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Targeting the p53 pathway to treat atypical teratoid rhabdoid tumors 靶向p53通路治疗非典型性横纹肌样瘤 Refaat, Alaa; Cho, Hyekyung P.; Williams, Justin S.; Stripay, Jennifer; Blankenship, Kaley; Mercer, Kimberly S.; De Vries, Rebekah; Connelly, Michele; Ganguly, Debolina; Robinson, Sarah; Savage, Evan; Twarog, Nathaniel R.; Attery, Ayush; Laha, Dipranjan; Yu, Kaiwen; Poudel, Suresh; Dhanda, Sandeep K.; Stewart, Clinton F.; Freeman, Burgess B.; Roberts, Charles W. M.; Tinkle, Christopher; Stewart, Elizabeth A.; Upadhyaya, Santhosh A.; Shelat, Anang A.; Roussel, Martine F. 分享 收藏
Molecular insights into response and resistance in children with relapsed/refractory brain tumors on ribociclib combination therapy: results from SJDAWN 关于接受ribociclib联合疗法治疗的复发/难治性脑瘤患儿的应答与耐药性的分子机制研究:SJDAWN研究的结果 Han, Katie; Robinson, Giles W.; Smith, Kyle S.; Kostecka, Anna; Dhanda, Sandeep K.; Lin, Tong; Filipovic, David; Lin, Hong; Mikkelsen, Margit; Sabin, Noah D.; Onar-Thomas, Arzu; Roussel, Martine F.; Stewart, Clinton; Orr, Brent A.; Gajjar, Amar; Northcott, Paul A. 分享 收藏
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Comparison of GFR estimation equations using creatinine, cystatin C, and their combination in pediatric hematology-oncology: no single equation is superior across subgroups 使用肌酐、胱抑素C及其组合估算GFR方程在儿科血液肿瘤学中的比较:没有单一方程在所有亚组中均具有优势 Phillips, Katelyn J.; Sun, Yilun; Tang, Li; Pappas, Andrew; Cross, Shane J.; Pauley, Jennifer L.; Mccormick, John; Molinelli, Alejandro R.; Bissler, John J.; Christensen, Anthony M.; Stewart, Clinton F. 分享 收藏
A phase 2 PBTC study of selumetinib for recurrent/progressive pediatric low-grade glioma: Strata 2, 5, and 6 with long-term outcomes on strata 1, 3, and 4 一项关于selumetinib治疗复发性/进展性儿童低级别胶质瘤的PBTC二期研究:Strata 2、5和6,以及Strata 1、3和4的长期结局。 Fangusaro, Jason; Onar-Thomas, Arzu; Young Poussaint, Tina; Lensing, Shelly; Ligon, Azra H.; Lindeman, Neal; Banerjee, Anuradha; Kilburn, Lindsay B.; Lenzen, Alicia; Pillay-Smiley, Natasha; Pollack, Ian F.; Robison, Nathan J.; Partap, Sonia; Qaddoumi, Ibrahim; Landi, Daniel; Jones, David T. W.; Stewart, Clinton F.; Fouladi, Maryam; Dunkel, Ira J. 分享 收藏
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MOLECULAR AND BIOLOGY CORRELATIVE RESULTS FROM THE PHASE 1B TRIAL OF UNESBULIN (PTC596) WITH RADIOTHERAPY IN CHILDREN NEWLY-DIAGNOSED WITH DIFFUSE INTRINSIC PONTINE GLIOMA (DIPG) AND HIGH-GRADE GLIOMA (HGG): A REPORT FROM THE COLLABORATIVE NETWORK FOR NEURO-ONCOLOGY CLINICAL TRIALS (CONNECT) Lazow, Margot; Baxter, Patricia; Kumar, Shiva