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Locoregional infusion of EGFR806-CAR T cells for recurrent or refractory pediatric CNS tumors: Results of the completed BrainChild02 phase 1 clinical trial Gust J,Cole BL,Ronsley R,Wilson AL,Seidel K,Wendler J,等. 局部区域灌注EGFR806-CAR T细胞治疗复发或难治性儿童中枢神经系统肿瘤:已完成brainChild02期1临床试验的结果. Neuro Oncol. (2025). doi: 10.1093/neuonc/noaf064 Gust, Juliane; Cole, Bonnie L.; Ronsley, Rebecca; Wilson, Ashley L.; Seidel, Kristy; Wendler, Jason; Pattabhi, Sowmya; Brown, Christopher; Rawlings-Rhea, Stephanie D.; Shtanukhina, Nadezhda; Browd, Samuel R.; Hauptman, Jason S.; Lee, Amy; Ojemann, Jeffrey G.; Crotty, Erin E.; Leary, Sarah E. S.; Perez, Francisco A.; Wright, Jason N.; Albert, Catherine M.; Pinto, Navin; Gardner, Rebecca A.; Vitanza, Nicholas A.; Jensen, Michael C.; Park, Julie R. 分享 收藏
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PEDIATRIC CRANIOPHARYNGIOMA: SINGLE CENTER RETROSPECTIVE STUDY OF SURVIVAL, ENDOCRINOLOGIC, AND VISION OUTCOMES IN 90 PATIENTS Ronsley, Rebecca; Tam, Lydia T.; Do, Olivia; Ermoian, Ralph P.; Leary, Sarah E. S.; Werny, David; Leonard, Skyler; Ferreria, Manuel; Ojemann, Jeffrey; Ellenbogen, Richard G.; Lee, Amy; Ruzevick, Jacob 分享 收藏
Looking beyond year 1 in the molecular era of pediatric brain tumor diagnosis: confirmatory testing of germline variants found on tumor sequencing 在儿科脑肿瘤诊断的分子时代展望第一年: 对肿瘤测序中发现的种系变异进行验证性测试 Greene, Brittany L.; Stasi, Shannon M.; Ting, Michelle A.; Waligorski, Natalie; Cole, Bonnie L.; Lockwood, Christina M.; Paulson, Vera A.; Buchan, Jillian G.; Lee, Amy; Ojemann, Jeffrey G.; Ellenbogen, Richard G.; Stevens, Jeffrey; Leary, Sarah E. S. 分享 收藏
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Lower levels of Th1 and Th2 cytokines in cerebrospinal fluid (CSF) at the time of initial CSF shunt placement in children are associated with subsequent shunt revision surgeries Simon, Tamara D.; Sedano, Sabrina; Rosenberg-Hasson, Yael; Durazo-Arvizu, Ramon; Whitlock, Kathryn B.; Hodor, Paul; Hauptman, Jason S.; Limbrick, David D.; McDonald, Patrick; Ojemann, Jeffrey G.; Maecker, Holden T. 分享 收藏
Long-term outcomes of mesial temporal laser interstitial thermal therapy for drug-resistant epilepsy and subsequent surgery for seizure recurrence: a multi-centre cohort study 内侧颞部激光间质热疗治疗耐药性癫痫的远期疗效及后续手术治疗癫痫复发的多中心队列研究 Youngerman, Brett E.; Banu, Matei A.; Khan, Farhan; McKhann, Guy M.; Schevon, Catherine A.; Jagid, Jonathan R.; Cajigas, Iahn; Theodotou, Christian B.; Ko, Andrew; Buckley, Robert; Ojemann, Jeffrey G.; Miller, John W.; Laxton, Adrian W.; Couture, Daniel E.; Popli, Gautam S.; Buch, Vivek P.; Halpern, Casey H.; Le, Scheherazade; Sharan, Ashwini D.; Sperling, Michael R.; Mehta, Ashesh D.; Englot, Dario J.; Neimat, Joseph S.; Konrad, Peter E.; Sheth, Sameer A.; Neal, Elliot G.; Vale, Fernando L.; Holloway, Kathryn L.; Air, Ellen L.; Schwalb, Jason M.; D'Haese, Pierre-Francois; Wu, Chengyuan 分享 收藏
Target cell-specific synaptic dynamics of excitatory to inhibitory neuron connections in supragranular layers of human neocortex 人类新皮层上层兴奋性与抑制性神经元连接的靶细胞特异性突触动力学 Kim, Mean-Hwan; Radaelli, Cristina; Thomsen, Elliot R.; Monet, Deja; Chartrand, Thomas; Jorstad, Nikolas L.; Mahoney, Joseph T.; Taormina, Michael J.; Long, Brian; Baker, Katherine; Bakken, Trygve E.; Campagnola, Luke; Casper, Tamara; Clark, Michael; Dee, Nick; D'Orazi, Florence; Gamlin, Clare; Kalmbach, Brian E.; Kebede, Sara; Lee, Brian R.; Ng, Lindsay; Trinh, Jessica; Cobbs, Charles; Gwinn, Ryder P.; Keene, C. Dirk; Ko, Andrew L.; Ojemann, Jeffrey G.; Silbergeld, Daniel L.; Sorensen, Staci A.; Berg, Jim; Smith, Kimberly A.; Nicovich, Philip R.; Jarsky, Tim; Zeng, Hongkui; Ting, Jonathan T.; Levi, Boaz P.; Lein, Ed 分享 收藏
