未登录 Primary Lateral Sclerosis Natural History Study: Primary Lateral Sclerosis Functional Rating Scale and Other Outcomes Assessment 原发性侧索硬化自然史研究：原发性侧索硬化功能评分量表及其他结局评估 Lee, Ikjae; Jang, Grace; Cheung, Ying Kuen (Ken); Sherman, Alexander V.; Johnston, Wendy S.; Diaz, Frank; Fernandes, J. Americo M.; Habib, Ali A.; Maragakis, Nicholas J.; Paganoni, Sabrina; Burke, Katherine; Oskarsson, Bjorn; Shah, Jaimin; Zinman, Lorne; Floeter, Mary Kay; Ajroud-Driss, Senda; Gwathmey, Kelly; Heiman-Patterson, Terry; Jawdat, Omar; Kasarskis, Edward J.; Kisanuki, Yaz Y.; Wymer, James; Fournier, Christina; Hayat, Ghazala; Heitzman, Daragh; Lomen-Hoerth, Catherine; Pulley, Michael T.; Scelsa, Stephen N.; Walk, David; Goutman, Stephen A.; Shoesmith, Christen; Simmons, Zachary; Sorenson, Eric; Elman, Lauren; Harms, Matthew B.; Hoover, Benjamin N.; Yun, Rebecca Y.; Santella, Regina M.; Mitsumoto, Hiroshi; PLS NHS Study Grp 分享 收藏
Efficacy and Safety of Zilucoplan in Amyotrophic Lateral Sclerosis, A Randomized Clinical Trial Zilucoplan治疗肌萎缩侧索硬化症的疗效与安全性：一项随机临床试验 Paganoni, Sabrina; Fournier, Christina N.; Macklin, Eric A.; Chibnik, Lori B.; Quintana, Melanie; Saville, Benjamin R.; Detry, Michelle A.; Vestrucci, Matteo; Marion, Joe; Mcglothlin, Anna; Ajroud-Driss, Senda; Chase, Marianne; Pothier, Lindsay; Harkey, Brittney A.; Yu, Hong; Sherman, Alexander V.; Shefner, Jeremy M.; Hall, Meghan; Kittle, Gale; Berry, James D.; Babu, Suma; Andrews, Jinsy; Dagostino, Derek; Tustison, Eric; Giacomelli, Elisa; Scirocco, Erica; Alameda, Gustavo; Locatelli, Eduardo; Ho, Doreen; Quick, Adam; Katz, Jonathan; Heitzman, Daragh; Appel, Stanley H.; Shroff, Sheetal; Felice, Kevin; Maragakis, Nicholas J.; Simmons, Zachary; Miller, Timothy M.; Olney, Nicholas; Weiss, Michael D.; Goutman, Stephen A.; Fernandes, Joseph Americo; Jawdat, Omar; Owegi, Margaret Ayo; Foster, Laura A.; Vu, Tuan; Ilieva, Hristelina; Newman, Daniel S.; Arcila-Londono, Ximena; Jackson, Carlayne E.; Ladha, Shafeeq; Heiman-Patterson, Terry; Caress, James B.; Swenson, Andrea; Peltier, Amanda; Lewis, Richard; Fee, Dominic; Elliott, Matthew; Kasarskis, Edward J.; Elman, Lauren; Rosenfeld, Jeffrey; Walk, David; Mcilduff, Courtney; Twydell, Paul; Young, Eufrosina; Johnson, Kristin; Rezania, Kourosh; Goyal, Namita A.; Cohen, Jeffrey A.; Benatar, Michael; Jones, Vovanti; Glass, Jonathan; Shah, Jaimin; Beydoun, Said R.; Wymer, James P.; Zilliox, Lindsay; Nayar, Shakti; Pattee, Gary L.; Martinez-Thompson, Jennifer; Harvey, Brittany; Patel, Shital; Mahoney, Paul; Duda, Petra W.; Cudkowicz, Merit E. 分享 收藏
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Design and Statistical Innovations in a Platform Trial for Amyotrophic Lateral Sclerosis Quintana, Melanie R.; Saville, Benjamin; Vestrucci, Matteo A.; Detry, Michelle; Chibnik, Lori; Shefner, Jeremy D.; Berry, James; Chase, Marianne; Andrews, Jinsy V.; Sherman, Alexander; Yu, Hong; Drake, Kristin; Cudkowicz, Merit; Paganoni, Sabrina A.; Macklin, Eric; HEALEY ALS Platform Trial Study Grp 分享 收藏
