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SaveAssessment of intrathecal therapy in the treatment of familial haemophagocytic lymphohistiocytosis
Zivkovic, Katarina; Bergsten, Elisabet; Arico, Maurizio; Astigarraga, Itziar; Ishii, Eiichi; Ladisch, Stephan; Lehmberg, Kai; Minkov, Milen; Nanduri, Vasanta; Henter, Jan-inge
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SavePropionyl Carnitine Metabolic Profile: Optimizing the Newborn Screening Strategy Through Customized Cut-Offs
Tommolini, Maria Lucia; Cufaro, Maria Concetta; Valentinuzzi, Silvia; Cicalini, Ilaria; Zucchelli, Mirco; Frisco, Alberto; Simonetti, Simonetta; Perrone Donnorso, Michela; Moccia, Sara; Bucci, Ines; Arico, Maurizio; De Laurenzi, Vincenzo; Federici, Luca; Pieragostino, Damiana; Rossi, Claudia
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SaveOutcome of primary hemophagocytic lymphohistiocytosis: a report on 143 patients from the Italian Registry
Pegoraro, Francesco; Chinnici, Aurora; Beneforti, Linda; Tanturli, Michele; Trambusti, Irene; De Fusco, Carmela; Micalizzi, Concetta; Barat, Veronica; Cesaro, Simone; Gaspari, Stefania; Dell'Acqua, Fabiola; Todesco, Alessandra; Timeus, Fabio; Arico, Maurizio; Favre, Claudio; Tondo, Annalisa; Coniglio, Maria Luisa; Sieni, Elena
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SaveNoninvasive DBS-Based Approaches to Assist Clinical Diagnosis and Treatment Monitoring of Gaucher Disease
Rossi, Claudia; Ferrante, Rossella; Valentinuzzi, Silvia; Zucchelli, Mirco; Buccolini, Carlotta; Di Rado, Sara; Trotta, Daniela; Stuppia, Liborio; Federici, Luca; Arico, Maurizio
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SaveBronchiolitis 2021-2022 epidemic: multicentric analysis of the characteristics and treatment approach in 214 children from different areas in Italy
Carlone, Giorgia; Graziano, Giusi; Trotta, Daniela; Cafagno, Claudio; Arico, Melodie O.; Campodipietro, Giacomo; Marabini, Claudio; Lizzi, Mauro; Fornaro, Martina; Caselli, Desiree; Valletta, Enrico; Arico, Maurizio
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SaveSTOP Pain Project-Opioid Response in Pediatric Cancer Patients and Gene Polymorphisms of Cytokine Pathways
Crescioli, Giada; Lombardi, Niccolo; Vagnoli, Laura; Bettiol, Alessandra; Giunti, Laura; Cetica, Valentina; Coniglio, Maria Luisa; Provenzano, Aldesia; Giglio, Sabrina; Bonaiuti, Roberto; Mugelli, Alessandro; Arico, Maurizio; Messeri, Andrea; Vannacci, Alfredo; Maggini, Valentina
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SaveNeutralizing Anti-IL-17A Antibody Demonstrates Preclinical Activity Enhanced by Vinblastine in Langerhans Cell Histiocytosis
Akefeldt, Selma Olsson; Ismail, Mohamad Bachar; Belot, Alexandre; Salvatore, Giulia; Bissay, Nathalie; Gavhed, Desiree; Arico, Maurizio; Henter, Jan-Inge; Valentin, Helene; Delprat, Christine
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SaveStem cell transplantation for children with hemophagocytic lymphohistiocytosis: results from the HLH-2004 study
Bergsten, Elisabet; Horne, AnnaCarin; Myrberg, Ida Hed; Arico, Maurizio; Astigarraga, Itziar; Ishii, Eiichi; Janka, Gritta; Ladisch, Stephan; Lehmberg, Kai; McClain, Kenneth L.; Minkov, Milen; Nanduri, Vasanta; Rosso, Diego A.; Sieni, Elena; Winiarski, Jacek; Henter, Jan-Inge
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SaveOpioid response in paediatric cancer patients and the Val158Met polymorphism of the human catechol-O-methyltransferase (COMT) gene: an Italian study on 87 cancer children and a systematic review
Lucenteforte, Ersilia; Vannacci, Alfredo; Crescioli, Giada; Lombardi, Niccolo; Vagnoli, Laura; Giunti, Laura; Cetica, Valentina; Coniglio, Maria Luisa; Pugi, Alessandra; Bonaiuti, Roberto; Arico, Maurizio; Giglio, Sabrina; Messeri, Andrea; Barale, Roberto; Giovannelli, Lisa; Mugelli, Alessandro; Maggini, Valentina
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