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Gustavo Tiscórnia

university of algarve
H指数:20
被引数:5,256

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FLT201, a novel liver-directed AAV gene therapy candidate for Gaucher disease type 1

FLT201,一种新型的肝脏靶向AAV基因治疗候选药物,用于治疗戈谢病1型

2025-05-070
OAAI
Rewired glycosylation activity promotes scarless regeneration and functional recovery in spiny mice after complete spinal cord transection
2022-02-0132
OA