未登录In vivo haemopoietic stem cell gene therapy enabled by postnatal trafficking通过出生后迁移实现的体内造血干细胞基因治疗
Milani, Michela; Fabiano, Anna; Perez-Rodriguez, Marta; Hernandez, Raisa Jofra; Zecchillo, Alessandra; Zonari, Erika; Ottonello, Sofia; Basso-Ricci, Luca; Canepari, Cesare; Volpin, Monica; Iannello, Valeria; Capo, Valentina; Quaranta, Pamela; Seffin, Luca; Russo, Fabio; Biffi, Mauro; Ormoli, Leonardo; Brombin, Chiara; Carlucci, Filippo; Forlino, Antonella; Filibian, Marta; Montini, Eugenio; Scala, Serena; Villa, Anna; Bueren, Juan Antonio; Rio, Paula; Aiuti, Alessandro; Cantore, Alessio; Naldini, Luigi .png)
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收藏Premature ageing of lung alveoli and bone marrow cells from Terc deficient mice with different telomere lengthsGuerrero-Lopez, Rosa; Manguan-Garcia, Cristina; Carrascoso-Rubio, Carlos; Lozano, M. Luz; Toldos-Torres, Marta; Garcia-Castro, Laura; Sanchez-Dominguez, Rebeca; Alberquilla, Omaira; Sanchez-Perez, Isabel; Molina-Molina, Maria; Bueren, Juan A.; Guenechea, Guillermo; Perona, Rosario; Sastre, Leandro 分享 收藏 分享 收藏 Prognostic significance of mutation type and chromosome fragility in Fanconi anemia范可尼贫血中突变类型和染色体脆性的预后意义Ramírez, MJ; Pujol, R; Minguillón, J; Bogliolo, M; Persico, I; Cavero, D; de la Cal, A; Río, P; Navarro, S; Casado, JA; Bailador, A; de la Fuente, AS; de Heredia, ML; Almazán, F; Antelo, ML; Argilés, B; Badell, I; Baragaño, M; Beléndez, C; Bermúdez, M; Bernués, M; Buedo, MI; Carrasco, E; Català, A; Costa, D; Cuesta, I; Fernández-Delgado, R; Fernández-Teijeir, A; Figuera, A; García, M; Gondra, A; González, M; Muñiz, SG; Hernández-Rodríguez, I; Ibañez, F; Kelleher, NJ; Lendínez, F; López, M; López-Almaraz, R; Marchante, I; Mendoza, C; Nieto, J; Ojeda, E; Payán-Pernía, S; Peláez, I; de Soto, IP; Portugal, R; Ramos-Arroyo, MA; Regueiro, A; Rodríguez, A; Rosell, J; Saez, R; Sánchez, J; Sánchez, M; Senent, ML; Tapia, M; Trujillo-Quintero, JP; Vagace, JM; Verdú-Amorós, J; Verdugo, V; Vidales, I; Villarreal, J; Díaz-de-Heredia, C; Sevilla, J; Bueren, J; Surralles, J 分享 收藏 Gene therapy restores the transcriptional program of stem cells in Fanconi anemiaLasaga, Miren; Rio, Paula; Vilas-Zornoza, Amaia; Planell, Nuria; Navarro, Susana; Alignani, Diego; Fernandez-Varas, Beatriz; Mouzo, Daniel; Zubicaray, Josune; Pujol, Roser M.; Nicoletti, Eileen; Schwartz, Jonathan D.; Sevilla, Julian; Ainciburi, Marina; Ullate-Agote, Asier; Surralles, Jordi; Perona, Rosario; Sastre, Leandro; Prosper, Felipe; Gomez-Cabrero, David; Bueren, Juan A. 分享 收藏 Access to gene therapy for rare diseases when commercialization is not fit for purpose当商业化不适合目的时，获得罕见疾病的基因治疗Fox, Thomas; Bueren, Juan; Candotti, Fabio; Fischer, Alain; Aiuti, Alessandro; Lankester, Arjan; AGORA Initiative, Michael; Albert, Michael; Bernardo, Maria Ester; Cavazzana, Marina; Ehl, Stephan; Neven, Benedicte; Prevot, Johan; Schambach, Axel; Sevilla, Julian; Thrasher, Adrian; Wynn, Rob; Booth, Claire 分享 收藏 分享 收藏 分享 收藏 Upregulation of NKG2D ligands impairs hematopoietic stem cell function in Fanconi anemiaCasado, Jose A.; Valeri, Antonio; Sanchez-Dominguez, Rebeca; Vela, Paula; Lopez, Andrea; Navarro, Susana; Alberquilla, Omaira; Hanenberg, Helmut; Pujol, Roser; Segovia, Jose-Carlos; Minguillon, Jordi; Surralles, Jordi; Diaz de Heredia, Cristina; Sevilla, Julian; Rio, Paula; Bueren, Juan A. 