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In vivo selection of synthetic nucleocapsids for tissue targeting Olshefsky, Audrey; Benasutti, Halli; Sylvestre, Meilyn; Butterfield, Gabriel L.; Rocklin, Gabriel J.; Richardson, Christian; Hicks, Derrick R.; Lajoie, Marc J.; Song, Kefan; Leaf, Elizabeth; Treichel, Catherine; Decarreau, Justin; Ke, Sharon; Kher, Gargi; Carter, Lauren; Chamberlain, Jeffrey S.; Baker, David; King, Neil P.; Pun, Suzie H. Share Save
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PCYT2-regulated lipid biosynthesis is critical to muscle health and ageing (vol 5, pg 495, 2023) Cikes, Domagoj; Elsayad, Kareem; Sezgin, Erdinc; Koitai, Erika; Torma, Ferenc; Orthofer, Michael; Yarwood, Rebecca; Heinz, Leonhard X.; Sedlyarov, Vitaly; Miranda, Nasser Darwish; Taylor, Adrian; Grapentine, Sophie; Al-Murshedi, Fathiya; Abot, Anne; Weidinger, Adelheid; Kutchukian, Candice; Sanchez, Colline; Cronin, Shane J. F.; Novatchkova, Maria; Kavirayani, Anoop; Schuetz, Thomas; Haubner, Bernhard; Haas, Lisa; Hagelkruys, Astrid; Jackowski, Suzanne; Kozlov, Andrey V.; Jacquemond, Vincent; Knauf, Claude; Superti-Furga, Giulio; Rullman, Eric; Gustafsson, Thomas; McDermot, John; Lowe, Martin; Radak, Zsolt; Chamberlain, Jeffrey S.; Bakovic, Marica; Banka, Siddharth; Penninger, Josef M. Share Save
PCYT2-regulated lipid biosynthesis is critical to muscle health and ageing Cikes, Domagoj; Elsayad, Kareem; Sezgin, Erdinc; Koitai, Erika; Ferenc, Torma; Orthofer, Michael; Yarwood, Rebecca; Heinz, Leonhard X.; Sedlyarov, Vitaly; Miranda, Nasser Darwish; Taylor, Adrian; Grapentine, Sophie; al-Murshedi, Fathiya; Abot, Anne; Weidinger, Adelheid; Kutchukian, Candice; Sanchez, Colline; Cronin, Shane J. F.; Novatchkova, Maria; Kavirayani, Anoop; Schuetz, Thomas; Haubner, Bernhard; Haas, Lisa; Hagelkruys, Astrid; Jackowski, Suzanne; Kozlov, Andrey; Jacquemond, Vincent; Knauf, Claude; Superti-Furga, Giulio; Rullman, Eric; Gustafsson, Thomas; McDermot, John; Lowe, Martin; Radak, Zsolt; Chamberlain, Jeffrey S.; Bakovic, Marica; Banka, Siddharth; Penninger, Josef M. Share Save
Assessment of systemic AAV-microdystrophin gene therapy in the GRMD model of Duchenne muscular dystrophy Birch, Sharla M.; Lawlor, Michael W.; Conlon, Thomas J.; Guo, Lee-Jae; Crudele, Julie M.; Hawkins, Eleanor C.; Nghiem, Peter P.; Ahn, Mihye; Meng, Hui; Beatka, Margaret J.; Fickau, Brittany A.; Prieto, Juan C.; Styner, Martin A.; Struharik, Michael J.; Shanks, Courtney; Brown, Kristy J.; Golebiowski, Diane; Bettis, Amanda K.; Balog-Alvarez, Cynthia J.; Clement, Nathalie; Coleman, Kirsten E.; Corti, Manuela; Pan, Xiufang; Hauschka, Stephen D.; Gonzalez, J. Patrick; Morris, Carl A.; Schneider, Joel S.; Duan, Dongsheng; Chamberlain, Jeffrey S.; Byrne, Barry J.; Kornegay, Joe. N. Share Save
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Micro-dystrophin gene therapy prevents heart failure in an improved Duchenne muscular dystrophy cardiomyopathy mouse model Howard, Zachary M.; Dorn, Lisa E.; Lowe, Jeovanna; Gertzen, Megan D.; Ciccone, Pierce; Rastogi, Neha; Odom, Guy L.; Accornero, Federica; Chamberlain, Jeffrey S.; Rafael-Fortney, Jill A. Share Save
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