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收藏Development of a rabbit model for adrenoleukodystrophy: A pilot study on gene therapy using rAAV9
Zhou, Xiaoya; Ma, Chui-Yan; Zhang, Xiaoxian; Xu, Xianchuan; Duan, Fuyu; Kou, Meng; Liu, Hongsheng; Zeng, Liang; Guo, Liyan; Chen, Shaoxiang; Chen, Li; Li, Ziyue; Luo, Jie; Wu, Jieying; Li, Zhejin; Li, Zhanjun; Sui, Tingting; Yuan, Ping; Lin, Zhijian; Chen, Hao; Lai, Liangxue; Lian, Qizhou
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收藏The RhoB p.S73F mutation leads to cerebral palsy through dysregulation of lipid homeostasis
Wu, Xinyu; Liu, Ruonan; Zhang, Zhongtian; Yang, Jie; Liu, Xin; Jiang, Liqiang; Fang, Mengmeng; Wang, Shoutang; Lai, Liangxue; Song, Yuning; Li, Zhanjun
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收藏Potential drug targets for tumors identified through Mendelian randomization analysis
Song, Na; Shi, Pingyu; Cui, Kai; Zeng, Liqun; Wang, Ziwei; Di, Wenyu; Li, Jinsong; Fan, Yanwu; Li, Zhanjun; Zhang, Jinghang; Su, Wei; Wang, Haijun
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收藏Precise large-fragment deletions in mammalian cells and mice generated by dCas9-controlled CRISPR/Cas3通过dCas9-controlled CRISPR/Cas3在哺乳动物细胞和小鼠中产生精确的大片段缺失
Li, Jinze; Zhao, Ding; Zhang, Tao; Xiong, Haoyang; Hu, Mingyang; Liu, Hongmei; Zhao, Feiyu; Sun, Xiaodi; Fan, Peng; Qian, Yuqiang; Wang, Di; Lai, Liangxue; Sui, Tingting; Li, Zhanjun
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收藏Decreasing predictable DNA off-target effects and narrowing editing windows of adenine base editors by fusing human Rad18 protein variant通过融合人类Rad18蛋白变体来减少可预测的DNA脱靶效应并缩小腺嘌呤碱基编辑器的编辑窗口
Wang, Ziru; Yuan, Hongming; Yang, Lin; Ma, Lerong; Zhang, Yuanzhu; Deng, Jiacheng; Li, Xueyuan; Xiao, Wenyu; Li, Zhanjun; Qiu, Jiazhang; Ouyang, Hongsheng; Pang, Daxin
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收藏Development of a highly efficient prime editor system in mice and rabbits
Qian, Yuqiang; Wang, Di; Niu, Wenchao; Shi, Zheng; Wu, Mao; Zhao, Ding; Li, Jinze; Gao, Xun; Zhang, Zhongtian; Lai, Liangxue; Li, Zhanjun
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收藏A strategy for Cas13 miniaturization based on the structure and AlphaFold
Zhao, Feiyu; Zhang, Tao; Sun, Xiaodi; Zhang, Xiyun; Chen, Letong; Wang, Hejun; Li, Jinze; Fan, Peng; Lai, Liangxue; Sui, Tingting; Li, Zhanjun
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收藏Unique progerin C-terminal peptide ameliorates Hutchinson-Gilford progeria syndrome phenotype by rescuing BUBR1 (vol 3, pg.no: 185, 2023)
Zhang, Na; Hu, Qianying; Sui, Tingting; Fu, Lu; Zhang, Xinglin; Wang, Yu; Zhu, Xiaojuan; Huang, Baiqu; Lu, Jun; Li, Zhanjun; Zhang, Yu
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收藏Unique progerin C-terminal peptide ameliorates Hutchinson-Gilford progeria syndrome phenotype by rescuing BUBR1
Zhang, Na; Hu, Qianying; Sui, Tingting; Fu, Lu; Zhang, Xinglin; Wang, Yu; Zhu, Xiaojuan; Huang, Baiqu; Lu, Jun; Li, Zhanjun; Zhang, Yu
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收藏Lp-PLA2 (Lipoprotein-Associated Phospholipase A2) Deficiency Lowers Cholesterol Levels and Protects Against Atherosclerosis in Rabbits
Chen, Jiahuan; Zhang, Huanyu; Li, Linquan; Zhang, Xinwei; Zhao, Dazhong; Wang, Lingyu; Wang, Jiaqi; Yang, Ping; Sun, Huan; Liu, Kun; Chen, Weiwei; Li, Lin; Lin, Feng; Li, Zhanjun; Chen, Y. Eugene; Zhang, Jifeng; Pang, Daxin; Ouyang, Hongsheng; He, Yuquan; Fan, Jianglin; Tang, Xiaochun
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收藏Anti-hsa-miR-59 alleviates premature senescence associated with Hutchinson-Gilford progeria syndrome in mice
Hu, Qianying; Zhang, Na; Sui, Tingting; Li, Guanlin; Wang, Zhiyao; Liu, Mingyue; Zhu, Xiaojuan; Huang, Baiqu; Lu, Jun; Li, Zhanjun; Zhang, Yu
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