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Franco Locatelli

irccs ospedale pediatrico bambino gesù

125H-index
2.1KPaper Count
7.1WCitation Count
Published Papers 617
Publication Date
2026 Update on Clinical Trials in β-Thalassemia
err2026-08-15
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errKhaled M. Musallam; Franco Locatelli; Mattia Algeri; Maria Domenica Cappellini; Ali T. Taher
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Population Pharmacokinetics of Bosutinib in Children with Philadelphia Chromosome-Positive Chronic Myelogenous Leukemia Based on a Phase I Dose-Finding Trial (ITCC-054/COG AAML1921) and Pediatric Recommended Phase II Dosage Evaluation
err2026-07-27
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errJen-Hao Wu; Francisco Bautista; Erica Brivio; Marieke Willemse; Karey Kowalski; Brian Jermain; May Garrett; Andrew Bukowinski; Carmelo Rizzari; Jessica Pollard; Laura Murillo-Sanjuán; Matthew Kutny; Sara Zarnegar-Lumley; Michele Redell; Stacy Cooper; Yves Bertrand; Arnaud Petit; Julie Krystal; Markus Metzler; Donna Lancaster; Jean-Pierre Bourquin; Jayashree Motwani; Inge M. van der Sluis; Franco Locatelli; Michael E. Roth; Nobuko Hijiya; C. Michel Zwaan; Alwin D. R. Huitema
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Efficacy of blinatumomab for dermatomyositis/SLE overlap syndrome occurring after allogeneic hematopoietic stem cell transplant performed for acute lymphoblastic leukemia
err2026-07-21
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PREAI
errRoberto Carta; Carmen Dolores De Luca; Valentina Bertaina; Stefania Gaspari; Pietro Merli; Daria Pagliara; Franco Locatelli
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Is the adult EBMT risk score valid and relevant for hematopoietic stem cell transplantation in children acute leukemia?
err2026-07-20
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errF. Baleydier; J. E. Galimard; F. Bernard; F. Gonzales; A. Dalissier; A. Al-Seraihy; J.-H. Dalle; C. R. S. Uppugunduri; L. Zubarovskaya; M. Zecca; F. Locatelli; A. Kulagin; F. Fagioli; S. Robinson; A. Balduzzi; A. Biffi; Y. Chalandon; P. Bader; S. Corbacioglu; Krzysztof Kalwak; M. Ansari
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Update of the decision-making algorithm on selecting transfusion-dependent β-thalassemic patients for gene therapy approaches: joint consensus report on behalf of EHA-specialized working group and EBMT hemoglobinopathies working party
err2026-07-16
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PREAI
errLucia de Franceschi; Mahmoud Aljurf; Donatella Baronciani; Celeste Bento; Christian Chabannon; Selim Corbacioglu; Josu de la Fuente; Gian Luca Forni; Antonis Kattamis; Franco Locatelli; Roland Meisel; Ali Taher; Paul Telfer; Isabelle Thuret; Emanuele Angelucci
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Inotuzumab ozogamicin in paediatric very high risk first B-cell acute lymphoblastic leukaemia relapse (ITCC-059): a multicentre, single-arm, phase 2 trial
err2026-06-15
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PREAI
errNicolò Peccatori; Franco Locatelli; Anneke C J Ammerlaan; Yilin Jiang; Vincent H J van der Velden; Andrej Lissat; Anna Nilsson; Bella Bielorai; Barbara De Moerloose; Susana Rives; Alba Rubio-San-Simon; Uta Dirksen; Gernot Engstler; Benedicte Bruno; Cristina Diaz-de-Heredia; Benoit Brethon; Francisco Bautista Sirvent; Fanny Rialland; Lucie Sramkova; Marlène Pasquet
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Correction of Ineffective Erythropoiesis and Normalization of Iron Homeostasis After Exagamglogene Autotemcel in Transfusion-Dependent β-Thalassemia
err2026-06-07
