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Laura Obici

amyloidosis research and treatment center

74H指数
400论文数
2.0W被引数
收录论文 158
发表时间
Impact of Baseline Polyneuropathy Severity on Eplontersen Efficacy in the NEURO-TTRansform Clinical Trial基线周围神经病变严重程度对NEURO-TTRansform临床试验中Eplontersen疗效的影响
err2026-10-08
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errOAAI
errThomas H. Brannagan III; Markus Weiler; Márcia Waddington Cruz; Sami Khella; John L. Berk; Morie Gertz; Ahmad Masri; Mathew S. Maurer; Jonas Wixner; Jonatan Nåtman; T. Jesse Kwoh; Maksym Pola; Laura Obici
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Eplontersen with and without background transthyretin stabilizers in transthyretin amyloid cardiomyopathy: secondary analysis of a phase 3, randomized controlled trialEplontersen与无背景甲状腺素转运蛋白稳定剂的甲状腺素转运蛋白淀粉样变性心肌病:一项3期、随机对照试验的二次分析
err2026-08-30
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errOAAI
errPablo García-Pavía; Francesco Cappelli; Margot K. Davis; Marianna Fontana; Julian D. Gillmore; Mazen Hanna; Ahmad Masri; Laura Obici; Scott D. Solomon; Brett W. Sperry; Nobuhiro Tahara; Márcia Waddington-Cruz; Kurt Boman; Sarah A. M. Cuddy; Philippe Debonnaire; Nowell M. Fine; Piotr Podolec; Ali Yilmaz; Tom Conrad; Qingqing Yang; Brian L. Claggett; Jersey Chen; Sotirios Tsimikas; Mathew S. Maurer
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Guidelines for the management of hereditary ATTR amyloidosis 20262026年遗传性ATTR淀粉样变性管理指南
err2026-07-09
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PREAI
errYoshiki Sekijima; Mitsuharu Ueda; John L. Berk; Laura Obici; Ronald M. Witteles; Violaine Planté-Bordeneuve; Markus Weiler; Marianna Fontana; Márcia Waddington Cruz; Teresa Coelho; Bo-Göran Ericzon; Pablo Garcia-Pavia; João Beirão; Jonas Wixner; Luísa Lobato; Yukio Ando; Giampaolo Merlini; Mathew S. Maurer
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Long-term efficacy and safety of vutrisiran in hereditary transthyretin amyloidosis with polyneuropathy: final analysis of the HELIOS-A randomized treatment extension在伴有周围神经病的遗传性甲状腺素转运蛋白淀粉样变性中vutrisiran的长期疗效与安全性:HELIOS-A随机治疗扩展的最终分析
err2026-06-15
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errCécile Cauquil; David Adams; Julian Gillmore; Alejandra Gonzalez-Duarte; Michelle Mezei; Laura Obici; Yoshiki Sekijima; Weizhi Zhao; Katherine Boyle; Prajakta Badri; Marianne Sweetser; Colleen Moffitt; Márcia Waddington-Cruz
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Cascade genetic screening in families with hereditary transthyretin amyloidosis: diagnostic and prognostic impact家族性遗传性甲状腺素转运蛋白淀粉样变性中的级联遗传筛查:诊断与预后影响
err2026-04-07
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errOAAI
errFrancesco Cappelli; Carlo Fumagalli; Marco Luigetti; Roberta Mussinelli; Simone Longhi; Pietro Guaraldi; Alberto Aimo; Alessia Argirò; Alessandro Barilaro; Elena Biagini; Giulia Biagioni; Marco Ceccanti; Alberto Cipriani; Cristina Chimenti; Laura De Michieli; Gianluca Di Bella; Michele Emdin; Francesca Graziani; Massimo Imazio; Giuseppe Limongelli; Carla Lofiego; Francesco Musca; Paolo Ossola; Mario Nuvolone; Stefano Perlini; Maurizio Pieroni; Aldostefano Porcari; Beatrice Musumeci; Giuseppe Palmiero; Federico Perfetto; Irene Ruotolo; Massimo Russo; Giacomo Tini; Giuseppe Vergaro; Fabio Vagnarelli; Federica Verrillo; Maria Ausilia Sciarrone; Alessandro Salvalaggio; Mattia Zampieri; Carlotta Mazzoni; Gianfranco Sinagra; Giovanni Palladini; Marco Merlo; Laura Obici; null
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A plain language review of the ATTRibute-CM study: efficacy and safety of acoramidis in transthyretin amyloid cardiomyopathyATTRibute-CM研究的通俗语言综述:acoramidis治疗转甲状腺素蛋白淀粉样变性心肌病的有效性与安全性
err2025-12-01
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PREAI
errGillmore, Julian D.; Judge, Daniel P.; Cappelli, Francesco; Fontana, Marianna; Garcia-Pavia, Pablo; Gibbs, Simon; Grogan, Martha; Hanna, Mazen; Hoffman, James; Masri, Ahmad; Maurer, Mathew S.; Nativi-Nicolau, Jose; Obici, Laura; Poulsen, Steen Hvitfeldt; Rockhold, Frank; Shah, Keyur B.; Soman, Prem; Garg, Jyotsna; Chiswell, Karen; Xu, Haolin; Cao, Xiaofan; Lystig, Ted; Sinha, Uma; Fox, Jonathan C.
