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Jeffrey S. Chamberlain

university of washington

87H-index
354Paper Count
2.5WCitation Count
Published Papers 141
Publication Date
Quantitative MRI Assessment of Myotoxin-Induced Skeletal Muscle Damage of mdx Mice
err2026-06-06
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errOAAI
errRavneet Vohra; Joshua Park; Feng Zhang; Jeffrey S. Chamberlain; Donghoon Lee
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Dystrophins DP71 and DP427 determine cell viability during proliferation and myofibre differentiation
err2026-04-11
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errOAAI
errSylwia Szwec; Alicja Durska; Paulina Kościelniak-Wawro; Jeffrey S. Chamberlain; Oleksandr Ostrovskyy; Karolina Dominiak; Solmaz Karimi; Patryk Konieczny
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Proteomics-based evaluation of AAV dystrophin gene therapy outcomes inmdx skeletal muscle
err2026-01-23
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PREAI
errJohnson, Erynn E.; Reyes, Theodore R.; Chamberlain, Jeffrey S.; Ervasti, James M.; Tasfaout, Hichem
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Promoting Tolerance in Myogenic Diseases
err2025-11-01
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PREAI
errFarahat, Philip K.; Villalta, S. Armando; Spangler, Jamie; Fabilane, Charina; Spencer, Melissa; Chamberlain, Jeffrey
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Genetic Strategies for Therapy of Duchenne Muscular Dystrophy
err2025-10-31
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errOAAI
errAgnieszka Łoboda; Jeffrey S. Chamberlain; Józef Dulak
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The future of gene therapy: Safer vectors, sharper focus
err2025-09-12
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PREAI
errJeffrey S. Chamberlain; Beverly L. Davidson; Lindsey A. George; Barry J. Byrne; David Barrett
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Bidirectional role of Costameres in the pathophysiology of mdx skeletal muscles
err2025-08-01
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PREAI
errBanks, Glen B.; Bisset, Darren R.; Chamberlain, Jeffrey S.
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In vivo selection of synthetic nucleocapsids for tissue targeting
err2023-11-08
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errOAAI
errOlshefsky, Audrey; Benasutti, Halli; Sylvestre, Meilyn; Butterfield, Gabriel L.; Rocklin, Gabriel J.; Richardson, Christian; Hicks, Derrick R.; Lajoie, Marc J.; Song, Kefan; Leaf, Elizabeth; Treichel, Catherine; Decarreau, Justin; Ke, Sharon; Kher, Gargi; Carter, Lauren; Chamberlain, Jeffrey S.; Baker, David; King, Neil P.; Pun, Suzie H.
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Dystrophin- and Utrophin-Based Therapeutic Approaches for Treatment of Duchenne Muscular Dystrophy: A Comparative Review
err2023-11-02
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errOAAI
errSzwec, Sylwia; Kaplucha, Zuzanna; Chamberlain, Jeffrey S.; Konieczny, Patryk
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PCYT2-regulated lipid biosynthesis is critical to muscle health and ageing (vol 5, pg 495, 2023)
err2023-04-06
err1
errOAAI
errCikes, Domagoj; Elsayad, Kareem; Sezgin, Erdinc; Koitai, Erika; Torma, Ferenc; Orthofer, Michael; Yarwood, Rebecca; Heinz, Leonhard X.; Sedlyarov, Vitaly; Miranda, Nasser Darwish; Taylor, Adrian; Grapentine, Sophie; Al-Murshedi, Fathiya; Abot, Anne; Weidinger, Adelheid; Kutchukian, Candice; Sanchez, Colline; Cronin, Shane J. F.; Novatchkova, Maria; Kavirayani, Anoop; Schuetz, Thomas; Haubner, Bernhard; Haas, Lisa; Hagelkruys, Astrid; Jackowski, Suzanne; Kozlov, Andrey V.; Jacquemond, Vincent; Knauf, Claude; Superti-Furga, Giulio; Rullman, Eric; Gustafsson, Thomas; McDermot, John; Lowe, Martin; Radak, Zsolt; Chamberlain, Jeffrey S.; Bakovic, Marica; Banka, Siddharth; Penninger, Josef M.
