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Integrated stem cell signature and cytomolecular risk determination in pediatric acute myeloid leukemia Huang, Benjamin J.; Smith, Jenny L.; Farrar, Jason E.; Wang, Yi-Cheng; Umeda, Masayuki; Ries, Rhonda E.; Leonti, Amanda R.; Crowgey, Erin; Furlan, Scott N.; Tarlock, Katherine; Armendariz, Marcos; Liu, Yanling; Shaw, Timothy, I; Wei, Lisa; Gerbing, Robert B.; Cooper, Todd M.; Gamis, Alan S.; Aplenc, Richard; Kolb, E. Anders; Rubnitz, Jeffrey; Ma, Jing; Klco, Jeffery M.; Ma, Xiaotu; Alonzo, Todd A.; Triche, Timothy, Jr.; Meshinchi, Soheil Share Save
CBFB-MYH11 fusion transcripts distinguish acute myeloid leukemias with distinct molecular landscapes and outcomes Huang, Benjamin J.; Smith, Jenny L.; Wang, Yi-Cheng; Taghizadeh, Kassra; Leonti, Amanda R.; Ries, Rhonda E.; Liu, Yanling; Kolekar, Pandurang; Tarlock, Katherine; Gerbing, Robert; Crowgey, Erin; Furlan, Scott N.; Shaw, Timothy, I; Hagiwara, Kohei; Wei, Lisa; Cooper, Todd M.; Gamis, Alan S.; Aplenc, Richard; Kolb, E. Anders; Farrar, Jason E.; Triche, Timothy; Alonzo, Todd A.; Ma, Xiaotu; Meshinchi, Soheil Share Save
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Single-cell analysis of RORα tracer mouse lung reveals ILC progenitors and effector ILC2 subsets Ghaedi, Maryam; Shen, Zi Yi; Orangi, Mona; Martinez-Gonzalez, Itziar; Wei, Lisa; Lu, Xiaoxiao; Das, Arundhoti; Heravi-Moussavi, Alireza; Marra, Marco A.; Bhandoola, Avinash; Takei, Fumio Share Save
Identification and Analyses of Extra-Cranial and Cranial Rhabdoid Tumor Molecular Subgroups Reveal Tumors with Cytotoxic T Cell Infiltration Chun, Hye-Jung E.; Johann, Pascal D.; Milne, Katy; Zapatka, Marc; Buellesbach, Annette; Ishaque, Naveed; Iskar, Murat; Erkek, Serap; Wei, Lisa; Tessier-Cloutier, Basile; Lever, Jake; Titmuss, Emma; Topham, James T.; Bowlby, Reanne; Chuah, Eric; Mungall, Karen L.; Ma, Yussanne; Mungall, Andrew J.; Moore, Richard A.; Taylor, Michael D.; Gerhard, Daniela S.; Jones, Steven J. M.; Korshunov, Andrey; Gessler, Manfred; Kerl, Kornelius; Hasselblatt, Martin; Fruehwald, Michael C.; Perlman, Elizabeth J.; Nelson, Brad H.; Pfister, Stefan M.; Marra, Marco A.; Kool, Marcel Share Save
Retinal AAV8-RS1 Gene Therapy for X-Linked Retinoschisis: Initial Findings from a Phase I/IIa Trial by Intravitreal Delivery Cukras, Catherine; Wiley, Henry E.; Jeffrey, Brett G.; Sen, H. Nida; Turriff, Amy; Zeng, Yong; Vijayasarathy, Camasamudram; Marangoni, Dario; Ziccardi, Lucia; Kjellstrom, Sten; Park, Tae Kwon; Hiriyanna, Suja; Wright, J. Fraser; Colosi, Peter; Wu, Zhijian; Bush, Ronald A.; Wei, Lisa L.; Sieving, Paul A. Share Save
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Human Gene Therapy for a Synaptic Disease: X-Linked Retinoschisis (XLRS) Sieving, Paul A.; Vijayasarathy, Camasamudram; Ou, Jinxing; Ziccardi, Lucia; Chen, Shan; Zeng, Yong; Marangoni, Dario; Li, Wei; Wu, Zhijian; Wei, Lisa L.; Bush, Ronald A. Share Save
A Dominant-Negative Isoform of IKAROS Expands Primitive Normal Human Hematopoietic Cells Beer, Philip A.; Knapp, David J. H. F.; Kannan, Nagarajan; Miller, Paul H.; Babovic, Sonja; Bulaeva, Elizabeth; Aghaeepour, Nima; Rabu, Gabrielle; Rostamirad, Shabnam; Shih, Kingsley; Wei, Lisa; Eaves, Connie J. Share Save
CNGB3-Achromatopsia Clinical Trial With CNTF: Diminished Rod Pathway Responses With No Evidence of Improvement in Cone Function Zein, Wadih M.; Jeffrey, Brett G.; Wiley, Henry E.; Turriff, Amy E.; Tumminia, Santa J.; Tao, Weng; Bush, Ronald A.; Marangoni, Dario; Wen, Rong; Wei, Lisa L.; Sieving, Paul A. Share Save
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Persistent Expression of PEDF in the Eye Using High-capacity Adenovectors Chen, Ping; Hamilton, Melissa; Thomas, Charles A.; Kroeger, Kurt; Carrion, Miguel; MacGill, Randall S.; Gehlbach, Peter; Brough, Douglas E.; Wei, Lisa L.; King, C. Richter; Bruder, Joseph T. Share Save
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