Senthil; Mohamad, Maya; Mackay, Alan; Stanek, Joseph; Rodriguez, Diana; Palmer, Joshua; Leach, James; Mikael, Leonie; Thomas, Diana; Fuller, Christine; Boue, Daniel; Pierson, Christopher; Breneman, John; Li, Xiao-Nan; Salloum, Ralph; Ashley, David; de Blank, Peter; Hwang, Eugene; Leary, Sarah; Plant, Ashley; Fisher, Michael; Chi, Susan; Murala, Mythili; Weetall, Marla; Rance, Mark; Baird, John; D'Silva, Dhiren; O'Keefe, Kylie; Leonard, Jeffrey; Stewart, Clinton; Jones, Chris; Mardis, Elaine; Fouladi, Maryam; Drissi, Rachid 分享 收藏
Entinostat as a combinatorial therapeutic for rhabdomyosarcoma Chauhan, Shefali; Lian, Emily; Habib, Iman; Liu, Qianqian; Anders, Nicole M.; Bugg, Megan M.; Federman, Noah C.; Reid, Joel M.; Stewart, Clinton F.; Cates, Tristan; Michalek, Joel E.; Keller, Charles 分享 收藏
REPORT ON PEDIATRIC BRAIN TUMOR CONSORTIUM (PBTC)-029B, A PROSPECTIVE PHASE 2 CLINICAL TRIAL OF SELUMETINIB IN TREATING YOUNG PATIENTS WITH RECURRENT/PROGRESSIVE LOW-GRADE GLIOMA: NEW RESULTS ON STRATA 2, 5, AND 6 WITH UPDATED LONG-TERM SURVIVAL OUTCOMES ON STRATA 1, 3, AND 4 Fangusaro, Jason; Onar-Thomas, Arzu; Poussaint, Tina Young; Lensing, Shelly; Ligon, Azra H.; Lindeman, Neal; Banerjee, Anuradha; Kilburn, Lindsay; Lenzen, Alicia; Pillay-Smiley, Natasha; Pollack, Ian F.; Robison, Nathan; Partap, Sonia; Qaddoumi, Ibrahim; Landi, Daniel; Jones, David T. W.; Stewart, Clinton F.; Fouladi, Maryam; Dunkel, Ira J. 分享 收藏
PEDIATRIC BRAIN TUMOR CONSORTIUM (PBTC)-056: A PHASE 1 STUDY OF THE ADAM-10 INHIBITOR, INCB007839, IN CHILDREN WITH RECURRENT/PROGRESSIVE HIGH-GRADE GLIOMAS TO TARGET MICROENVIRONMENTAL NEUROLOGIN-3 Lenzen, Alicia; Partap, Sonia; Billups, Catherine; Poussaint, Tina Young; Sait, Sameer Farouk; Robison, Nathan; Castellino, Craig C.; Felker, James; Stewart, Clinton; Fangusaro, Jason; Onar-Thomas, Arzu; Dunkel, Ira J.; Warren, Katherine E.; Monje, Michelle 分享 收藏
RESULTS FROM THE SJ-ELIOT PHASE 1 CLINICAL TRIAL EVALUATING PREXASERTIB (LY2606368) IN COMBINATION WITH CYCLOPHOSPHAMIDE OR GEMCITABINE FOR CHILDREN AND ADOLESCENTS WITH REFRACTORY OR RECURRENT MEDULLOBLASTOMA Gottardo, Nicholas G.; Endersby, Raelene; Billups, Catherine; Orr, Brent; Hansford, Jordan R.; Hassall, Tim; Zielgler, David S.; Stewart, Clinton; Onar-Thomas, Arzu; Clarke, Molly; Roussel, Martine F.; Gajjar, Amar; Robinson, Giles W. 分享 收藏
RESULTS FROM SJDAWN: A ST JUDE CHILDREN'S RESEARCH HOSPITAL PHASE 1 STUDY EVALUATING MOLECULARLY DRIVEN DOUBLET THERAPIES FOR ALL CHILDREN WITH REFRACTORY OR RECURRENT CENTRAL NERVOUS SYSTEM (CNS) MALIGNANT NEOPLASMS AND YOUNG ADULTS WITH SHH MEDULLOBLASTOMA Robinson, Giles W.; Orr, Brent A.; Dhanda, Sandeep K.; Lin, Tong; Sabin, Noah D.; Han, Katie; Kostecka, Anna; Onar-Thomas, Arzu; Roussel, Martine F.; Stewart, Clinton; Gajjar, Amar; Northcott, Paul A. 分享 收藏
