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收藏Progranulin AAV gene therapy for frontotemporal dementia: translational studies and phase 1/2 trial interim results
Sevigny, Jeffrey; Uspenskaya, Olga; Heckman, Laura Dean; Wong, Li Chin; Hatch, Daniel A.; Tewari, Ambika; Vandenberghe, Rik; Irwin, David J.; Saracino, Dario; Le Ber, Isabelle; Ahmed, Rebekah; Rohrer, Jonathan D.; Boxer, Adam L.; Boland, Sebastian; Sheehan, Patricia; Brandes, Alissa; Burstein, Suzanne R.; Shykind, Benjamin M.; Kamalakaran, Sitharthan; Daniels, Carter W.; David Litwack, E.; Mahoney, Erin; Velaga, Jenny; McNamara, Ilan; Sondergaard, Patricia; Sajjad, Syed A.; Kobayashi, Yvonne M.; Abeliovich, Asa; Hefti, Franz
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