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Left ventriculo-arterial coupling in a contemporary cohort of patients with wild-type transthyretin cardiac amyloidosis treated with tafamidis野生型转甲状腺素蛋白心脏淀粉样变性患者当代队列的左心室-动脉耦联,经塔夫胺司治疗
err2025-11-03
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errOAAI
errGiuseppe Damiano Sanna; Valeria Anna Di Simone; Paolo Milani; Alessandro Fogliani; Roberta Mussinelli; Gianluigi Guida; Andrea Attanasio; Laura Obici; Marco Basset; Martina Nanci; Andrea Foli; Gavino Casu; Leonardo De Luca; Mario Nuvolone; Giampaolo Merlini; Stefano Perlini; Giovanni Palladini
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Effect of Acoramidis on Recurrent and Cumulative Cardiovascular Outcomes in ATTR-CM: Exploratory Analysis from ATTRibute-CMAcoramidis对ATTR-CM中复发性及累积心血管结局的影响:ATTRibute-CM研究的探索性分析
errJACC
IF0
err2025-09-28
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errOAAI
errAhmad Masri; Daniel P. Judge; Frederick L. Ruberg; Julian D. Gillmore; Justin L. Grodin; Laura Obici; Mathew S. Maurer; Marianna Fontana; Steen Hvitfeldt Poulsen; Peter van der Meer; Richard K. Cheng; Sarah A.M. Cuddy; Amrut V. Ambardekar; Kuangnan Xiong; Xiaofan Cao; Gillian Murtagh; Suresh Siddhanti; Adam Castaño; Jean-François Tamby; Jonathan C. Fox; Kevin M. Alexander; Ronald Witteles
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Role of extracellular space and matrix remodeling in cardiac amyloidosis细胞外空间和基质重塑在心脏淀粉样变性中的作用
err2025-07-14
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errOAAI
errFrancesca Lavatelli; Loredana Marchese; Palma Patrizia Mangione; Sara Raimondi; Diana Canetti; Guglielmo Verona; Lucia Venneri; Eloisa Arbustini; Laura Obici; Alessandra Corazza; Vittorio Bellotti; Sofia Giorgetti
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Change in prevalence of ATTR variants in Italy: results from a national surveyFumagalli, C.; Longhi, S.; Aimo, A.; Argirò, A.; Barilaro, A.; Biagini, E.; Biagioni, G.; Ceccanti, M.; Cipriani, A.; Chimenti, C.; 等. 意大利ATTR变异患病率的变化——全国调查结果. Eur. Heart J. Qual. Care Clin. Outcomes. 2025, qcaf024. [Google Scholar] [CrossRef]
err2025-05-01
err7
PREAI
errFumagalli, Carlo; Longhi, Simone; Aimo, Alberto; Argiro, Alessia; Barilaro, Alessandro; Biagini, Elena; Biagioni, Giulia; Ceccanti, Marco; Cipriani, Alberto; Chimenti, Cristina; De Michieli, Laura; Di Bella, Gianluca; Emdin, Michele; Graziani, Francesca; Guaraldi, Pietro; Imazio, Massimo; Limongelli, Giuseppe; Lofiego, Carla; Luigetti, Marco; Marazia, Stefania; My, Filomena; Musca, Francesco; Ossola, Paolo; Palladini, Giovanni; Perlini, Stefano; Porcari, Aldostefano; Mussinelli, Roberta; Musumeci, Beatrice; Palmiero, Giuseppe; Perfetto, Federico; Russo, Massimo; Tini, Giacomo; Vergaro, Giuseppe; Vagnarelli, Fabio; Verrillo, Federica; Varra, Guerino Giuseppe; Sciarrone, Maria Ausilia; Sinagra, Gianfranco; Merlo, Marco; Obici, Laura; Cappelli, Francesco
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Efficacy of Acoramidis on All-Cause Mortality and Cardiovascular Hospitalization in Transthyretin Amyloid Cardiomyopathy阿卡拉米定对转甲状腺素蛋白淀粉样变性心肌病全因死亡率和心血管住院的疗效
err2025-03-01
err1
errOAAI
errJudge, Daniel P.; Alexander, Kevin M.; Cappelli, Francesco; Fontana, Marianna; Garcia-Pavia, Pablo; Gibbs, Simon D. J.; Grogan, Martha; Hanna, Mazen; Masri, Ahmad; Maurer, Mathew S.; Obici, Laura; Soman, Prem; Cao, Xiaofan; Lystig, Ted; Tamby, Jean-Francois; Siddhanti, Suresh; Castano, Adam; Katz, Leonid; Fox, Jonathan C.; Mahaffey, Kenneth W.; Gillmore, Julian D.