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errSujit Sheth; Selim Corbacioglu; Josu de la Fuente; Mattia Algeri; Joachim Rupprecht; Kevin H. M. Kuo; Ami J. Shah; Peter Lang; Hayley Merkeley; Ben Carpenter; Markus Y. Mapara; Robert I. Liem; Stephan Grupp; Yogi Chopra; Amanda M. Li; Janet L. Kwiatkowski; Melanie Kirby-Allen; Maria Domenica Cappellini; Antonis Kattamis; Sakellarios Zairis; Tina Liu; William Hobbs; Haydar Frangoul; Franco Locatelli; Roland Meisel; the CLIMB THAL-111 and CLIMB-131 Study Groups
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Carfilzomib plus induction chemotherapy in children with relapsed or refractory acute lymphoblastic leukemia
err2026-06-05
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errFranco Locatelli; Musa Karakukcu; Van Huynh; Berta González-Martínez; Mecneide Mendes Lins; Meng-Yao Lu; Maria Luisa Sulis; Melinda Pauly; Christopher Morris; Megan Braunlin; Mihaela Talpes; Lia Gore
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Multi-omics analyses identify EZH2 as a central driver in rhabdomyosarcoma radioresistance and highlight Tazemetostat as an effective radiosensitizer in vitro and in vivo
err2026-06-01
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errMatteo Cassandri; Antonella Porrazzo; Simona Camero; Silvia Pomella; Valeria Manzi; Francesca Vulcano; Luisa Milazzo; Francesca Pedini; Deborah Pajalunga; Andrea Casagrande; Giada Mele; Valentina Lulli; Enrico Romano; Michele Signore; Massimo Spada; Maria Teresa D’Urso; Silvia Codenotti; Alessandro Fanzani; Annunziata Mauro; Giovanna Marchese; Simone Sidoli; Giovanni Luca Gravina; Giovanni Barillari; Franco Locatelli; Francesca Megiorni; Rossella Rota; Francesco Marampon
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The impact of pre-transplant extramedullary disease on the outcome of allogeneic hematopoietic cell transplantation for acute myeloid leukaemia in children- on behalf of PDWP/EBMT
err2026-05-19
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PREAI
errJuliana Silva; Jacques-Emmanuel Galimard; Jean-Hugues Dalle; Franco Locatelli; Hawazen S. Alsaedi; Miguel Angel Diaz; Charlotte Jubert; Cecile Renard; Giuseppina Simone; Peter Bader; Franca Fagioli; Vassiliki Kitra Roussou; Caroline L. Furness; Robert Wynn; Birgit Burkhardt; Alessandra Biffi; Marc Bierings; Cristina Díaz de Heredia; Arcangelo Prete; Amos Toren; Katharine Patrick; Wolfgang Holter; Krzysztof Kalwak; Arnaud Dalissier; Kanchan Rao; Selim Corbacioglu
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Gilteritinib + chemotherapy in children with relapsed/refractory FLT3-ITD AML: results from the phase 1/2 SKIPPER trial
err2026-05-12
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errPhilip Connor; Raul Ribeiro; Albert Catala; Alice Norton; Michael M Schündeln; Nahla Hasabou; David Delgado; Alexandra Heinloth; Jason Hill; Stanley Gill; Theophile Bigirumurame; Sarah K Tasian; Franco Locatelli
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A specific stem cell program and CD112 immunological axis dysfunctions underpinning monosomy 7-associated myeloid neoplasms
err2026-05-11
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errAnair Graciela Lema Fernandez; Carlotta Nardelli; Martina Quintini; Valeria Di Battista; Valentina Pierini; Barbara Crescenzi; Fabrizia Pellanera; Caterina Matteucci; Valentina Bardelli; Maria Crocioni; Giovanni Martino; Francesco Maria Adamo; Francesca Milano; Maria Paola Martelli; Pietro Merli; Loredana Bury; Paolo Gorello; Mattia Forcato; Franco Locatelli; Loredana Ruggeri; Cristina Mecucci
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CD84 is a specific target for acute myeloid leukemia CAR-T cell therapy
err2026-05-08
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errMartina Pigazzi; Silvia Merlini; Ambra Da Ros; Olivia Marini; Giovanni Faggin; Nicolò Fortuna; Raffaele Mattera; Barbara Buldini; Paolo Rizzardi; Soheil Meshinchi; Giuseppe Basso; Franco Locatelli; Alessandra Biffi
