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Ex Vivo Generation of Human T-Cell Progenitors from Cord Blood CD34+Cells Can Accelerate Immune Reconstitution after Umbilical Cord Blood Transplantation in Adult Patient with Hematologic Malignancies Forcade, Edouard; Huynh, Anne; Magrin, Elisa; Diana, Jean-Sebastien; Schwartz, Eden; Aussel, Clotilde; Gabrion, Aurelie; Maulet, Axelle; Girardot, Alice; Ternaux, Brigitte; Tuchmann-Durand, Caroline; Baek, Jimni; Lhermitte, Ludovic; Touzart, Aurore; Asnafi, Vahid; Bouazza, Naim; Bauquet, Aurelie; Soheili, Shabi; Negre, Olivier; Andre, Isabelle; Treluyer, Jean-Marc; Hermine, Olivier; Cavazzana, Marina Share Save
RAC2 gain-of-function variants causing inborn error of immunity drive NLRP3 inflammasome activation Doye, Anne; Chaintreuil, Paul; Lagresle-Peyrou, Chantal; Batistic, Ludovic; Marion, Valentine; Munro, Patrick; Loubatier, Celine; Chirara, Rayana; Sorel, Natal; Bessot, Boris; Bronnec, Pauline; Contenti, Julie; Courjon, Johan; Giordanengo, Valerie; Jacquel, Arnaud; Barbry, Pascal; Couralet, Marie; Aladjidi, Nathalie; Fischer, Alain; Cavazzana, Marina; Mallebranche, Coralie; Visvikis, Orane; Kracker, Sven; Moshous, Despina; Verhoeyen, Els; Boyer, Laurent Share Save
Restoration of T and B Cell Differentiation after RAG1 Gene Transfer in Human RAG1 Defective Hematopoietic Stem Cells Sorel, Natael; Diaz-Pascual, Francisco; Bessot, Boris; Sadek, Hanem; Mollet, Chloe; Chouteau, Myriam; Zahn, Marco; Gil-Farina, Irene; Tajer, Parisa; van Eggermond, Marja; Berghuis, Dagmar; Lankester, Arjan C.; Andre, Isabelle; Gabriel, Richard; Cavazzana, Marina; Pike-Overzet, Kasrin; Staal, Frank J. T.; Lagresle-Peyrou, Chantal Share Save
Non-viral DNA delivery and TALEN editing correct the sickle cell mutation in hematopoietic stem cells Moiani, Arianna; Letort, Gil; Lizot, Sabrina; Chalumeau, Anne; Foray, Chloe; Felix, Tristan; Le Clerre, Diane; Temburni-Blake, Sonal; Hong, Patrick; Leduc, Sophie; Pinard, Noemie; Marechal, Alan; Seclen, Eduardo; Boyne, Alex; Mayer, Louisa; Hong, Robert; Pulicani, Sylvain; Galetto, Roman; Gouble, Agnes; Cavazzana, Marina; Juillerat, Alexandre; Miccio, Annarita; Duclert, Aymeric; Duchateau, Philippe; Valton, Julien Share Save
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Exagamglogene Autotemcel for Severe Sickle Cell Disease Frangoul, H.; Locatelli, F.; Sharma, A.; Bhatia, M.; Mapara, M.; Molinari, L.; Wall, D.; Liem, R. I.; Telfer, P.; Shah, A. J.; Cavazzana, M.; Corbacioglu, S.; Rondelli, D.; Meisel, R.; Dedeken, L.; Lobitz, S.; de Montalembert, M.; Steinberg, M. H.; Walters, M. C.; Eckrich, M. J.; Imren, S.; Bower, L.; Simard, C.; Zhou, W.; Xuan, F.; Morrow, P. K.; Hobbs, W. E.; Grupp, S. A. Share Save
