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收藏In Remembrance of Professor Zelig Eshhar: A Life Committed to CAR-T缅怀泽利格·埃什哈教授:一位致力于CAR-T的一生
Debets, Reno; Hawkins, Robert; Gilham, David; Gorochov, Guy; Schumacher, Ton; Uckert, Wolfgang; Blankenstein, Thomas; Crawford, Dorothy; Taylor, Naomi; Szollosi, Janos; Stauss, Hans; Mondino, Anna; Allavena, Paola; Alarcon, Balbino; Buning, Hildegard; Abken, Hinrich
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收藏Scientific Advancements in Gene Therapies: Opportunities for Global Regulatory Convergence
Olaghere, Jimi; Williams, David A.; Farrar, Jeremy; Buening, Hildegard; Calhoun, Cecelia; Ho, Tony; Inamdar, Maneesha S.; Liu, David; Makani, Julie; Nyarko, Kwasi; Ruiz, Sol; Tisdale, John; Mccune, Joseph M.; Boadi, Esther; Reagan Udall Fn FDA
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收藏Ligand-modified rAAV6 vectors with nanoblades allow high-level gene knockin in HSPCs without compromising cell survival纳米刃修饰的rAAV6载体能够实现造血干细胞和祖细胞(HSPCs)的高效基因敲入,且不影响细胞存活。
Gutierrez-Guerrero, Alejandra; Perian, Severine; Leray, Aurelien; Martinello, Chiara; Recalde, Maria Jimena Abrey; Costa, Caroline; Herrero, Cecilia Iglesias; Bouzelha, Mohammed; Alvarez-Dorta, Dimitri; Gouin, Sebastien G.; Ayuso, Eduard; Adjali, Oumeya; Buning, Hildegard; Deniaud, David; Mevel, Mathieu
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收藏Third-generation lentiviral gene therapy rescues function in a mouse model of Usher 1B
Schott, Juliane W.; Huang, Peixin; Morgan, Michael; Nelson-Brantley, Jennifer; Koehler, Ally; Renslo, Bryan; Buening, Hildegard; Warnecke, Athanasia; Schambach, Axel; Staecker, Hinrich
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收藏Hepatitis D virus interferes with hepatitis B virus RNA production via interferon-dependent and-independent mechanisms丁型肝炎病毒通过干扰素依赖性和非依赖性机制干扰乙型肝炎病毒RNA的产生
Lucifora, Julie; Alfaiate, Dulce; Pons, Caroline; Michelet, Maud; Ramirez, Ricardo; Fusil, Floriane; Amirache, Fouzia; Rossi, Axel; Legrand, Anne-Flore; Charles, Emilie; Vegna, Serena; Farhat, Rayan; Rivoire, Michel; Passot, Guillaume; Gadot, Nicolas; Testoni, Barbara; Bach, Charlotte; Baumert, Thomas F.; Hyrina, Anastasia; Beran, Rudolf K.; Zoulim, Fabien; Boonstra, Andre; Buening, Hildegard; Verrier, Eloi R.; Cosset, Francois-Loic; Fletcher, Simon P.; Salvetti, Anna; Durantel, David
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收藏Adeno-associated virus serotype 2 capsid variants for improved liver-directed gene therapy
Meumann, Nadja; Cabanes-Creus, Marti; Ertelt, Moritz; Navarro, Renina Gale; Lucifora, Julie; Yuan, Qinggong; Nien-Huber, Karin; Abdelrahman, Ahmed; Vu, Xuan-Khang; Zhang, Liang; Franke, Ann-Christin; Schmithals, Christian; Piiper, Albrecht; Vogt, Annabelle; Gonzalez-Carmona, Maria; Frueh, Jochen T.; Ullrich, Evelyn; Meuleman, Philip; Talbot, Steven R.; Odenthal, Margarete; Ott, Michael; Seifried, Erhard; Schoeder, Clara T.; Schwable, Joachim; Lisowski, Leszek; Buning, Hildegard
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收藏A multiplexed barcode approach to simultaneously evaluate gene delivery by adeno-associated virus capsid variants in nonhuman primates
Stone, Daniel; Meumann, Nadja; Kuhlmann, Anne-Sophie; Peterson, Christopher W.; Xie, Hong; Roychoudhury, Pavitra; Loprieno, Michelle A.; Vu, Xuan-Khang; Strongin, Daniel E.; Kenkel, Elizabeth J.; Haick, Anoria; Stensland, Laurence; Obenza, Willimark M.; Parrott, Jacob; Nelson, Veronica; Murnane, Robert D.; Huang, Meei-Li; Aubert, Martine; Kiem, Hans-Peter; Buening, Hildegard; Jerome, Keith R.
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收藏AAV capsid engineering identified two novel variants with improved in vivo tropism for cardiomyocytesAAV衣壳工程鉴定了两种具有改善的心肌细胞体内趋向性的新变体
Rode, Laura; Baer, Christian; Gross, Sonja; Rossi, Axel; Meumann, Nadja; Viereck, Janika; Abbas, Naisam; Xiao, Ke; Riedel, Isabelle; Gietz, Anika; Zimmer, Karina; Odenthal, Margarete; Buening, Hildegard; Thum, Thomas
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收藏Novel AAV capsids for intravitreal gene therapy of photoreceptor disorders用于光感受器疾病的玻璃体内基因治疗的新型AAV衣壳
Pavlou, Marina; Schon, Christian; Occelli, Laurence M.; Rossi, Axel; Meumann, Nadja; Boyd, Ryan F.; Bartoe, Joshua T.; Siedlecki, Jakob; Gerhardt, Maximilian J.; Babutzka, Sabrina; Bogedein, Jacqueline; Wagner, Johanna E.; Priglinger, Siegfried G.; Biel, Martin; Petersen-Jones, Simon M.; Buening, Hildegard; Michalakis, Stylianos
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