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Michael Gapinske

university of illinois urbana-champaign

8H指数
27论文数
804被引数
收录论文 9
发表时间
In vivo CRISPR base editing for treatment of Huntington’s disease体内CRISPR碱基编辑治疗亨廷顿病
err2026-07-29
err0
errOAAI
errShraddha Shirguppe; Michael Gapinske; Devyani Swami; Kyrollos Shenouda; Angelo Miskalis; Nicholas Gosstola; Daniela Del Bosque Siller; Isabelle Guerra; Pankaj Acharya; Dana Joulani; Maddie G. Szkwarek; Ananthan Nambiar; Abhishek Bhattacharjee; Anagha S. Dangi; Norah Odle; Gabrielle E. Nathan; Gianna Elias; Michelle Stilger; Jackson Winter; Wendy S. Woods; Daphine Anand; Colin K. W. Lim; Sergei Maslov; Thomas Gaj; Pablo Perez-Pinera
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SPLICER: a highly efficient base editing toolbox that enables in vivo therapeutic exon skipping
err2024-11-28
err0
errOAAI
errMiskalis, Angelo; Shirguppe, Shraddha; Winter, Jackson; Elias, Gianna; Swami, Devyani; Nambiar, Ananthan; Stilger, Michelle; Woods, Wendy S.; Gosstola, Nicholas; Gapinske, Michael; Zeballos, Alejandra; Moore, Hayden; Maslov, Sergei; Gaj, Thomas; Perez-Pinera, Pablo
err分享
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Targeting Duchenne muscular dystrophy by skipping DMD exon 45 with base editors
err2023-09-01
err3
errOAAI
errGapinske, Michael; Winter, Jackson; Swami, Devyani; Gapinske, Lauren; Woods, Wendy S.; Shirguppe, Shraddha; Miskalis, Angelo; Busza, Anna; Joulani, Dana; Kao, Collin J.; Kostan, Kurt; Bigot, Anne; Bashir, Rashid; Perez-Pinera, Pablo
err分享
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Treatment of a Mouse Model of ALS by In Vivo Base Editing
err2020-04-01
err146
errOAAI
errLim, Colin K. W.; Gapinske, Michael; Brooks, Alexandra K.; Woods, Wendy S.; Powell, Jackson E.; Zeballos, M. Alejandra C.; Winter, Jackson; Perez-Pinera, Pablo; Gaj, Thomas
err分享
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Targeted exon skipping with AAV-mediated split adenine base editors (vol 5, 41, 2019)
err2019-10-15
err2
errOAAI
errWinter, Jackson; Luu, Alan; Gapinske, Michael; Manandhar, Sony; Shirguppe, Shraddha; Woods, Wendy S.; Song, Jun S.; Perez-Pinera, Pablo
err分享
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Targeted exon skipping with AAV-mediated split adenine base editors
err2019-08-20
err35
errOAAI
errWinter, Jackson; Luu, Alan; Gapinske, Michael; Manandhar, Sony; Shirguppe, Shraddha; Woods, Wendy S.; Song, Jun S.; Perez-Pinera, Pablo
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Multiplexed and tunable transcriptional activation by promoter insertion using nuclease-assisted vector integration
err2019-04-01
err12
errOAAI
errBrown, Alexander; Winter, Jackson; Gapinske, Michael; Tague, Nathan; Woods, Wendy S.; Perez-Pinera, Pablo
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CRISPR-SKIP: programmable gene splicing with single base editors
err2018-08-15
err148
errOAAI
errGapinske, Michael; Luu, Alan; Winter, Jackson; Woods, Wendy S.; Kostan, Kurt A.; Shiva, Nikhil; Song, Jun S.; Perez-Pinera, Pablo
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Damage, Healing, and Remodeling in Optogenetic Skeletal Muscle Bioactuators
err2017-05-10
err66
errOAAI
errRaman, Ritu; Grant, Lauren; Seo, Yongbeom; Cvetkovic, Caroline; Gapinske, Michael; Palasz, Alexandra; Dabbous, Howard; Kong, Hyunjoon; Pinera, Pablo Perez; Bashir, Rashid
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