Not logged in A retrospective study of isatuximab-pomalidomidedexamethasone in relapsed/refractory systemic AL amyloidosis Vohra, Sargam Rachit; Ravichandran, Sriram; Foard, Darren; Martinez-Naharro, Ana; Venneri, Lucia; Fontana, Marianna; Whelan, Carol J.; Hawkins, Philip N.; Gillmore, Julian; Lachmann, Helen J.; Mahmood, Shameem; Wechalekar, Ashutosh D. Share Save
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Transthyretin amyloid cardiomyopathy: natural history and treatment response assessed by cardiovascular magnetic resonance Patel, Rishi K.; Ioannou, Adam; Sheikh, Awais; Razvi, Yousuf; Mansell, Josephine; Martinez-Naharro, Ana; Knight, Daniel; Kotecha, Tushar; Porcari, Aldostefano; Chacko, Liza; Brown, James; Manisty, Charlotte; Moon, James C.; Lachmann, Helen J.; Wechalekar, Ashutosh; Whelan, Carol; Venneri, Lucia; Kellman, Peter; Hawkins, Philip N.; Gillmore, Julian D.; Fontana, Marianna Share Save
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Kidney Outcomes in Transthyretin Amyloid Cardiomyopathy Ioannou, Adam; Razvi, Yousuf; Porcari, Aldostefano; Rauf, Muhammad U.; Martinez-Naharro, Ana; Venneri, Lucia; Kazi, Salsabeel; Pasyar, Ali; Luxhoj, Carina M.; Petrie, Aviva; Moody, William; Steeds, Richard P.; Sperry, Brett W.; Witteles, Ronald M.; Whelan, Carol; Wechalekar, Ashutosh; Lachmann, Helen; Hawkins, Philip N.; Solomon, Scott D.; Gillmore, Julian D.; Fontana, Marianna Share Save
Recommendations for Transitioning Young People with Primary Immunodeficiency Disorders and Autoinflammatory Diseases to Adult Care Israni, Muskan; Alderson, Eliska; Mahlaoui, Nizar; Obici, Laura; Rossi-Semerano, Linda; Lachmann, Helen; Avramovic, Mojca Zajc; Guffroy, Aurelien; Dalm, Virgil; Rimmer, Rachel; Solis, Leire; Villar, Carlota; Gennery, Andrew R.; Skeffington, Stephanie; Nordin, Julia; Warnatz, Klaus; Korganow, Anne-Sophie; Anton, Jordi; Cattalini, Marco; Berg, Stefan; Soler-Palacin, Pere; Campbell, Mari; Burns, Siobhan O.; ESID Clinical Working Party, Ann; ERN RITA Transition Working Grp Consortium, Anna Share Save
Mevalonate kinase deficiency: an updated clinical overview and revision of the SHARE recommendations Lengvari, Lilla; Takacs, Kata; Lengyel, Anna; Palinkas, Annamaria; Wouters, Carine Helena; Kone-Paut, Isabelle; Kuemmerte-Deschner, Jasmin; Jeyaratnam, Jerold; Anton, Jordi; Lachmann, Helen Jane; Gattorno, Marco; Hofer, Michael; Toplak, NataSa; Weiser, Peter; Kallinich, Tilmann; Ozen, Seza; Hentgen, Veronique; Uziel, Yosef; Horvath, Zsuzsanna; Szabados, Marton; Brogan, Paul; Constantin, Tamas; Frenkel, Joost Share Save
Redefining Cardiac Involvement and Targets of Treatment in Systemic Immunoglobulin AL Amyloidosis Porcari, Aldostefano; Masi, Ambra; Martinez-Naharro, Ana; Razvi, Yousuf; Patel, Rishi; Ioannou, Adam; Rauf, Muhammad U.; Sinigiani, Giulio; Wisniowski, Brendan; Filisetti, Stefano; Currie-Cathey, Jasmine; O'Beara, Sophie; Kotecha, Tushar; Knight, Dan; Moon, James C.; Sinagra, Gianfranco; Virsinskaite, Ruta; Gilbertson, Janet; Venneri, Lucia; Petrie, Aviva; Lachmann, Helen; Whelan, Carol; Kellman, Peter; Ravichandran, Sriram; Cohen, Oliver; Mahmood, Shameem; Manisty, Charlotte; Hawkins, Philip N.; Gillmore, Julian D.; Wechalekar, Ashutosh D.; Fontana, Marianna Share Save
