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Ronald G. Crystal

weill cornell medicine

154H-index
1.1KPaper Count
8.6WCitation Count
Published Papers 274
Publication Date
Impact of population-specific pharmacogenomic variants on drug dosing in ICU patients
err2026-05-21
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errMahboubeh R. Rostami; Juan Rodriguez-Flores; Ali Ait Hssain; Alya Al Shakaki; Huda Khan; Muneera Vakayil; Edin Karic; Maha Elhamid; Lubna Gamal Al Tawil; Jason G. Mezey; Amal Robay; Ronald G. Crystal
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Twenty-Year Survival Analysis of Adeno-Associated Virus Vector Serotype 2-Mediated Gene Therapy to the Central Nervous System for CLN2 Disease
err2025-01-01
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PREAI
errSondhi, Dolan; Kaminsky, Stephen M.; Rosenberg, Jonathan B.; Rostami, Mahboubeh R.; Hackett, Neil R.; Crystal, Ronald G.
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AAVrh.10 delivery of novel APOE2-Christchurch variant suppresses amyloid and Tau pathology in Alzheimer's disease mice
err2024-12-01
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PREAI
errGuenaydin, Caner; Sondhi, Dolan; Kaminsky, Stephen M.; Lephart, Hailey C.; Leopold, Philip L.; Hackett, Neil R.; Khanna, Richie; Crystal, Ronald G.
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Angiogenic Gene Therapy for Refractory Angina: Results of the EXACT Phase 2 Trial
err2024-05-01
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errNakamura, Kenta; Henry, Timothy D.; Traverse, Jay H.; Latter, David A.; Mokadam, Nahush A.; Answini, Geoffrey A.; Williams, Adam R.; Sun, Benjamin C.; Burke, Christopher R.; Bakaeen, Faisal G.; Dicarli, Marcelo F.; Chaitman, Bernard R.; Peterson, Mark W.; Byrnes, Dawn G.; Ohman, E. Magnus; Pepine, Carl J.; Crystal, Ronald G.; Rosengart, Todd K.; Kowalewski, Elaine; Koch, Gary G.; Dittrich, Howard C.; Povsic, Thomas J.
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Management of Select Adverse Events Following Delandistrogene Moxeparvovec Gene Therapy for Patients With Duchenne Muscular Dystrophy
err2024-04-11
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errZaidman, Craig M.; Goedeker, Natalie L.; Aqul, Amal A.; Butterfield, Russell J.; Connolly, Anne M.; Crystal, Ronald G.; Godwin, Kara E.; Hor, Kan N.; Mathews, Katherine D.; Proud, Crystal M.; Smyth, Elizabeth Kula; Veerapandiyan, Aravindhan; Watkins, Paul B.; Mendell, Jerry R.
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Expression and processing of mature human frataxin after gene therapy in mice
err2024-04-10
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errRojsajjakul, Teerapat; Selvan, Nithya; De, Bishnu; Rosenberg, Jonathan B.; Kaminsky, Stephen M.; Sondhi, Dolan; Janki, Peter; Crystal, Ronald G.; Mesaros, Clementina; Khanna, Richie; Blair, Ian A.
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Serial Sampling of the Small Airway Epithelium to Identify Persistent Smoking-dysregulated Genes
err2023-10-01
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errStrulovici-Barel, Yael; Rostami, Mahboubeh R.; Kaner, Robert J.; Mezey, Jason G.; Crystal, Ronald G.
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EXACT Trial: Results of the Phase 1 Dose-Escalation Study
err2023-08-01
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errPovsic, Thomas J.; Henry, Timothy D.; Traverse, Jay H.; Anderson, R. David; Answini, Geoffrey A.; Sun, Benjamin C.; Arnaoutakis, George J.; Boudoulas, Konstantinos D.; Williams, Adam R.; Dittrich, Howard C.; Tarka, Elizabeth A.; Latter, David A.; Ohman, E. Magnus; Peterson, Mark W.; Byrnes, Dawn; Pepine, Carl J.; DiCarli, Marcelo F.; Crystal, Ronald G.; Rosengart, Todd K.; Mokadam, Nahush A.
