Not logged in An atlas of cells in the human tonsil Massoni-Badosa, Ramon; Aguilar-Fernandez, Sergio; Nieto, Juan C.; Soler-Vila, Paula; Elosua-Bayes, Marc; Marchese, Domenica; Kulis, Marta; Vilas-Zornoza, Amaia; Buhler, Marco Matteo; Rashmi, Sonal; Alsinet, Clara; Caratu, Ginevra; Moutinho, Catia; Ruiz, Sara; Lorden, Patricia; Lunazzi, Giulia; Colomer, Dolors; Frigola, Gerard; Blevins, Will; Romero-Rivero, Lucia; Jimenez-Martinez, Victor; Vidal, Anna; Mateos-Jaimez, Judith; Maiques-Diaz, Alba; Ovejero, Sara; Moreaux, Jerome; Palomino, Sara; Gomez-Cabrero, David; Agirre, Xabier; Weniger, Marc A.; King, Hamish W.; Garner, Lucy C.; Marini, Federico; Cervera-Paz, Francisco Javier; Baptista, Peter M.; Vilaseca, Isabel; Rosales, Cecilia; Ruiz-Gaspa, Silvia; Talks, Benjamin; Sidhpura, Keval; Pascual-Reguant, Anna; Hauser, Anja E.; Haniffa, Muzlifah; Prosper, Felipe; Kueppers, Ralf; Gut, Ivo Glynne; Campo, Elia; Martin-Subero, Jose Ignacio; Heyn, Holger Share Save
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Therapeutic expression of human clotting factors IX and X following adeno-associated viral vector-mediated intrauterine gene transfer in early-gestation fetal macaques Chan, Jerry K. Y.; Gil-Farina, Irene; Johana, Nuryanti; Rosales, Cecilia; Tan, Yi Wan; Ceiler, Jessika; Mcintosh, Jenny; Ogden, Bryan; Waddington, Simon N.; Schmidt, Manfred; Biswas, Arijit; Choolani, Mahesh; Nathwani, Amit C.; Mattar, Citra N. Z. Share Save
In Utero Transfer of Adeno-Associated Viral Vectors Produces Long-Term Factor IX Levels in a Cynomolgus Macaque Model Mattar, Citra N. Z.; Gil-Farina, Irene; Rosales, Cecilia; Johana, Nuryanti; Tan, Yvonne Yi Wan; McIntosh, Jenny; Kaeppel, Christine; Waddington, Simon N.; Biswas, Arijit; Choolani, Mahesh; Schmidt, Manfred; Nathwani, Amit C.; Chan, Jerry K. Y. Share Save
Longitudinal Surveillance of Non Human Primate Recipients of Intrauterine Gene Transfer for Coagulation Factor Deficiencies Mattar, Citra; Biswas, Arijit; Johana, Nuryanti; Tan, Yvonne Y. W.; Rosales, Cecilia; McKintosh, Jenny; Tan, Lay-Geok; Gil-Farina, Irene; Choolani, Mahesh; Schmidt, Manfred; Nathwani, Amit; Chan, Jerry K. Y. Share Save
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Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B Nathwani, A. C.; Reiss, U. M.; Tuddenham, E. G. D.; Rosales, C.; Chowdary, P.; McIntosh, J.; Della Peruta, M.; Lheriteau, E.; Patel, N.; Raj, D.; Riddell, A.; Pie, J.; Rangarajan, S.; Bevan, D.; Recht, M.; Shen, Y. -M.; Halka, K. G.; Basner-Tschakarjan, E.; Mingozzi, F.; High, K. A.; Allay, J.; Kay, M. A.; Ng, C. Y. C.; Zhou, J.; Cancio, M.; Morton, C. L.; Gray, J. T.; Srivastava, D.; Nienhuis, A. W.; Davidoff, A. M. Share Save
DEVELOPMENT OF A LIVER-SPECIFIC, TUMOUR-SELECTIVE RECOMBINANT ADENO-ASSOCIATED VIRUS VECTOR TO TARGET HEPATOCELLULAR CARCINOMA Della Peruta, M.; Binny, C.; Nathwani, D.; McIntosh, J.; Rosales, C.; Davidoff, A. M.; Williams, R.; Chokshi, S.; Nathwani, A. C. Share Save
Adenovirus-Associated Virus Vector-Mediated Gene Transfer in Hemophilia B Nathwani, Amit C.; Tuddenham, Edward G. D.; Rangarajan, Savita; Rosales, Cecilia; McIntosh, Jenny; Linch, David C.; Chowdary, Pratima; Riddell, Anne; Pie, Arnulfo Jaquilmac; Harrington, Chris; O'Beirne, James; Smith, Keith; Pasi, John; Glader, Bertil; Rustagi, Pradip; Ng, Catherine Y. C.; Kay, Mark A.; Zhou, Junfang; Spence, Yunyu; Morton, Christopher L.; Allay, James; Coleman, John; Sleep, Susan; Cunningham, John M.; Srivastava, Deokumar; Basner-Tschakarjan, Etiena; Mingozzi, Federico; High, Katherine A.; Gray, John T.; Reiss, Ulrike M.; Nienhuis, Arthur W.; Davidoff, Andrew M. Share Save
Long-term Safety and Efficacy Following Systemic Administration of a Self-complementary AAV Vector Encoding Human FIX Pseudotyped With Serotype 5 and 8 Capsid Proteins Nathwani, Amit C.; Rosales, Cecilia; McIntosh, Jenny; Rastegarlari, Ghasem; Nathwani, Devhrut; Raj, Deepak; Nawathe, Sushmita; Waddington, Simon N.; Bronson, Roderick; Jackson, Scott; Donahue, Robert E.; High, Katherine A.; Mingozzi, Federico; Ng, Catherine Y. C.; Zhou, Junfang; Spence, Yunyu; McCarville, M. Beth; Valentine, Marc; Allay, James; Coleman, John; Sleep, Susan; Gray, John T.; Nienhuis, Arthur W.; Davidoff, Andrew M. Share Save
The dynamic DNA methylomes of double-stranded DNA viruses associated with human cancer Fernandez, Agustin F.; Rosales, Cecilia; Lopez-Nieva, Pilar; Grana, Osvaldo; Ballestar, Esteban; Ropero, Santiago; Espada, Jesus; Melo, Sonia A.; Lujambio, Amaia; Fraga, Mario F.; Pino, Irene; Javierre, Biola; Carmona, Francisco J.; Acquadro, Francesco; Steenbergen, Renske D. M.; Snijders, Peter J. F.; Meijer, Chris J.; Pineau, Pascal; Dejean, Anne; Lloveras, Belen; Capella, Gabriel; Quer, Josep; Buti, Maria; Esteban, Juan-Ignacio; Allende, Helena; Rodriguez-Frias, Francisco; Castellsague, Xavier; Minarovits, Janos; Ponce, Jordi; Capello, Daniela; Gaidano, Gianluca; Cigudosa, Juan Cruz; Gomez-Lopez, Gonzalo; Pisano, David G.; Valencia, Alfonso; Piris, Miguel Angel; Bosch, Francesc X.; Cahir-McFarland, Ellen; Kieff, Elliott; Esteller, Manel Share Save