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PCYT2-regulated lipid biosynthesis is critical to muscle health and ageing
err2023-03-20
err14
PREAI
errCikes, Domagoj; Elsayad, Kareem; Sezgin, Erdinc; Koitai, Erika; Ferenc, Torma; Orthofer, Michael; Yarwood, Rebecca; Heinz, Leonhard X.; Sedlyarov, Vitaly; Miranda, Nasser Darwish; Taylor, Adrian; Grapentine, Sophie; al-Murshedi, Fathiya; Abot, Anne; Weidinger, Adelheid; Kutchukian, Candice; Sanchez, Colline; Cronin, Shane J. F.; Novatchkova, Maria; Kavirayani, Anoop; Schuetz, Thomas; Haubner, Bernhard; Haas, Lisa; Hagelkruys, Astrid; Jackowski, Suzanne; Kozlov, Andrey; Jacquemond, Vincent; Knauf, Claude; Superti-Furga, Giulio; Rullman, Eric; Gustafsson, Thomas; McDermot, John; Lowe, Martin; Radak, Zsolt; Chamberlain, Jeffrey S.; Bakovic, Marica; Banka, Siddharth; Penninger, Josef M.
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Assessment of systemic AAV-microdystrophin gene therapy in the GRMD model of Duchenne muscular dystrophy
err2023-01-04
err29
PREAI
errBirch, Sharla M.; Lawlor, Michael W.; Conlon, Thomas J.; Guo, Lee-Jae; Crudele, Julie M.; Hawkins, Eleanor C.; Nghiem, Peter P.; Ahn, Mihye; Meng, Hui; Beatka, Margaret J.; Fickau, Brittany A.; Prieto, Juan C.; Styner, Martin A.; Struharik, Michael J.; Shanks, Courtney; Brown, Kristy J.; Golebiowski, Diane; Bettis, Amanda K.; Balog-Alvarez, Cynthia J.; Clement, Nathalie; Coleman, Kirsten E.; Corti, Manuela; Pan, Xiufang; Hauschka, Stephen D.; Gonzalez, J. Patrick; Morris, Carl A.; Schneider, Joel S.; Duan, Dongsheng; Chamberlain, Jeffrey S.; Byrne, Barry J.; Kornegay, Joe. N.
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Comparison of dystrophin expression following gene editing and gene replacement in an aged preclinical DMD animal model
err2022-06-01
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errOAAI
errBengtsson, Niclas E.; Crudele, Julie M.; Klaiman, Jordan M.; Halbert, Christine L.; Hauschka, Stephen D.; Chamberlain, Jeffrey S.
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A Boost for Muscle with Gene Therapy
err2022-03-24
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PREAI
errChamberlain, Jeffrey S.
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Micro-dystrophin gene therapy prevents heart failure in an improved Duchenne muscular dystrophy cardiomyopathy mouse model
err2021-04-08
err19
errOAAI
errHoward, Zachary M.; Dorn, Lisa E.; Lowe, Jeovanna; Gertzen, Megan D.; Ciccone, Pierce; Rastogi, Neha; Odom, Guy L.; Accornero, Federica; Chamberlain, Jeffrey S.; Rafael-Fortney, Jill A.
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Dystrophin Gene-Editing Stability Is Dependent on Dystrophin Levels in Skeletal but Not Cardiac Muscles
err2021-03-01
err19
errOAAI
errBengtsson, Niclas E.; Tasfaout, Hichem; Hauschka, Stephen D.; Chamberlain, Jeffrey S.
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Gene Therapy Rescues Cardiac Dysfunction in Duchenne Muscular Dystrophy Mice by Elevating Cardiomyocyte Deoxy-Adenosine Triphosphate
err2019-11-01
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errOAAI
errKolwicz, Stephen C.; Hall, John K.; Moussavi-Harami, Farid; Chen, Xiolan; Hauschka, Stephen D.; Chamberlain, Jeffrey S.; Regnier, Michael; Odom, Guy L.
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Surrogate gene therapy for muscular dystrophy
err2019-10-07
err9
PREAI
errDavies, Kay E.; Chamberlain, Jeffrey S.
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