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Edmund C. Lee

regulus therapeutics inc.

7H-index
36Paper Count
1.1KCitation Count
Published Papers 9
Publication Date
The nucleobase guanine at the 3’-terminus of oligonucleotide RGLS4326 drives off-target AMPAR inhibition and CNS toxicity
err2025-11-28
err0
errOAAI
errTania Valencia; Laura Y. Yen; Cindy Berman; Thomas Vincent; Scott Davis; Francesca Varrone; Jianfeng Huang; Jessica Mastroianni; Morgan Carlson; Tate Owen; Amin Kamel; Denis Drygin; Garth A. Kinberger; Shanti Pal Gangwar; Maria V. Yelshanskaya; John Ridley; Robert Kirby; Jesus Alvarez; Ronak Lakhia; Vishal Patel; Alexander I. Sobolevsky; Edmund C. Lee
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PKD1 and PKD2 mRNA cis-inhibition drives polycystic kidney disease progression
err2022-08-15
err27
errOAAI
errLakhia, Ronak; Ramalingam, Harini; Chang, Chun-Mien; Cobo-Stark, Patricia; Biggers, Laurence; Flaten, Andrea; Alvarez, Jesus; Valencia, Tania; Wallace, Darren P.; Lee, Edmund C.; Patel, Vishal
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Discovery and preclinical evaluation of anti-miR-17 oligonucleotide RGLS4326 for the treatment of polycystic kidney disease
err2019-09-12
err112
errOAAI
errLee, Edmund C.; Valencia, Tania; Allerson, Charles; Schairer, Annelie; Flaten, Andrea; Yheskel, Matanel; Kersjes, Kara; Li, Jian; Gatto, Sole; Takhar, Mandeep; Lockton, Steven; Pavlicek, Adam; Kim, Michael; Chu, Tiffany; Soriano, Randy; Davis, Scott; Androsavich, John R.; Sarwary, Salma; Owen, Tate; Kaplan, Julia; Liu, Kai; Jang, Graham; Neben, Steven; Bentley, Philip; Wright, Timothy; Patel, Vishal
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Lipid Nanoparticle-Mediated Delivery of Anti-miR-17 Family Oligonucleotide Suppresses Hepatocellular Carcinoma Growth
err2017-05-02
err20
errOAAI
errHuang, Xinqiang; Magnus, Jill; Kaimal, Vivek; Karmali, Priya; Li, Jian; Walls, Marlena; Prudente, Rene; Sung, Eric; Sorourian, Mehran; Lee, Robin; Davis, Scott; Yang, Xia; Estrella, Heather; Lee, Edmund C.; Chau, B. Nelson; Pavlicek, Adam; Zabludoff, Sonya
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microRNA-17 family promotes polycystic kidney disease progression through modulation of mitochondrial metabolism
err2017-02-16
err156
errOAAI
errHajarnis, Sachin; Lakhia, Ronak; Yheskel, Matanel; Williams, Darren; Sorourian, Mehran; Liu, Xueqing; Aboudehen, Karam; Zhang, Shanrong; Kersjes, Kara; Galasso, Ryan; Li, Jian; Kaimal, Vivek; Lockton, Steven; Davis, Scott; Flaten, Andrea; Johnson, Joshua A.; Holland, William L.; Kusminski, Christine M.; Scherer, Philipp E.; Harris, Peter C.; Trudel, Marie; Wallace, Darren P.; Igarashi, Peter; Lee, Edmund C.; Androsavich, John R.; Patel, Vishal
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A miR-221 multigene pharmacodynamic signature for assessing miR-221 inhibition
err2014-10-01
err0
PREAI
errPavlicek, Adam; Vincent, Thomas; Guicherit, Oivin; Chau, Nelson; Zabludoff, Sonya; Gibson, Neil; Lee, Edmund C.
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miR-221: A potential therapeutic target for hepatocellular carcinoma
err2014-10-01
err3
PREAI
errLee, Edmund C.; Xu, Jessica; Vincent, Thomas; Chen, Jie; Nelson, Michael; Huang, Xinqiang; Marcusson, Eric; Androsavich, John; Davis, Scott; Pavlicek, Adam; Gibson, Neil; Zabludoff, Sonya
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Optimization of Benzodiazepinones as Selective Inhibitors of the X-Linked Inhibitor of Apoptosis Protein (XIAP) Second Baculovirus IAP Repeat (BIR2) Domain
err2013-10-07
err52
PREAI
errKester, Robert F.; Donnell, Andrew F.; Lou, Yan; Remiszewski, Stacy W.; Lombardo, Louis J.; Chen, Shaoqing; Le, Nam T.; Lo, Jennifer; Moliterni, John A.; Han, Xiaochun; Hogg, J. Heather; Liang, Weiling; Michoud, Christophe; Rupert, Kenneth C.; Mischke, Steven; Le, Kang; Weisel, Martin; Janson, Cheryl A.; Lukacs, Christine M.; Fretland, Adrian J.; Hong, Kyoungja; Polonskaia, Ann; Gao, Lin; Li, Shirley; Solis, Dave S.; Aguilar, Doug; Tardell, Christine; Dvorozniak, Mark; Tannu, Shahid; Lee, Edmund C.; Schutt, Andy D.; Goggin, Barry
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Evaluation of the Proteasome Inhibitor MLN9708 in Preclinical Models of Human Cancer
err2010-02-28
err479
errOAAI
errKupperman, Erik; Lee, Edmund C.; Cao, Yueying; Bannerman, Bret; Fitzgerald, Michael; Berger, Allison; Yu, Jie; Yang, Yu; Hales, Paul; Bruzzese, Frank; Liu, Jane; Blank, Jonathan; Garcia, Khristofer; Tsu, Christopher; Dick, Larry; Fleming, Paul; Yu, Li; Manfredi, Mark; Rolfe, Mark; Bolen, Joe
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