Population pharmacokinetics of methotrexate and 7-hydroxymethotrexate and delayed excretion in infants and young children with brain tumors Campagne, Olivia; Huang, Jie; Lin, Tong; Reddick, Wilburn E.; Selvo, Nicholas S.; Onar-Thomas, Arzu; Ward, Deborah; Robinson, Giles; Gajjar, Amar; Stewart, Clinton F. 分享 收藏
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Non-chemotherapy adjuvant agents in TP53 mutant Ewing sarcoma Kim, Jin-Ah; Crawford, Kenneth A.; Spada, Piero A.; Martin, Leah R.; Zhang, Jiaqi; Wong, Rain; Reid, Joel M.; Stewart, Clinton F.; Frank, Timothy M.; Liu, Qianqian; Michalek, Joel E.; Keller, Charles 分享 收藏
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A PHASE 1 STUDY OF SAVOLITINIB IN RECURRENT, PROGRESSIVE, OR REFRACTORY MEDULLOBLASTOMA, HIGH-GRADE GLIOMA, DIFFUSE INTRINSIC PONTINE GLIOMA, AND CENTRAL NERVOUS SYSTEM (CNS) TUMORS HARBORING MET ABERRATIONS: A PEDIATRIC BRAIN TUMOR CONSORTIUM TRIAL Salloum, Ralph; Huang, Jie; Stewart, Clinton F.; Fuller, Christine; Smolarek, Teresa; Lenzen, Alicia; Waanders, Angela J.; Baxter, Patiricia; Lindsay, Holly; Robison, Nathan; Pillay-Smiley, Natasha; Partap, Sonia; Fangusaro, Jason; Onar-Thomas, Arzu; Fouladi, Maryam; Dunkel, Ira J. 分享 收藏
UPDATED FINDINGS FROM THE PHASE IB STUDY OF UNESBULIN (PTC596) IN CHILDREN WITH NEWLY-DIAGNOSED DIFFUSE INTRINSIC PONTINE GLIOMA (DIPG) AND HIGH-GRADE GLIOMA (HGG): A REPORT FROM THE COLLABORATIVE NETWORK FOR NEURO-ONCOLOGY CLINICAL TRIALS (CONNECT) 新诊断的弥漫性内在性脑桥胶质瘤 (DIPG) 和高级别胶质瘤 (HGG) 儿童UNESBULIN (PTC596) IB期研究的最新发现: 来自神经肿瘤学临床试验合作网络 (CONNECT) 的报告 Lazow, Margot; Baxter, Patricia; Stanek, Joseph; Rodriguez, Diana; Kumar, Shiva Senthil; Palmer, Joshua; Leach, James; Mikael, Leonie; Thomas, Diana; Fuller, Christine; Boue, Daniel; Pierson, Christopher; Breneman, John; Li, Xiao-Nan; Salloum, Ralph; Ashley, David; De Blank, Peter; Hwang, Eugene; Leary, Sarah; Plant, Ashley; Fisher, Michael; Chi, Susan; Crabtree, Dorothy; Murali, Mythili; Weetall, Marla; Rance, Mark; Maliakal, Pius; Baird, John; D'Silva, Dhiren; O'Keefe, Kylie; Leonard, Jeffrey; Stewart, Clinton; Mardis, Elaine; Fouladi, Maryam; Drissi, Rachid 分享 收藏
Genetic susceptibility to cognitive decline following craniospinal irradiation for pediatric central nervous system tumors 小儿中枢神经系统肿瘤颅脊髓照射后认知功能下降的遗传易感性 Brown, Austin L.; Sok, Pagna; Raghubar, Kimberly P.; Lupo, Philip J.; Richard, Melissa A.; Morrison, Alanna C.; Yang, Jun J.; Stewart, Clinton F.; Okcu, Mehmet Fatih; Chintagumpala, Murali M.; Gajjar, Amar; Kahalley, Lisa S.; Conklin, Heather; Scheurer, Michael E. 分享 收藏