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Gene Therapy to Treat Osteopenia Associated With Chronic Ethanol Consumption and Aldehyde Dehydrogenase 2 Deficiency
err2023-02-16
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errCamilleri, Anna E.; Cung, Michelle; Hart, Fiona M.; Pagovich, Odelya E.; Crystal, Ronald G.; Greenblatt, Matthew B.; Stiles, Katie M.
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Evaluating the state of the science for adeno-associated virus integration: An integrated perspective
err2022-08-01
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errSabatino, Denise E.; Bushman, Frederic D.; Chandler, Randy J.; Crystal, Ronald G.; Davidson, Beverly L.; Dolmetsch, Ricardo; Eggan, Kevin C.; Gao, Guangping; Gil-Farina, Irene; Kay, Mark A.; McCarty, Douglas M.; Montini, Eugenio; Ndu, Adora; Yuan, Jing
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Impaired differentiation of small airway basal stem/progenitor cells in people living with HIV
err2022-02-22
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errChung, Nancy P. Y.; Khan, K. M. Faisal; Andreoli, Mirko; Kaner, Robert J.; O'Beirne, Sarah L.; Crystal, Ronald G.
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Can gene therapy be used to prevent cancer? Gene therapy for aldehyde dehydrogenase 2 deficiency
err2021-11-19
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errMontel, Rachel A.; Munoz-Zuluaga, Carlos; Stiles, Katie M.; Crystal, Ronald G.
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Metabolic and Metabo-Clinical Signatures of Type 2 Diabetes, Obesity, Retinopathy, and Dyslipidemia
err2021-11-03
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errYousri, Noha A.; Suhre, Karsten; Yassin, Esraa; Al-Shakaki, Alya; Robay, Amal; Elshafei, Maha; Chidiac, Omar; Hunt, Steven C.; Crystal, Ronald G.; Fakhro, Khalid A.
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Epicardial delivery of XC001 gene therapy for refractory angina coronary treatment (The EXACT Trial): Rationale, design, and clinical considerations
err2021-11-01
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PREAI
errPovsic, Thomas J.; Henry, Timothy D.; Ohman, E. Magnus; Pepine, Carl J.; Crystal, Ronald G.; Rosengart, Todd K.; Reinhardt, Rickey R.; Dittrich, Howard C.; Traverse, Jay H.; Answini, Geoffrey A.; Mokadam, Nahush A.
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Gene therapy in a murine model of chronic eosinophilic leukemia-not otherwise specified (CEL-NOS)
errLEUKEMIA
IF13.4
err2021-09-20
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PREAI
errPagovich, Odelya E.; Stiles, Katie M.; Camilleri, Anna E.; Russo, Anthony R.; Nag, Saparja; Crystal, Ronald G.
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A Novel STK4 Mutation Impairs T Cell Immunity Through Dysregulation of Cytokine-Induced Adhesion and Chemotaxis Genes
err2021-08-24
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errGuennoun, Andrea; Bougarn, Salim; Khan, Taushif; Mackeh, Rafah; Rahman, Mahbuba; Al-Ali, Fatima; Ata, Manar; Aamer, Waleed; Prosser, Debra; Habib, Tanwir; Chin-Smith, Evonne; Al-Darwish, Khawla; Zhang, Qian; Al-Shakaki, Alya; Robay, Amal; Crystal, Ronald G.; Fakhro, Khalid; Al-Naimi, Amal; Al Maslamani, Eman; Tuffaha, Amjad; Janahi, Ibrahim; Janahi, Mohammad; Love, Donald R.; Karim, Mohammed Yousuf; Lo, Bernice; Hassan, Amel; Adeli, Mehdi; Marr, Nico
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Gene therapy for a murine model of eosinophilic esophagitis
err2021-05-10
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PREAI
errCamilleri, Anna E.; Nag, Saparja; Russo, Anthony R.; Stiles, Katie M.; Crystal, Ronald G.; Pagovich, Odelya E.
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Extracellular vesicles from human airway basal cells respond to cigarette smoke extract and affect vascular endothelial cells
err2021-03-17
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errSaxena, Ashish; Walters, Matthew S.; Shieh, Jae-Hung; Shen, Ling-Bo; Gomi, Kazunori; Downey, Robert J.; Crystal, Ronald G.; Moore, Malcolm A. S.
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