分享 收藏 分享 收藏 分享 收藏 Natural gene therapy by reverse mosaicism leads to improved hematology in Fanconi anemia patientsRamirez, Maria Jose; Pujol, Roser; Trujillo-Quintero, Juan Pablo; Minguillon, Jordi; Bogliolo, Massimo; Rio, Paula; Navarro, Susana; Casado, Jose A.; Badell, Isabel; Carrasco, Estela; Balmana, Judith; Catala, Albert; Sevilla, Julian; Belendez, Cristina; Argiles, Bienvenida; Lopez, Monica; Diaz de Heredia, Cristina; Rao, Gayatri; Nicoletti, Eileen; Schwartz, Jonathan D.; Bueren, Juan A.; Surralles, Jordi 分享 收藏 Next-generation Sequencing in Bone Marrow Failure Syndromes and Isolated Cytopenias: Experience of the Spanish Network on Bone Marrow Failure SyndromesGalvez, Eva; Vallespin, Elena; Arias-Salgado, Elena G.; Sanchez-Valdepenas, Carmen; Gimenez, Yari; Navarro, Susana; Rio, Paula; Bogliolo, Massimo; Pujol, Roser; Peiro, Montserrat; Nevado, Julian; Zubicaray, Josune; Sebastian, Elena; Catala, Albert; Belendez, Cristina; Diaz de Heredia, Cristina; Galera, Ana; Badell, Isabel; Madero, Luis; Perona, Rosario; Sastre, Leandro; Surralles, Jordi; Bueren, Juan; Lapunzina, Pablo; Sevilla, Julian 分享 收藏 Enhanced anti-inflammatory effects of mesenchymal stromal cells mediated by the transient ectopic expression of CXCR4 and IL10Hervas-Salcedo, Rosario; Fernandez-Garcia, Maria; Hernando-Rodriguez, Miriam; Quintana-Bustamante, Oscar; Segovia, Jose-Carlos; Alvarez-Silva, Marcio; Garcia-Arranz, Mariano; Minguez, Pablo; del Pozo, Victoria; Rodriguez de Alba, Marta; Garcia-Olmo, Damian; Ayuso, Carmen; Luisa Lamana, Maria; Bueren, Juan A.; Maria Yanez, Rosa 分享 收藏 Generation of dyskeratosis congenita-like hematopoietic stem cells through the stable inhibition of DKC1通过稳定抑制DKC1产生先天性角化障碍样造血干细胞Carrascoso-Rubio, Carlos; Zittersteijn, Hidde A.; Pintado-Berninches, Laura; Fernandez-Varas, Beatriz; Lozano, M. Luz; Manguan-Garcia, Cristina; Sastre, Leandro; Bueren, Juan A.; Perona, Rosario; Guenechea, Guillermo 分享 收藏 Natural estrogens enhance the engraftment of human hematopoietic stem and progenitor cells in immunodeficient miceFananas-Baquero, Sara; Orman, Israel; Aparicio, Federico Becerra; de Miguel, Silvia Bermudez; Merino, Jordi Garcia; Yanez, Rosa; Sainz, Yolanda Fernandez; Sanchez, Rebeca; Dessy-Rodriguez, Mercedes; Alberquilla, Omaira; Alfaro, David; Zapata, Agustin; Bueren, Juan A.; Segovia, Jose Carlos; Quintana-Bustamante, Oscar 分享 收藏 The downregulated membrane expression of CD18 in CD34+ cells defines a primitive population of human hematopoietic stem cellsMesa-Nunez, Cristina; Leon-Rico, Diego; Aldea, Montserrat; Damian, Carlos; Sanchez-Baltasar, Raquel; Sanchez, Rebeca; Alberquilla, Omaira; Segovia, Jose Carlos; Bueren, Juan Antonio; Almarza, Elena 分享 收藏 TALEN mediated gene editing in a mouse model of Fanconi anemiaJose Pino-Barrio, Maria; Gimenez, Yari; Villanueva, Mariela; Hildenbeutel, Marcus; Sanchez-Dominguez, Rebeca; Rodriguez-Perales, Sandra; Pujol, Roser; Surralles, Jordi; Rio, Paula; Cathomen, Toni; Mussolino, Claudio; Antonio Bueren, Juan; Navarro, Susana 分享 收藏 分享 收藏 分享 收藏 
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