Locoregional CAR T cells for children with CNS tumors: Clinical procedure and catheter safety Vitanza, Nicholas A.; Ronsley, Rebecca; Choe, Michelle; Henson, Casey; Breedt, Mandy; Barrios-Anderson, Adriel; Wein, Amy; Brown, Christopher; Beebe, Adam; Kong, Ada; Kirkey, Danielle; Lee, Brittany M.; Leary, Sarah E. S.; Crotty, Erin E.; Hoeppner, Corrine; Holtzclaw, Susan; Wilson, Ashley L.; Gustafson, Joshua A.; Foster, Jessica B.; Iliff, Jeffrey J.; Goldstein, Hannah E.; Browd, Samuel R.; Lee, Amy; Ojemann, Jeffrey G.; Pinto, Navin; Gust, Juliane; Gardner, Rebecca A.; Jensen, Michael C.; Hauptman, Jason S.; Park, Julie R. 分享 收藏
Intraventricular B7-H3 CAR T Cells for Diffuse Intrinsic Pontine Glioma: Preliminary First-in-Human Bioactivity and Safety 脑室内B7-H3 CAR T细胞用于弥漫性内源性脑桥胶质瘤: 初步的人类首次生物活性和安全性 Vitanza, Nicholas A.; Wilson, Ashley L.; Huang, Wenjun; Seidel, Kristy; Brown, Christopher; Gustafson, Joshua A.; Yokoyama, Jason K.; Johnson, Adam J.; Baxter, Blake A.; Koning, Ryan W.; Reid, Aquene N.; Meechan, Michael; Biery, Matthew C.; Myers, Carrie; Rawlings-Rhea, Stephanie D.; Albert, Catherine M.; Browd, Samuel R.; Hauptman, Jason S.; Lee, Amy; Ojemann, Jeffrey G.; Berens, Michael E.; Dun, Matthew D.; Foster, Jessica B.; Crotty, Erin E.; Leary, Sarah E. S.; Cole, Bonnie L.; Perez, Francisco A.; Wright, Jason N.; Orentas, Rimas J.; Chour, Tony; Newell, Evan W.; Whiteaker, Jeffrey R.; Zhao, Lei; Paulovich, Amanda G.; Pinto, Navin; Gust, Juliane; Gardner, Rebecca A.; Jensen, Michael C.; Park, Julie R. 分享 收藏
Acute Postoperative Seizures and Engel Class Outcome at 1 Year Postselective Laser Amygdalohippocampal Ablation for Mesial Temporal Lobe Epilepsy Barkley, Ariana S.; Sullivan, Liam T.; Gibson, Alec W.; Zalewski, Kody; Mac Donald, Christine L.; Barber, Jason K.; Hakimian, Shahin; Ko, Andrew L.; Ojemann, Jeffrey G.; Hauptman, Jason S. 分享 收藏
Profiling PI3K-AKT-MTOR variants in focal brain malformations reveals new insights for diagnostic care Pirozzi, Filomena; Berkseth, Matthew; Shear, Rylee; Gonzalez, Lorenzo; Timms, Andrew E.; Sulc, Josef; Pao, Emily; Oyama, Nora; Forzano, Francesca; Conti, Valerio; Guerrini, Renzo; Doherty, Emily S.; Saitta, Sulagna C.; Lockwood, Christina M.; Pritchard, Colin C.; Dobyns, William B.; Novotny, Edward; Wright, Jason N. N.; Saneto, Russell P.; Friedman, Seth; Hauptman, Jason; Ojemann, Jeffrey; Kapur, Raj P.; Mirzaa, Ghayda M. 分享 收藏
Mutations of the DNA repair gene PNKP in a patient with microcephaly, seizures, and developmental delay (MCSZ) presenting with a high-grade brain tumor 患有高等级脑瘤的小头畸形,癫痫发作和发育迟缓 (MCSZ) 患者的DNA修复基因PNKP突变 Jiang, Bingcheng; Murray, Cameron; Cole, Bonnie L.; Glover, J. N. Mark; Chan, Gordon K.; Deschenes, Jean; Mani, Rajam S.; Subedi, Sudip; Nerva, John D.; Wang, Anthony C.; Lockwood, Christina M.; Mefford, Heather C.; Leary, Sarah E. S.; Ojemann, Jeffery G.; Weinfeld, Michael; Ene, Chibawanye, I 分享 收藏
Closing the Loop With Cortical Sensing: The Development of Adaptive Deep Brain Stimulation for Essential Tremor Using the Activa PC plus S Fraczek, Tomasz M.; Ferleger, Benjamin I.; Brown, Timothy E.; Thompson, Margaret C.; Haddock, Andrew J.; Houston, Brady C.; Ojemann, Jeffrey G.; Ko, Andrew L.; Herron, Jeffrey A.; Chizeck, Howard J. 分享 收藏
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