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Umbilical Cord Blood Transplantation for Fanconi Anemia With a Special Focus on Late Complications: a Study on Behalf of Eurocord and SAAWP-EBMT Rafi, Hanadi; Volt, Fernanda; Bierings, Marc; Dalle, Jean-Hugues; Ayas, Mouhab; Rihani, Rawad; Faraci, Maura; de Simone, Giuseppina; Sengeloev, Henrik; Passweg, Jakob; Cavazzana, Marina; Costello, Regis; Maertens, Johan; Biffi, Alessandra; Johansson, Jan-Erik; Montoro, Juan; Guepin, Gabrielle Roth; Diaz, Miguel Angel; Sirvent, Anne; Kenzey, Chantal; Franco, Monica M. Rivera; Cappelli, Barbara; Scigliuolo, Graziana Maria; Rocha, Vanderson; Ruggeri, Annalisa; Risitano, Antonio; De Latour, Regis Peffault; Gluckman, Eliane Share Save
A case of T-cell acute lymphoblastic leukemia in retroviral gene therapy for ADA-SCID Cesana, Daniela; Cicalese, Maria Pia; Calabria, Andrea; Merli, Pietro; Caruso, Roberta; Volpin, Monica; Rudilosso, Laura; Migliavacca, Maddalena; Barzaghi, Federica; Fossati, Claudia; Gazzo, Francesco; Pizzi, Simone; Ciolfi, Andrea; Bruselles, Alessandro; Tucci, Francesca; Spinozzi, Giulio; Pais, Giulia; Benedicenti, Fabrizio; Barcella, Matteo; Merelli, Ivan; Gallina, Pierangela; Giannelli, Stefania; Dionisio, Francesca; Scala, Serena; Casiraghi, Miriam; Strocchio, Luisa; Vinti, Luciana; Pacillo, Lucia; Draghi, Eleonora; Cesana, Marcella; Riccardo, Sara; Colantuono, Chiara; Six, Emmanuelle; Cavazzana, Marina; Carlucci, Filippo; Schmidt, Manfred; Cancrini, Caterina; Ciceri, Fabio; Vago, Luca; Cacchiarelli, Davide; Gentner, Bernhard; Naldini, Luigi; Tartaglia, Marco; Montini, Eugenio; Locatelli, Franco; Aiuti, Alessandro Share Save
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Ovarian tissue cryopreservation for fertility preservation before hematopoietic stem cell transplantation in patients with sickle cell disease: safety, ovarian function follow-up, and results of ovarian tissue transplantation Missontsa, Mitawa Millin; Bernaudin, Francoise; Fortin, Anne; Dhedin, Nathalie; Pondarre, Corinne; Yakouben, Karima; Neven, Benedicte; Castelle, Martin; Cavazzana, Marina; Lezeau, Harry; Peycelon, Matthieu; Paye-Jaouen, Annabel; Sroussi, Jeremy; Diesch-Furlanetto, Tamara; Barraud-Lange, Virginie; Sarnacki, Sabine; Fahd, Mony; Marchand, Isis; Delcour, Clemence; Vexiau, Dominique; Arlet, Jean-Benoit; Kamdem, Annie; Arnaud, Cecile; Dalle, Jean-Hugues; Poirot, Catherine Share Save
Activated phosphoinositide 3-kinase d syndrome: Update from the ESID Registry and comparison with other autoimmune-lymphoproliferative inborn errors of immunity Maccari, Maria Elena; Wolkewitz, Martin; Schwab, Charlotte; Lorenzini, Tiziana; Leiding, Jennifer W.; Aladjdi, Nathalie; Abolhassani, Hassan; Abou-Chahla, Wadih; Aiuti, Alessandro; Azarnoush, Saba; Baris, Safa; Barlogis, Vincent; Barzaghi, Federica; Baumann, Ulrich; Bloomfield, Marketa; Bohynikova, Nadezda; Bodet, Damien; Boutboul, David; Bucciol, Giorgia; Buckland, MattheW S.; Burns, Siobhan O.; Cancrini, Caterina; Cath, Pascal; Cavazzana, Marina; Cheminant, Morgane; Chinello, Matteo; Ciznar, Peter; Coulter, Tanya