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Microvascular obstruction in cardiac amyloidosis Netti, Lucrezia; Ioannou, Adam; Martinez-Naharro, Ana; Razvi, Yousuf; Porcari, Aldostefano; Venneri, Lucia; Maestrini, Viviana; Knight, Dan; Virsinskaite, Ruta; Rauf, Muhammad U.; Kotecha, Tushar; Patel, Rishi K.; Wechelakar, Ashutosh; Lachmann, Helen; Kellman, Peter; Manisty, Charlotte; Moon, James; Hawkins, Philip N.; Gillmore, Julian D.; Fontana, Marianna Share Save
Refining prognostication in systemic AL amyloidosis: limited value of dFLC Khwaja, Jahanzaib; Ravichandran, Sriram; Bomsztyk, Joshua; Cohen, Oliver; Foard, Darren; Naharro, Ana; Venneri, Lucia; Fontana, Marianna; Whelan, Carol; Hawkins, Philip N.; Gillmore, Julian D.; Lachmann, Helen J.; Mahmood, Shameem; Wechalekar, Ashutosh Share Save
Expansion of the National Amyloidosis Centre staging system to detect early mortality in transthyretin cardiac amyloidosis Nitsche, Christian; Ioannou, Adam; Patel, Rishi K.; Razvi, Yousuf; Porcari, Aldostefano; Rauf, Muhammad U.; Bandera, Francesco; Aimo, Alberto; Emdin, Michele; Martinez-Naharro, Ana; Venneri, Lucia; Petrie, Aviva; Wechalekar, Ashutosh; Lachmann, Helen; Hawkins, Philip N.; Gillmore, Julian D.; Fontana, Marianna Share Save
Cardiopulmonary Exercise Testing in Evaluating Transthyretin Amyloidosis Patel, Rishi K.; Bandera, Francesco; Venneri, Lucia; Porcari, Aldostefano; Razvi, Yousuf; Ioannou, Adam; Chacko, Liza; Martinez-Naharro, Ana; Rauf, Muhammad U.; Knight, Daniel; Brown, James; Petrie, Aviva; Wechalekar, Ashutosh; Whelan, Carol; Lachmann, Helen; Muthurangu, Vivek; Guazzi, Marco; Hawkins, Philip N.; Gillmore, Julian D.; Fontana, Marianna Share Save
Multiorgan Dysfunction and Associated Prognosis in Transthyretin Cardiac Amyloidosis Ioannou, Adam; Nitsche, Christian; Porcari, Aldostefano; Patel, Rishi K.; Razvi, Yousuf; Rauf, Muhammad U.; Martinez-Naharro, Ana; Venneri, Lucia; Accietto, Antonella; Netti, Lucrezia; Bandera, Francesco; Virsinskaite, Ruta; Kotecha, Tushar; Knight, Dan; Petrie, Aviva; Whelan, Carol; Wechalekar, Ashutosh; Lachmann, Helen; Hawkins, Philip N.; Gillmore, Julian D.; Fontana, Marianna Share Save
Deep phenotyping of p.(V142I)-associated variant transthyretin amyloid cardiomyopathy: Distinct from wild-type transthyretin amyloidosis? Razvi, Yousuf; Ioannou, Adam; Patel, Rishi K.; Chacko, Liza; Karia, Nina; Riefolo, Mattia; Porcari, Aldostefano; Rauf, Muhammad Umaid; Starr, Neasa; Ganesananthan, Sashiananthan; Blakeney, Iona; Kaza, Nandita; Filisetti, Stefano; Bolhuis, Roos Eline; Rowczenio, Dorota; Gilbertson, Janet; Hutt, David; Mahmood, Shameem; Lachmann, Helen J.; Wechalekar, Ashutosh D.; Kotecha, Tushar; Knight, Daniel S.; Coghlan, John G.; Petrie, Aviva; Whelan, Carol J.; Venneri, Lucia; Martinez-Naharro, Ana; Hawkins, Phillip; Fontana, Marianna; Gillmore, Julian D. Share Save
Myocardial perfusion in cardiac amyloidosis Chacko, Liza; Kotecha, Tushar; Ioannou, Adam; Patel, Niket; Martinez-Naharro, Ana; Razvi, Yousuf; Patel, Rishi; Massa, Paolo; Venneri, Lucia; Brown, James; Porcari, Aldostefano; Knott, Kristopher; Manisty, Charlotte; Knight, Daniel; Lockie, Tim; Rakhit, Roby; Lachmann, Helen; Wechelakar, Ashutosh; Whelan, Carol; Ponticos, Markella; Moon, James; Gonzalez, Arantxa; Gilbertson, Janet; Riefolo, Mattia; Leone, Ornella; Xue, Hui; Hawkins, Philip; Kellman, Peter; Gillmore, Julian; Fontana, Marianna Share Save