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SaveIntravenous gentamicin therapy induces functional type VII collagen in patients with recessive dystrophic epidermolysis bullosa: an open-label clinical trial
Woodley, David T.; Hao, Michelle; Kwong, Andrew; Levian, Brandon; Cogan, Jon; Hou, Yingping; Mosallaei, Daniel; Kleinman, Elana; Zheng, Kate; Chung, Claire; Kim, Gene; Peng, David; Chen, Mei
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SaveMolecular and Clinical Outcomes After Intravenous Gentamicin Treatment for Patients With Junctional Epidermolysis Bullosa Caused by Nonsense Variants
Mosallaei, Daniel; Hao, Michelle; Antaya, Richard J.; Levian, Brandon; Kwong, Andrew; Cogan, Jon; Hamilton, Claire; Schwieger-Briel, Agnes; Tan, Calvin; Tang, Xin; Woodley, David T.; Chen, Mei
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