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Fabry disease biomarker evaluation during a five-year gene therapy clinical trial Auray-Blais, Christiane; Lavoie, Pamela; Martineau, Tristan; Rupar, Tony; Barber, Dwayne L.; Keating, Armand; Foley, Ronan; Khan, Aneal; West, Michael L.; Medin, Jeffrey A. Share Save
Lentiviral gene therapy for Fabry disease-5 Year end of study analysis for the FACTS trial Khan, Aneal; Barber, Dwayne; Rupar, Tony; Auray-Blais, Christiane; Fraser, Graeme; Fowler, Daniel; Foley, Ronan; Keating, Armand; West, Michael L.; Medin, Jeffrey A. Share Save
Lentivirus-mediated gene therapy for Fabry disease: 5-year End-of-Study results from the Canadian FACTs trial Khan, Aneal; Barber, Dwayne L.; Mckillop, William M.; Rupar, C. Anthony; Auray-Blais, Christiane; Fraser, Graeme; Fowler, Daniel H.; Berger, Alexandra; Foley, Ronan; Keating, Armand; West, Michael L.; Medin, Jeffrey A. Share Save
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Lentivirus-mediated gene therapy for Fabry disease Khan, Aneal; Barber, Dwayne L.; Huang, Ju; Rupar, C. Anthony; Rip, Jack W.; Auray-Blais, Christiane; Boutin, Michel; O'Hoski, Pamela; Gargulak, Kristy; McKillop, William M.; Fraser, Graeme; Wasim, Syed; LeMoine, Kaye; Jelinski, Shelly; Chaudhry, Ahsan; Prokopishyn, Nicole; Morel, Chantal F.; Couban, Stephen; Duggan, Peter R.; Fowler, Daniel H.; Keating, Armand; West, Michael L.; Foley, Ronan; Medin, Jeffrey A. Share Save
FACTs Fabry gene therapy clinical trial: Two-year data Medin, Jeffrey A.; Khan, Aneal; Huang, Ju; Barber, Dwayne; Rupar, C. Anthony; Auray-Blais, Christiane; Fraser, Graeme; Fowler, Daniel H.; Keating, Armand; West, Michael L.; Foley, Ronan Share Save
Pre-Clinical Preparation and Validation of Tumor Cell-Based IL-12 Immunotherapy for Acute Myeloid Leukemia Au, Bryan C.; Liu, Yuanfeng; Huang, Ju; Nelles, Megan; Arruda, Andrea; Rothe, Michael; Paul, Gabi; Schambach, Axel; Barber, Dwayne L.; Minden, Mark D.; Paige, Christopher J.; Medin, Jeffrey A. Share Save
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Loss of JAK2 regulation via a heterodimeric VHL-SOCS1 E3 ubiquitin ligase underlies Chuvash polycythemia Russell, Ryan C.; Sufan, Roxana I.; Zhou, Bing; Heir, Pardeep; Bunda, Severa; Sybingco, Stephanie S.; Greer, Samantha N.; Roche, Olga; Heathcote, Samuel A.; Chow, Vinca W. K.; Boba, Lukasz M.; Richmond, Terri D.; Hickey, Michele M.; Barber, Dwayne L.; Cheresh, David A.; Simon, M. Celeste; Irwin, Meredith S.; Kim, William Y.; Ohh, Michael Share Save
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