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Outcomes of 544 Patients with t(6;9)/DEK::NUP214 acute myeloid leukemia undergoing allogeneic stem cell transplantation: an EBMT study on behalf of the acute leukemia working party (ALWP) and the pediatric diseases working party (PDWP)
err2026-04-22
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PREAI
errFabio Andreozzi; Jacques-Emmanuel Galimard; Johan Maertens; Mahmoud Aljurf; Katherine Clesham; Jaime Sanz; Sebastien Maury; Sandrine Loron; Jakob Passweg; Thomas Schroeder; Urpu Salmenniemi; Gwendolyn van Gorkom; Regis Peffault de Latour; Peter A. von dem Borne; Franco Locatelli; Robert F. Wynn; Jean-Hugues Dalle; Jordi Esteve; Arnon Nagler; Katharina Kleinschmidt; Mohamad Mohty; Krzysztof Kalwak; Fabio Ciceri
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Second Allogeneic Hematopoietic Cell Transplantation After Graft Failure Is an Effective Curative Option in Children With Hemoglobinopathies
err2026-04-07
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errArianna Panigari; Mattia Algeri; Pietro Merli; Tommaso Mina; Michele Massa; Annalisa Agostini; Gloria Acquafredda; Tina Diana Boti Lou; Francesco Scattaglia; Giovanna Giorgiani; Jolanda Pianese; Ilaria Pili; Francesco Quagliarella; Daria Pagliara; Patrizia Comoli; Marco Zecca; Franco Locatelli
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Proteasome inhibition promotes Foxn1 expression in thymic epithelial cells and induces thymic regeneration in mice
err2026-03-26
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PREAI
errShirley Genah; Marsha Pellegrino; Manuela Giansanti; Angelica Mancusi; Alessio Taviani; Antonella Cardinale; Marco Rosichini; Sara Flamini; Maria Luigia Catanoso; Ezio Giorda; Gabriele Volpe; Michela Piccione; Francesca Nazio; Jarrod A. Dudakov; Marcel R. M. van den Brink; Emmanuel de Billy; Franco Locatelli; Enrico Velardi
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Outcome of Second Conditioned Allogeneic Stem Cell Transplant in Children with Non-SCID Inborn Errors of Immunity
err2026-03-05
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errZohreh Nademi; Su Han Lum; Patrick Gilbert; Tiarlan Sirait; Musa Karakukcu; Franco Locatelli; Ansgar Schulz; Jolanta Gozdzik; Aydan Ikinciogullari; Krzysztof Kalwak; Hawazen Alsaedi; Marc Bierings; Peter Bader; Cristina Diaz de Heredia; Jacek Winiarski; Tania Nicole Masmas; Arjan. C Lankester; Melissa Gabriel; Alessandra Biffi; Richard Mitchell
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Anti-CD19 CAR T cells for pediatric patients with treatment-refractory autoimmune diseases
err2026-02-05
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PREAI
errMarco Becilli; Markus Metzler; Claudia Bracaglia; Rebecca Nicolai; Tobias Krickau; Francesca Del Bufalo; Chiara Rosignoli; Emiliano Marasco; Nora Naumann-Bartsch; Virginia Messia; Pietro Merli; Daria Pagliara; Mattia Algeri; Aurelio Secinaro; Maria Giuseppina Cefalo; Francesca Diomedi Camassei; Valentina Bertaina; Matilde Sinibaldi; Antonella Insalaco; Michael Aigner; Giovanna Leone; Giuseppina Li Pira; Monica Gunetti; Stefan Berg; Biagio De Angelis; Simon Völkl; Linda Hanssens; Fabian Müller; Andreas Mackensen; Concetta Quintarelli; Georg Schett; Fabrizio De Benedetti; Franco Locatelli
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Advancing Precision Therapy in Pediatric Acute Myeloid Leukemia Through PDX Models and Mitochondrial Targeting
err2026-01-29
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errAmbra Da Ros; Alberto Peloso; Giorgia Longo; Maddalena Benetton; Valentina Indio; Stefano Cairo; Monica Sandri; Barbara Buldini; Silvia Bresolin; Antonio Rosato; Andrea Pession; Claudia Tregnago; Franco Locatelli; Martina Pigazzi
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