I.; D'Aveni, Maud; Ekwall, Olov; Eric, Zelimir; Eren, Efrem; Fasth, Anders; Frange, Pierre; Fournier, Benjamin; Garcia-Prat, Marina; Gardembas, Martine; Geier, Christoph; Ghosh, Sujal; Goda, Vera; Hammarstrom, Lennar; Hauck, Fabian; Heeg, Maximilian; Heropolitanska-Pliszka, Edyta; Hilfanova, Anna; Jolles, Stephen; Karakoc-Aydiner, Elif; Kindle, Gerhard R.; Kiykim, Ayca; Klemann, Christian; Koletsi, Patra; Koltan, Sylwia; Kondratenko, Irina; Korholz, Julia; Kruger, Renate; Jeziorski, Eric; Levy, Romain; Le Guenno, Guillaume; Lefevre, Guillaume; Lougaris, Vassilios; Marzollo, Antonio; Mahlaoui, Nizar; Malphettes, Marion; Meinhardt, Andrea; Merlin, Etienne; Meyts, Isabelle; Milota, Tomas; Moreira, Fernando; Moshous, Despina; Mukhina, Anna; Neth, Olaf; Neubert, Jennifer; Neven, Benedicte; Nieters, Alexandra; Nove-Josserand, Raphaele; Oksenhendler, Eric; Ozen, Ahmet; Olbrich, Peter; Perlat, Antoinette; Pac, Malgorzata; Schmid, Jana Pachlopnik; Pacillo, Lucia; Parra-Martinez, Alba; Paschenko, Olga; Pellier, Isabelle; Sefer, Asena Pinar; Plebani, Alessandro; Plantaz, Dominique; Prader, Seraina; Raffray, Loic; Ritterbusch, Henrike; Riviere, Jacques G.; Rivalta, Beatrice; Rusch, Stephan; Sakovich, Inga; Savic, Sinisa; Scheible, Raphael; Schleinitz, Nicolas; Schuetz, Catharina; Schulz, Ansgar; Sediva, Anna; Semeraro, Michaela; Sharapova, Svetlana O.; Shcherbina, Anna; Slatter, Mary A.; Sogkas, Georgios; Soler-Palacin, Pere; Speckmann, Carsten; Stephan, Jean-Louis; Suarez, Felipe; Tommasini, Alberto; Truck, Johannes; Uhlmann, Annette; van Aerde, Koen J.; van Montfrans, Joris; von Bernuth, Horst; Warnatz, Klaus; Williams, Tony; Worth, Austen J. J.; Ip, Winnie; Picard, Capucine; Catherinot, Emilie; Nademi, Zohreh; Grimbacher, Bodo; Satter, Lisa R. Forbes; Kracker, Sven; Chandra, Anita; Condliffe, Alison M.; Ehl, Stephan Share Save
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Late-onset enteric virus infection associated with hepatitis (EVAH) in transplanted SCID patients Riller, Quentin; Fourgeaud, Jacques; Bruneau, Julie; De Ravin, Suk See; Smith, Grace; Fusaro, Mathieu; Meriem, Samy; Magerus, Aude; Luka, Marine; Abdessalem, Ghaith; Lhermitte, Ludovic; Jamet, Anne; Six, Emmanuelle; Magnani, Alessandra; Castelle, Martin; Levy, Romain; Lecuit, Mathilde M.; Fournier, Benjamin; Winter, Sarah; Semeraro, Michaela; Pinto, Graziella; Abid, Hanene; Mahlaoui, Nizar; Cheikh, Nathalie; Florkin, Benoit; Frange, Pierre; Jeziorski, Eric; Suarez, Felipe; Sarrot-Reynauld, Francoise; Nouar, Dalila; Debray, Dominique; Lacaille, Florence; Picard, Capucine; Perot, Philippe; Regnault, Beatrice; Da Rocha, Nicolas; de Cevins, Camille; Delage, Laure; Perot, Brieuc P.; Vinit, Angelique; Carbone, Francesco; Brunaud, Camille; Marchais, Manon; Stolzenberg, Marie-Claude; Asnafi, Vahid; Molina, Thierry; Rieux-Laucat, Frederic; Notarangelo, Luigi D.; Pittaluga, Stefania; Philippe, Jean; Moshous, Despina; Blanche, Stephane; Malech, Harry; Eloit, Marc; Cavazzana, Marina; Fischer, Alain; Menager, Mickaeeurol M.; Neven, Benedicte Share Save