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SaveRecapitulation of premature ageing with iPSCs from Hutchinson-Gilford progeria syndrome (Apr, 10.1038/s41586-025-08924-0, 2025)
Liu, Guang-Hui; Barkho, Basam Z.; Ruiz, Sergio; Diep, Dinh; Qu, Jing; Yang, Sheng-Lian; Panopoulos, Athanasia D.; Suzuki, Keiichiro; Kurian, Leo; Walsh, Christopher; Thompson, James; Boue, Stephanie; Fung, Ho Lim; Sancho-Martinez, Ignacio; Zhang, Kun; Yates Iii, John; Belmonte, Juan Carlos Izpisua
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SaveDynamic WNT signaling controls differentiation of hematopoietic progenitor cells from human pluripotent stem cells
Li, Mo; Suzuki, Keiichiro; Wang, Mengge; Benner, Christopher; Ku, Manching; Ma, Li; Kobari, Ladan; Kim, Na Young; Montserrat, Nuria; Chang, Chan-Jung; Liu, Guanghui; Qu, Jing; Xu, Jinna; Zhang, Yingzi; Aizawa, Emi; Wu, Jun; Douay, Luc; Esteban, Concepcion Rodriguez
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SaveOptimization of HITI-Mediated Gene Insertion for Rhodopsin and Peripherin-2 in Mouse Rod Photoreceptors: Targeting Dominant Retinitis Pigmentosa
Onishi, Akishi; Tsunekawa, Yuji; Mandai, Michiko; Ishimaru, Aiko; Ohigashi, Yoko; Sho, Junki; Yasuda, Kazushi; Suzuki, Keiichiro; Belmonte, Juan Carlos Izpisua; Matsuzaki, Fumio; Takahashi, Masayo
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SaveComprehensive High-Depth Proteomic Analysis of Plasma Extracellular Vesicles Containing Preparations in Rett Syndrome
Hagiwara, Sho; Shiohama, Tadashi; Takahashi, Satoru; Ishikawa, Masaki; Kawashima, Yusuke; Sato, Hironori; Sawada, Daisuke; Uchida, Tomoko; Uchikawa, Hideki; Kobayashi, Hironobu; Shiota, Megumi; Nabatame, Shin; Tsujimura, Keita; Hamada, Hiromichi; Suzuki, Keiichiro
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SaveOptimization of an adeno-associated viral vector for epidermal keratinocytes in vitro and in vivo
Shen, Qi; Suga, Shogo; Moriwaki, Yuta; Du, Zening; Aizawa, Emi; Okazaki, Mutsumi; Belmonte, Juan Carlos Izpisua; Hirabayashi, Yusuke; Suzuki, Keiichiro; Kurita, Masakazu
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SaveTherapeutic strategy for spinal muscular atrophy by combining gene supplementation and genome editing
Hatanaka, Fumiyuki; Suzuki, Keiichiro; Shojima, Kensaku; Yu, Jingting; Takahashi, Yuta; Sakamoto, Akihisa; Prieto, Javier; Shokhirev, Maxim; Nunez Delicado, Estrella; Rodriguez Esteban, Concepcion; Izpisua Belmonte, Juan Carlos
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SaveWiskott-Aldrich syndrome protein forms nuclear condensates and regulates alternative splicing (vol 13, 3646, 2022)
Yuan, Baolei; Zhou, Xuan; Suzuki, Keiichiro; Ramos-Mandujano, Gerardo; Wang, Mengge; Tehseen, Muhammad; Cortes-Medina, Lorena V.; Moresco, James J.; Dunn, Sarah; Hernandez-Benitez, Reyna; Hishida, Tomoaki; Kim, Na Young; Andijani, Manal M.; Bi, Chongwei; Ku, Manching; Takahashi, Yuta; Xu, Jinna; Qiu, Jinsong; Huang, Ling; Benner, Christopher; Aizawa, Emi; Qu, Jing; Liu, Guang-Hui; Li, Zhongwei; Yi, Fei; Ghosheh, Yanal; Shao, Changwei; Shokhirev, Maxim; Comoli, Patrizia; Frassoni, Francesco; Yates, John R., III; Fu, Xiang-Dong; Esteban, Concepcion Rodriguez; Hamdan, Samir; Izpisua Belmonte, Juan Carlos; Li, Mo
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SaveWiskott-Aldrich syndrome protein forms nuclear condensates and regulates alternative splicing
Yuan, Baolei; Zhou, Xuan; Suzuki, Keiichiro; Ramos-Mandujano, Gerardo; Wang, Mengge; Tehseen, Muhammad; Cortes-Medina, Lorena, V; Moresco, James J.; Dunn, Sarah; Hernandez-Benitez, Reyna; Hishida, Tomoaki; Kim, Na Young; Andijani, Manal M.; Bi, Chongwei; Ku, Manching; Takahashi, Yuta; Xu, Jinna; Qiu, Jinsong; Huang, Ling; Benner, Christopher; Aizawa, Emi; Qu, Jing; Liu, Guang-Hui; Li, Zhongwei; Yi, Fei; Ghosheh, Yanal; Shao, Changwei; Shokhirev, Maxim; Comoli, Patrizia; Frassoni, Francesco; Yates, John R., III; Fu, Xiang-Dong; Esteban, Concepcion Rodriguez; Hamdan, Samir; Li, Mo; Belmonte, Juan Carlos Izpisua
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SaveEstablishment of mouse model of inherited PIGO deficiency and therapeutic potential of AAV-based gene therapy
Kuwayama, Ryoko; Suzuki, Keiichiro; Nakamura, Jun; Aizawa, Emi; Yoshioka, Yoshichika; Ikawa, Masahito; Nabatame, Shin; Inoue, Ken-Ichi; Shimmyo, Yoshiari; Ozono, Keiichi; Kinoshita, Taroh; Murakami, Yoshiko
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SavePrecise in vivo genome editing via single homology arm donor mediated intron-targeting gene integration for genetic disease correction
Suzuki, Keiichiro; Yamamoto, Mako; Hernandez-Benitez, Reyna; Li, Zhe; Wei, Christopher; Devi Soligalla, Rupa; Aizawa, Emi; Hatanaka, Fumiyuki; Kurita, Masakazu; Reddy, Pradeep; Ocampo, Alejandro; Hishida, Tomoaki; Sakurai, Masahiro; Nemeth, Amy N.; Nunez Delicado, Estrella; Campistol, Josep M.; Magistretti, Pierre; Guillen, Pedro; Esteban, Concepcion Rodriguez; Gong, Jianhui; Yuan, Yilin; Gu, Ying; Liu, Guang-Hui; Lopez-Otin, Carlos; Wu, Jun; Zhang, Kun; Belmonte, Juan Carlos Izpisua
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