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收藏Engineering a photoactivatable A-to-I RNA base editor for gene therapy in vivo工程化构建一种适用于体内基因治疗的A-to-I光激活RNA碱基编辑器
Li, Huiying; Qiu, Yuhao; Song, Bowen; Quan, Xinyi; Zhang, Dan; Li, Xinru; Yang, Jingyun; Liu, Xiaohong; Zeng, Zhiyang; Jing, Ji; Yin, Shuming; Dai, Qi; Wang, Liren; Han, Honghui; Ye, Haifeng; Sun, Zhenliang; Cheng, Yiyun; Zhang, Xueli; Du, Bing
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收藏Amelioration of metabolic and behavioral defects through base editing in the PahR408W phenylketonuria mouse model通过碱基编辑改善苯丙酮尿症PahR408W小鼠模型的代谢和行为缺陷
Yin, Shuming; Gao, Liangcai; Sun, Xiaoyue; Zhang, Mei; Gao, Hongyi; Chen, Xiaoqing; Zhang, Dan; Ming, Xinyu; Yang, Lei; Hu, Yaqiang; Chen, Xi; Liu, Meizhen; Zhan, Xia; Guan, Yuting; Wang, Liren; Han, Lianshu; Zhu, Ping; Li, Dali
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收藏Engineering IscB to develop highly efficient miniature editing tools in mammalian cells and embryos
Xue, Niannian; Hong, Dishan; Zhang, Dan; Wang, Qian; Zhang, Shun; Yang, Lei; Chen, Xi; Li, Yongmei; Han, Honghui; Hu, Chunyi; Liu, Mingyao; Song, Gaojie; Guan, Yuting; Wang, Liren; Zhu, Yifan; Li, Dali
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收藏Engineering APOBEC3A deaminase for highly accurate and efficient base editing
Yang, Lei; Huo, Yanan; Wang, Man; Zhang, Dan; Zhang, Tianai; Wu, Hao; Rao, Xichen; Meng, Haowei; Yin, Shuming; Mei, Jiale; Zhang, Dexin; Chen, Xi; Lv, Jia; Liu, Meizhen; Cheng, Yiyun; Guan, Yuting; Feng, Bo; Song, Gaojie; Yi, Chengqi; Liu, Mingyao; Zeng, Fanyi; Wang, Liren; Li, Dali
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收藏Feedback activation of EGFR/wild-type RAS signaling axis limits KRASG12D inhibitor efficacy in KRASG12D-mutated colorectal cancer
Feng, Juanjuan; Hu, Zhongwei; Xia, Xinting; Liu, Xiaogu; Lian, Zhengke; Wang, Hui; Wang, Liren; Wang, Cun; Zhang, Xueli; Pang, Xiufeng
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收藏Gain-of-function variants in SYK cause immune dysregulation and systemic inflammation in humans and mice
Wang, Lin; Aschenbrenner, Dominik; Zeng, Zhiyang; Cao, Xiya; Mayr, Daniel; Mehta, Meera; Capitani, Melania; Warner, Neil; Pan, Jie; Wang, Liren; Li, Qi; Zuo, Tao; Cohen-Kedar, Sarit; Lu, Jiawei; Ardy, Rico Chandra; Mulder, Daniel J.; Dissanayake, Dilan; Peng, Kaiyue; Huang, Zhiheng; Li, Xiaoqin; Wang, Yuesheng; Wang, Xiaobing; Li, Shuchao; Bullers, Samuel; Gammage, Anis N.; Warnatz, Klaus; Schiefer, Ana-Iris; Krivan, Gergely; Goda, Vera; Kahr, Walter H. A.; Lemaire, Mathieu; Lu, Chien-Yi; Siddiqui, Iram; Surette, Michael G.; Kotlarz, Daniel; Engelhardt, Karin R.; Griffin, Helen R.; Rottapel, Robert; Decaluwe, Helene; Laxer, Ronald M.; Proietti, Michele; Hambleton, Sophie; Elcombe, Suzanne; Guo, Cong-Hui; Grimbacher, Bodo; Dotan, Iris; Ng, Siew C.; Freeman, Spencer A.; Snapper, Scott B.; Klein, Christoph; Boztug, Kaan; Huang, Ying; Li, Dali; Uhlig, Holm H.; Muise, Aleixo M.
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收藏Knockdown of lactate dehydrogenase by adeno-associated virus-delivered CRISPR/Cas9 system alleviates primary hyperoxaluria type 1
Zheng, Rui; Fang, Xiaoliang; Chen, Xi; Huang, Yunteng; Xu, Guofeng; He, Lei; Li, Yueyan; Niu, Xuran; Yang, Lei; Wang, Liren; Li, Dali; Geng, Hongquan
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