Evidence for Survival Benefit in ALS with CNM-Au8 Treatment Across Three Study Populations Berry, James; Maragakis, Nicholas; Paganoni, Sabrina; Quintana, Melanie; Macklin, Eric; Saville, Benjamin; Andrews, Jinsy; Shefner, Jeremy; Detry, Michelle; Menon, Parvathi; Huynh, William; Mahoney, Colin; Stommel, Elijah; Hall, Meghan; Connolly, Mariah; Kittle, Gale; Chase, Marianne; Sherman, Alexander; Yu, Hong; Pothier, Lindsay; Drake, Kristin; Chibnik, Lori; Bind, Marie-Abele; Vestrucci, Matteo; Glanzman, Robert; Hotchkin, Michael; Vucic, Steve; Kiernan, Matthew; Cudkowicz, Merit 分享 收藏
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Effect of sodium phenylbutyrate/taurursodiol on tracheostomy/ventilation-free survival and hospitalisation in amyotrophic lateral sclerosis: long-term results from the CENTAUR trial Paganoni, Sabrina; Hendrix, Suzanne; Dickson, Samuel P.; Knowlton, Newman; Berry, James D.; Elliott, Michael A.; Maiser, Samuel; Karam, Chafic; Caress, James B.; Owegi, Margaret Ayo; Quick, Adam; Wymer, James; Goutman, Stephen A.; Heitzman, Daragh; Heiman-Patterson, Terry D.; Jackson, Carlayne; Quinn, Colin; Rothstein, Jeffrey D.; Kasarskis, Edward J.; Katz, Jonathan; Jenkins, Liberty; Ladha, Shafeeq S.; Miller, Timothy M.; Scelsa, Stephen N.; Vu, Tuan H.; Fournier, Christina; Johnson, Kristin M.; Swenson, Andrea; Goyal, Namita; Pattee, Gary L.; Babu, Suma; Chase, Marianne; Dagostino, Derek; Hall, Meghan; Kittle, Gale; Eydinov, Mathew; Ostrow, Joseph; Pothier, Lindsay; Randall, Rebecca; Shefner, Jeremy M.; Sherman, Alexander, V; Tustison, Eric; Vigneswaran, Prasha; Yu, Hong; Cohen, Joshua; Klee, Justin; Tanzi, Rudolph; Gilbert, Walter; Yeramian, Patrick; Cudkowicz, Merit 分享 收藏
Adaptive Platform Trials to Transform Amyotrophic Lateral Sclerosis Therapy Development Paganoni, Sabrina; Berry, James D.; Quintana, Melanie; Macklin, Eric; Saville, Benjamin R.; Detry, Michelle A.; Chase, Marianne; Sherman, Alexander, V; Yu, Hong; Drake, Kristin; Andrews, Jinsy; Shefner, Jeremy; Chibnik, Lori B.; Vestrucci, Matteo; Cudkowicz, Merit E. 分享 收藏
Investigating the Utility of Multimodal Conversational Technology and Audiovisual Analytic Measures for the Assessment and Monitoring of Amyotrophic Lateral Sclerosis at Scale Neumann, Michael; Roesler, Oliver; Liscombe, Jackson; Kothare, Hardik; Suendermann-Oeft, David; Pautler, David; Navar, Indu; Anvar, Aria; Kumm, Jochen; Norel, Raquel; Fraenkel, Ernest; Sherman, Alexander, V; Berry, James D.; Pattee, Gary L.; Wang, Jun; Green, Jordan R.; Ramanarayanan, Vikram 分享 收藏
