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Switching from inotersen to eplontersen in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy: analysis from NEURO-TTRansform (vol 271, pg 6655, 2024) 从伊托塞森切换到艾普隆特塞森治疗遗传性甲状腺素转运蛋白介导的淀粉样变性伴多发性神经病变:NEURO-TTRansform(第271卷,第6655页,2024年)的分析 Conceicao, Isabel; Berk, John L.; Weiler, Markus; Kowacs, Pedro A.; Dasgupta, Noel R.; Khella, Sami; Chao, Chi-Chao; Attarian, Shahram; Kwoh, T. Jesse; Jung, Shiangtung W.; Chen, Jersey; Viney, Nicholas J.; Yu, Rosie Z.; Gertz, Morie; Masri, Ahmad; Cruz, Marcia Waddington; Coelho, Teresa 分享 收藏
Diagnostic Test Accuracy of Bone Scintigraphy in the Diagnosis of Attr Amyloidosis: A Systematic Review and Meta-Analysis 骨闪烁显像在诊断ATTR淀粉样变性中的诊断试验准确性:一项系统评价和荟萃分析 Azzam, Muayad; Kawtharany, Hassan; Nazzal, Jamil; Kukreti, Vishal; Seftel, Matthew D.; Alkhader, Aseel; Hamarsha, Qais; Khraise, Tala; Almasri, Mohammad Mahmoud; Zeid, Hadi Khaled Abou; Alwan, Iktimal; Jaber, Noor; Fraitekh, Mohammad; Dasgupta, Noel; Comenzo, Raymond; Jamal, Faizi; Aguirre, Maria Adela; Boedicker, Deborah; Bumma, Naresh; Carroll, Antonia; Cook, Joselle; de la Torre, Alfredo H.; Dispenzieri, Angela; Khouri, Jack; Leung, Nelson; Picken, Maria M.; Raza, Shahzad; Sanchorawala, Vaishali; Shaikh, Hira; Sarswat, Nitasha; Singh, Daulath; Mustafa, Reem A. 分享 收藏
Diagnostic Test Accuracy of Fat Pad Sampling and Bone Marrow Biopsies in the Diagnosis of AL Amyloidosis: A Systematic Review and Meta-Analysis 脂肪垫取样和骨髓活检在AL淀粉样变性诊断中的诊断试验准确性:一项系统评价和荟萃分析 Azzam, Muayad; Kawtharany, Hassan; Nazzal, Jamil; Kukreti, Vishal; Seftel, Matthew D.; Alkhader, Aseel; Hamarsha, Qais; Khraise, Tala; Almasri, Mohammad Mahmoud; Zeid, Hadi Khaled Abou; Alwan, Iktimal; Jaber, Noor; Qadir, Mustafa; Carroll, Antonia; Dispenzieri, Angela; Khouri, Jack; Picken, Maria M.; Raza, Shahzad; Shaikh, Hira; Aguirre, Maria Adela; Boedicker, Deborah; Bumma, Naresh; Cook, Joselle; Comenzo, Raymond; Jamal, Faizi; Dasgupta, Noel; Torre, Alfredo H. De La; Leung, Nelson; Sanchorawala, Vaishali; Sarswat, Nitasha; Singh, Daulath; Mustafa, Reem A. 分享 收藏
Eplontersen for Hereditary Transthyretin Amyloidosis With Polyneuropathy Eplontersen用于遗传性甲状腺素蛋白淀粉样变性伴多发性神经病 Coelho, Teresa; Marques, Wilson, Jr.; Dasgupta, Noel R.; Chao, Chi-Chao; Parman, Yesim; Franca, Marcondes Cavalcante, Jr.; Guo, Yuh-Cherng; Wixner, Jonas; Ro, Long-Sun; Calandra, Cristian R.; Kowacs, Pedro A.; Berk, John L.; Obici, Laura; Barroso, Fabio A.; Weiler, Markus; Conceicao, Isabel; Jung, Shiangtung W.; Buchele, Gustavo; Brambatti, Michela; Chen, Jersey; Hughes, Steven G.; Schneider, Eugene; Viney, Nicholas J.; Masri, Ahmad; Gertz, Morie R.; Ando, Yukio; Gillmore, Julian D.; Khella, Sami; Dyck, P. James B.; Cruz, Marcia Waddington 分享 收藏
Characteristics of Patients with Hereditary Transthyretin Amyloidosis-Polyneuropathy (ATTRv-PN) in NEURO-TTRansform, an Open-label Phase 3 Study of Eplontersen Eplontersen的开放标签3期研究neuro-ttransform中遗传性甲状腺素蛋白淀粉样变性多发性神经病 (attrv-pn) 患者的特征 Coelho, Teresa; Cruz, Marcia Waddington; Chao, Chi-Chao; Parman, Yesim; Wixner, Jonas; Weiler, Markus; Barroso, Fabio A.; Dasgupta, Noel R.; Jung, Shiangtung W.; Schneider, Eugene; Viney, Nicholas J.; Dyck, P. James B.; Ando, Yukio; Gillmore, Julian D.; Khella, Sami; Gertz, Morie A.; Obici, Laura; Berk, John L. 分享 收藏
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AA cardiomyopathy Dasgupta, Noel R.; Cummings, Oscar W.; Phillips, Carrie L.; Benson, Merrill D. 分享 收藏