Terranova, Paola; Ceccherini, Isabella; Montanari, Eugenia; Calvillo, Michaela; Pierri, Filomena; Micalizzi, Concetta; Maggiore, Rosario; Guardo, Daniela; Zanardi, Sabrina; Facchini, Elena; Maggio, Angela; Mastrodicasa, Elena; Corti, Paola; Russo, Giovanna; Pillon, Marta; Farruggia, Piero; Cesaro, Simone; Barone, Angelica; Tosetti, Francesca; Ramenghi, Ugo; Crescenzio, Nicoletta; Bleesing, Jack; Dufour, Carlo; Fioredda, Francesca 分享 收藏
Hematopoietic stem cell transplantation for inborn errors of immunity: 30-year single-center experience Dell'Orso, Gianluca; Bagnasco, Francesca; Giardino, Stefano; Pierri, Filomena; Ferrando, Giulia; Di Martino, Daniela; Micalizzi, Concetta; Guardo, Daniela; Volpi, Stefano; Sabatini, Federica; Miano, Maurizio; Gattorno, Marco; Dufour, Carlo; Faraci, Maura 分享 收藏
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Stem Cell Transplantation in Patients Affected by Shwachman-Diamond Syndrome: Expert Consensus and Recommendations From the EBMT Severe Aplastic Anaemia Working Party Cesaro, Simone; Donadieu, Jean; Cipolli, Marco; Dalle, Jean Hugues; Styczynski, Jan; Masetti, Riccardo; Strahm, Brigitte; Mauro, Margherita; Alseraihy, Amal; Aljurf, Mahmoud; Dufour, Carlo; de la Tour, Regis Peffault 分享 收藏
TACI variants as underlying condition in autoimmune neutropenia: Description of four cases Fioredda, Francesca; Beccaria, Andrea; Turrini, Elena; Casartelli, Pietro; Coviello, Domenico; Maffei, Massimo; Lanciotti, Marina; Lupia, Michela; Terranova, Paola; Grossi, Alice; Ceccherini, Isabella; Miano, Maurizio; Dufour, Carlo 分享 收藏
Sirolimus Restores Erythropoiesis and Controls Immune Dysregulation in a Child With Cartilage-Hair Hypoplasia: A Case Report Del Borrello, Giovanni; Miano, Maurizio; Micalizzi, Concetta; Lupia, Michela; Ceccherini, Isabella; Grossi, Alice; Cavalli, Andrea; Gustincich, Stefano; Rusmini, Marta; Faraci, Maura; Dell'Orso, Gianluca; Ramenghi, Ugo; Mesini, Alessio; Ricci, Erica; Schiavone, Maurizio; Di Iorgi, Natascia; Dufour, Carlo 分享 收藏
Underlying Inborn Errors of Immunity in Patients With Evans Syndrome and Multilineage Cytopenias: A Single-Centre Analysis Miano, Maurizio; Guardo, Daniela; Grossi, Alice; Palmisani, Elena; Fioredda, Francesca; Terranova, Paola; Cappelli, Enrico; Lupia, Michela; Traverso, Monica; Dell'Orso, Gianluca; Corsolini, Fabio; Beccaria, Andrea; Lanciotti, Marina; Ceccherini, Isabella; Dufour, Carlo 分享 收藏