Trial of Sodium Phenylbutyrate-Taurursodiol for Amyotrophic Lateral Sclerosis Paganoni, Sabrina; Macklin, Eric A.; Hendrix, Suzanne; Berry, James D.; Elliott, Michael A.; Maiser, Samuel; Karam, Chafic; Caress, James B.; Owegi, Margaret A.; Quick, Adam; Wymer, James; Goutman, Stephen A.; Heitzman, Daragh; Heiman-Patterson, Terry; Jackson, Carlayne E.; Quinn, Colin; Rothstein, Jeffrey D.; Kasarskis, Edward J.; Katz, Jonathan; Jenkins, Liberty; Ladha, Shafeeq; Miller, Timothy M.; Scelsa, Stephen N.; Vu, Tuan H.; Fournier, Christina N.; Glass, Jonathan D.; Johnson, Kristin M.; Swenson, Andrea; Goyal, Namita A.; Pattee, Gary L.; Andres, Patricia L.; Babu, Suma; Chase, Marianne; Dagostino, Derek; Dickson, Samuel P.; Ellison, Noel; Hall, Meghan; Hendrix, Kent; Kittle, Gale; McGovern, Michelle; Ostrow, Joseph; Pothier, Lindsay; Randall, Rebecca; Shefner, Jeremy M.; Sherman, Alexander V.; Tustison, Eric; Vigneswaran, Prasha; Walker, Jason; Yu, Hong; Chan, James; Wittes, Janet; Cohen, Joshua; Klee, Justin; Leslie, Kent; Tanzi, Rudolph E.; Gilbert, Walter; Yeramian, Patrick D.; Schoenfeld, David; Cudkowicz, Merit E. 分享 收藏
FAIR data sharing: The roles of common data elements and harmonization Kush, R. D.; Warzel, D.; Kush, M. A.; Sherman, A.; Navarro, E. A.; Fitzmartin, R.; Petavy, F.; Galvez, J.; Becnel, L. B.; Zhou, F. L.; Harmon, N.; Jauregui, B.; Jackson, T.; Hudson, L. 分享 收藏
Prospective natural history study of C9orf72 ALS clinical characteristics and biomarkers Cammack, Alexander J.; Atassi, Nazem; Hyman, Theodore; van den Berg, Leonard H.; Harms, Matthew; Baloh, Robert H.; Brown, Robert H.; van Es, Michael A.; Veldink, Jan H.; de Vries, Balint S.; Rothstein, Jeffrey D.; Drain, Caroline; Jockel-Balsarotti, Jennifer; Malcolm, Amber; Boodram, Sonia; Salter, Amber; Wightman, Nicholas; Yu, Hong; Sherman, Alexander, V; Esparza, Thomas J.; McKenna-Yasek, Diane; Owegi, Margaret A.; Douthwright, Catherine; McCampbell, Alexander; Ferguson, Toby; Cruchaga, Carlos; Cudkowicz, Merit; Miller, Timothy M. 分享 收藏
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Being PRO-ACTive: What can a Clinical Trial Database Reveal About ALS? 积极主动: 临床试验数据库能揭示关于ALS的什么？ Zach, Neta; Ennist, David L.; Taylor, Albert A.; Alon, Hagit; Sherman, Alexander; Kueffner, Robert; Walker, Jason; Sinani, Ervin; Katsovskiy, Igor; Cudkowicz, Merit; Leitner, Melanie L. 分享 收藏
The PRO-ACT database Design, initial analyses, and predictive features Atassi, Nazem; Berry, James; Shui, Amy; Zach, Neta; Sherman, Alexander; Sinani, Ervin; Walker, Jason; Katsovskiy, Igor; Schoenfeld, David; Cudkowicz, Merit; Leitner, Melanie 分享 收藏
Crowdsourced analysis of clinical trial data to predict amyotrophic lateral sclerosis progression Kueffner, Robert; Zach, Neta; Norel, Raquel; Hawe, Johann; Schoenfeld, David; Wang, Liuxia; Li, Guang; Fang, Lilly; Mackey, Lester; Hardiman, Orla; Cudkowicz, Merit; Sherman, Alexander; Ertaylan, Gokhan; Grosse-Wentrup, Moritz; Hothorn, Torsten; van Ligtenberg, Jules; Macke, Jakob H.; Meyer, Timm; Schoelkopf, Bernhard; Tran, Linh; Vaughan, Rubio; Stolovitzky, Gustavo; Leitner, Melanie L. 分享 收藏
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