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Five-Year Results With Patisiran for Hereditary Transthyretin Amyloidosis With Polyneuropathy帕斯利伦治疗遗传性转甲状腺素蛋白淀粉样变性伴多发性神经病变的五年结果
err2025-01-13
err1
PREAI
errAdams, David; Wixner, Jonas; Polydefkis, Michael; Berk, John L.; Conceicao, Isabel M.; Dispenzieri, Angela; Peltier, Amanda; Ueda, Mitsuharu; Bender, Shaun; Capocelli, Kelley; Jay, Patrick Y.; Yureneva, Elena; Obici, Laura; Patisiran Global OLE Study Grp
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Predictors of Early Death in Patients With Wild-Type Transthyretin Cardiac Amyloidosis
err2025-01-07
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errMilani, Paolo; Sanna, Giuseppe Damiano; Mussinelli, Roberta; Basset, Marco; Guida, Gianluigi; Attanasio, Andrea; Nanci, Martina; Fabris, Francesca; Bellofiore, Claudia; Fogliani, Alessandro; Novello, Elisa; Benigna, Francesca; Obici, Laura; Benvenuti, Pietro; Ciardo, Martina; Nuvolone, Mario; Averaimo, Manuela; Casu, Gavino; Foli, Andrea; Perlini, Stefano; Merlini, Giampaolo; Palladini, Giovanni
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Recommendations for Transitioning Young People with Primary Immunodeficiency Disorders and Autoinflammatory Diseases to Adult Care将患有原发性免疫缺陷病和自身炎症性疾病的年轻人转变为成人护理的建议
err2024-12-17
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errOAAI
errIsrani, Muskan; Alderson, Eliska; Mahlaoui, Nizar; Obici, Laura; Rossi-Semerano, Linda; Lachmann, Helen; Avramovic, Mojca Zajc; Guffroy, Aurelien; Dalm, Virgil; Rimmer, Rachel; Solis, Leire; Villar, Carlota; Gennery, Andrew R.; Skeffington, Stephanie; Nordin, Julia; Warnatz, Klaus; Korganow, Anne-Sophie; Anton, Jordi; Cattalini, Marco; Berg, Stefan; Soler-Palacin, Pere; Campbell, Mari; Burns, Siobhan O.; ESID Clinical Working Party, Ann; ERN RITA Transition Working Grp Consortium, Anna
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Neurohormonal therapies at baseline and follow-up and survival in patients with wild-type transthyretin cardiac amyloidosis基线及随访时的神经激素疗法与野生型甲状腺素运载蛋白心脏淀粉样变性患者的生存情况
err2024-11-12
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PREAI
errAimo, Alberto; Tini, Giacomo; Vergaro, Giuseppe; Milani, Paolo; Zampieri, Mattia; Caponetti, Angelo; Fabris, Francesca; Foli, Andrea; Mazzoni, Carlotta; Gagliardi, Christian; Longhi, Simone; Saturi, Giulia; Serenelli, Matteo; Fabbri, Gioele; De Michieli, Laura; Palmiero, Giuseppe; Ciliberti, Giuseppe; Carigi, Samuela; Mandoli, Giulia; Rella, Valeria; Mussinelli, Roberta; Cameli, Matteo; Marzo, Francesca; Limongelli, Giuseppe; Cipriani, Alberto; Perlini, Stefano; Obici, Laura; Perfetto, Federico; Sinagra, Gianfranco; Merlo, Marco; Musumeci, Beatrice; Biagini, Elena; Cappelli, Francesco; Palladini, Giovanni; Emdin, Michele; Canepa, Marco
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Evolution over time of cardiac biomarkers, electrocardiographic and echocardiographic features in a large cohort of patients with wild-type transthyretin cardiac amyloidosis treated with tafamidis
err2024-10-28
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PREAI
errSanna, G.; Milani, P.; Fogliani, A.; Guida, G.; Attanasio, A.; Foli, A.; Basset, M.; Nanci, M.; Mussinelli, R.; Obici, L.; Nuvolone, M.; Perlini, S.; Casu, G.; Merlini, G.; Palladini, G.
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AA amyloidosis: An uncommon case presenting with a polyneuropathy
err2024-10-01
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PREAI
errSciarrone, Maria Ausilia; Vitali, Francesca; Romano, Angela; Gremese, Elisa; Bruno, Dario; Obici, Laura; Luigetti, Marco
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