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Interneuron-specific dual-AAV SCN1A gene replacement corrects epileptic phenotypes in mouse models of Dravet syndrome 神经元特异性的双AAV SCN1A基因替换纠正了Dravet综合征小鼠模型的癫痫表型 Mich, John K.; Ryu, Jiyun; Wei, Aguan D.; Gore, Bryan B.; Guo, Rong; Bard, Angela M.; Martinez, Refugio A.; Luber, Emily M.; Liu, Jiatai; Bishaw, Yemeserach M.; Christian, Robert J.; Oliveira, Luiz M.; Miranda, Nicole; Ramirez, Jan-Marino; Ting, Jonathan T.; Lein, Ed S.; Levi, Boaz P. 分享 收藏
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Adeno-associated viral vectors for functional intravenous gene transfer throughout the non-human primate brain Chuapoco, Miguel R.; Flytzanis, Nicholas C.; Goeden, Nick; Octeau, J. Christopher; Roxas, Kristina M.; Chan, Ken Y.; Scherrer, Jon; Winchester, Janet; Blackburn, Roy J.; Campos, Lillian J.; Man, Kwun Nok Mimi; Sun, Junqing; Chen, Xinhong; Lefevre, Arthur; Singh, Vikram Pal; Arokiaraj, Cynthia M.; Shay, Timothy F.; Vendemiatti, Julia; Jang, Min J.; Mich, John K.; Bishaw, Yemeserach; Gore, Bryan B.; Omstead, Victoria; Taskin, Naz; Weed, Natalie; Levi, Boaz P.; Ting, Jonathan T.; Miller, Cory T.; Deverman, Benjamin E.; Pickel, James; Tian, Lin; Fox, Andrew S.; Gradinaru, Viviana 分享 收藏
Functional gene delivery to and across brain vasculature of systemic AAVs with endothelial-specific tropism in rodents and broad tropism in primates Chen, Xinhong; Wolfe, Damien A.; Bindu, Dhanesh Sivadasan; Zhang, Mengying; Taskin, Naz; Goertsen, David; Shay, Timothy F.; Sullivan, Erin E.; Huang, Sheng-Fu; Kumar, Sripriya Ravindra; Arokiaraj, Cynthia M.; Plattner, Viktor M.; Campos, Lillian J.; Mich, John K.; Monet, Deja; Ngo, Victoria; Ding, Xiaozhe; Omstead, Victoria; Weed, Natalie; Bishaw, Yeme; Gore, Bryan B.; Lein, Ed S.; Akrami, Athena; Miller, Cory; Levi, Boaz P.; Keller, Annika; Ting, Jonathan T.; Fox, Andrew S.; Eroglu, Cagla; Gradinaru, Viviana 分享 收藏
Enhancer viruses for combinatorial cell-subclass-specific labeling Graybuck, Lucas T.; Daigle, Tanya L.; Sedeno-Cortes, Adriana E.; Walker, Miranda; Kalmbach, Brian; Lenz, Garreck H.; Morin, Elyse; Thuc Nghi Nguyen; Garren, Emma; Bendrick, Jacqueline L.; Kim, Tae Kyung; Zhou, Thomas; Mortrud, Marty; Yao, Shenqin; Siverts, La' Akea; Larsen, Rachael; Gore, Bryan B.; Szelenyi, Eric R.; Trader, Cameron; Balaram, Pooja; van Velthoven, Cindy T. J.; Chiang, Megan; Mich, John K.; Dee, Nick; Goldy, Jeff; Cetin, Ali H.; Smith, Kimberly; Way, Sharon W.; Esposito, Luke; Yao, Zizhen; Gradinaru, Viviana; Sunkin, Susan M.; Lein, Ed; Levi, Boaz P.; Ting, Jonathan T.; Zeng, Hongkui; Tasic, Bosiljka 分享 收藏
Functional enhancer elements drive subclass-selective expression from mouse to primate neocortex Mich, John K.; Graybuck, Lucas T.; Hess, Erik E.; Mahoney, Joseph T.; Kojima, Yoshiko; Ding, Yi; Somasundaram, Saroja; Miller, Jeremy A.; Kalmbach, Brian E.; Radaelli, Cristina; Gore, Bryan B.; Weed, Natalie; Omstead, Victoria; Bishaw, Yemeserach; Shapovalova, Nadiya, V; Martinez, Refugio A.; Fong, Olivia; Yao, Shenqin; Mortrud, Marty; Chong, Peter; Loftus, Luke; Bertagnolli, Darren; Goldy, Jeff; Casper, Tamara; Dee, Nick; Opitz-Araya, Ximena; Cetin, Ali; Smith, Kimberly A.; Gwinn, Ryder P.; Cobbs, Charles; Ko, Andrew L.; Ojemann, Jeffrey G.; Keene, C. Dirk; Silbergeld, Daniel L.; Sunkin, Susan M.; Gradinaru, Viviana; Horwitz, Gregory D.; Zeng, Hongkui; Tasic, Bosiljka; Lein, Ed S.; Ting, Jonathan T.; Levi, Boaz P. 分享 收藏
Roundabout receptor 2 maintains inhibitory control of the adult midbrain Gore, Bryan B.; Miller, Samara M.; Jo, Yong Sang; Baird, Madison A.; Hoon, Mrinalini; Sanford, Christina A.; Hunker, Avery; Lu, Weining; Wong, Rachel O.; Zweifel, Larry S. 分享 收藏
A-kinase Anchoring Protein 79/150 Recruits Protein Kinase C to Phosphorylate Roundabout Receptors Samelson, Bret K.; Gore, Bryan B.; Whiting, Jennifer L.; Nygren, Patrick J.; Purkey, Alicia M.; Colledge, Marcie; Langeberg, Lorene K.; Dell'Acqua, Mark L.; Zweifel, Larry S.; Scott, John D. 分享 收藏
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