Not logged inA simple surrogate approach for the quantitation of C4 (7α-hydroxy-4-cholesten-3-one) in human serum via LC-MS/MS and its application in a clinical study
Yin, Feng; Vakkalanka, Mani Deepika; Wiley, Walter; Woolf, M. Shane; Basir, Yousef; Shah, Kumar; Wheeler, Aaron M.; Yuan, Moucun; Mylott Jr, William R.; Baratta, Mike
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SaveMultimodal Detection of Narcolepsy Type 1 Using Genetic and Nocturnal Polysomnography Data
Olsen, Mads; Zahid, Alexander Neergaard; Galinsky, Kevin; Retnam, Reuben; Lin, Ling; Yan, Han; Tracey, Brian; Buhl, Derek; Volfson, Dmitri; Mignot, Emmanuel
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SaveAAV delivery of GBA1 suppresses α-synuclein accumulation in Parkinson's disease models and restores functions in Gaucher's disease models
Okai, Takuro; Sato, Sho; Deshpande, Mugdha; Matsumoto, Shin-ichi; Nakayama, Miyu; Yamamoto, Syunsuke; Strack-Logue, Bettina; Hioki, Takeshi; Tanaka, Maiko; Proetzel, Gabriele
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SaveEfficacy, Safety, Tolerability, and Serum IgG Trough Levels of Hyaluronidase-Facilitated Subcutaneous Immunoglobulin 10% in US Pediatric Patients with Primary Immunodeficiency Diseases
Patel, Niraj C.; Walter, Jolan E.; Wasserman, Richard L.; Rubinstein, Arye; Kankirawatana, Suthida; Shepherd, Meagan W.; Greco, Erin; Li, Zhaoyang; Russo-Schwarzbaum, Sharon; Saeed-Khawaja, Shumyla; Mccoy, Barbara; Yel, Leman
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SaveMass cytometric analysis of circulating monocyte subsets in a murine model of diabetic gastroparesis
Alasfoor, S; Jessen, E; Pullapantula, SR; Voisin, JR; Hsi, LC; Pavelko, KD; Farwana, S; Patraw, JA; Chai, XY; Ji, SH; Strausbauch, MA; Cipriani, G; Wei, L; Linden, DR; Hou, RX; Myers, R; Bhattarai, Y; Wykosky, J; Burns, AJ; Dasari, S; Farrugia, G; Grover, M
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SaveAn Acetylcholine M1 Receptor-Positive Allosteric Modulator (TAK-071) in Parkinson Disease With Cognitive Impairment
Shanbhag, Niraj M.; Padmanabhan, Jaya L.; Zhang, Zheng; Harel, Brian T.; Jia, Hongxia; Kangarloo, Tairmae; Yin, Wei; Dowling, Ariel V.; Laurenza, Antonio; Khudyakov, Polyna; Galinsky, Kevin; Latzman, Robert D.; Simuni, Tanya; Weintraub, Daniel; Horak, Fay B.; Lustig, Cindy; Maruff, Paul; Simen, Arthur A.
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