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Anti-gene oligonucleotides targeting Friedreich's ataxia expanded GAA•TTC repeats increase Frataxin expression 靶向Friedreich's ataxia扩展的GAA•TTC重复序列的反义寡核苷酸可增加Frataxin表达 Mozafari, Negin; Milagres, Salome; Umek, Tea; Rocha, Cristina S. J.; Vargiu, Claudia M.; Freyberger, Fiona; Saher, Osama; Napierala, Marek; Napierala, Jill S.; Blomberg, Pontus; Jorgensen, Per T.; Punga, Tanel; Smith, C. I. Edvard; Wengel, Jesper; Zain, Rula 分享 收藏
Cell-penetrating peptide-conjugated, splice-switching oligonucleotides mitigate the phenotype in BTK/Tec double deficient X-linked agammaglobulinemia model 穿膜肽偶联的剪接转换寡核苷酸可缓解BTK/Tec双缺陷型X连锁无丙种球蛋白血症模型的表型 Bestas, Burcu; Estupinan, H. Yesid; Wang, Qing; Kharazi, Shabnam; He, Chenfei; K. Mohammad, Dara; Gupta, Dhanu; Wiklander, Oscar P. B.; Lehto, Taavi; Lundin, Karin E.; Berglof, Anna; Karlsson, Mikael C. I.; Abendroth, Frank; El Andaloussi, Samir; Gait, Michael J.; Wood, Matthew J. A.; Leumann, Christian J.; Stetsenko, Dmitry A.; Mansson, Robert; Wengel, Jesper; Zain, Rula; Smith, C. I. Edvard 分享 收藏
Anti-gene oligonucleotide clamps invade dsDNA and downregulate huntingtin expression Umek, Tea; Lundin, Karin E.; Mowoe, Metoboroghene O.; Hao, Yitong; Roudi, Samantha; Zura, Lana; Jorgensen, Per T.; Lou, Chenguang; Hagey, Daniel W.; Wengel, Jesper; Smith, C. I. Edvard; Zain, Rula 分享 收藏
An Albumin-Holliday Junction Biomolecular Modular Design for Programmable Multifunctionality and Prolonged Circulation 用于可编程多功能和延长循环的白蛋白-霍利迪连接生物分子模块设计 Dinesen, Anders; Andersen, Veronica L.; Elkhashab, Marwa; Pilati, Diego; Bech, Pernille; Fuchs, Elisabeth; Samuelsen, Torbjorn R.; Winther, Alexander; Cai, Yunpeng; Marcher, Anders; Wall, Archie; Omer, Marjan; Nielsen, Jesper S.; Chudasama, Vijay; Baker, James R.; Gothelf, Kurt V.; Wengel, Jesper; Kjems, Jorgen; Howard, Kenneth A. 分享 收藏
Chemical Modifications and Design Influence the Potency of Huntingtin Antigene Oligonucleotides Saher, Osama; Zaghloul, Eman M. M.; Umek, Tea; Hagey, Daniel W. W.; Mozafari, Negin; Danielsen, Mathias B. B.; Gouda, Alaa S. S.; Lundin, Karin E. E.; Jorgensen, Per T. T.; Wengel, Jesper; Smith, C. I. Edvard; Zain, Rula 分享 收藏
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Investigating discovery strategies and pharmacological properties of stereodefined phosphorodithioate LNA gapmers Duschmale, Joerg; Schaeublin, Adrian; Funder, Erik; Schmidt, Steffen; Kielpinski, Lukasz J.; Nymark, Helle; Jensen, Klaus; Koch, Troels; Duschmale, Martina; Koller, Erich; Moller, Marianne Ravn; Schadt, Simone; Husser, Christophe; Brink, Andreas; Sewing, Sabine; Minz, Tanja; Wengel, Jesper; Bleicher, Konrad; Li, Meiling 分享 收藏
Albumin Biomolecular Drug Designs Stabilized through Improved Thiol Conjugation and a Modular Locked Nucleic Acid Functionalized Assembly Dinesen, Anders; Winther, Alexander; Wall, Archie; Maercher, Anders; Palmfeldt, Johan; Chudasama, Vijay; Wengel, Jesper; Gothelf, Kurt, V; Baker, James R.; Howard, Kenneth A. 分享 收藏
Chirality transmission in macromolecular domains Pandey, Shankar; Mandal, Shankar; Danielsen, Mathias Bogetoft; Brown, Asha; Hu, Changpeng; Christensen, Niels Johan; Kulakova, Alina Vitaliyivna; Song, Shixi; Brown, Tom; Jensen, Knud J.; Wengel, Jesper; Lou, Chenguang; Mao, Hanbin 分享 收藏
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Oligonucleotides Targeting DNA Repeats Downregulate Huntingtin Gene Expression in Huntington's Patient-Derived Neural Model System Umek, Tea; Olsson, Thomas; Gissberg, Olof; Saher, Osama; Zaghloul, Eman M.; Lundin, Karin E.; Wengel, Jesper; Hanse, Eric; Zetterberg, Henrik; Vizlin-Hodzic, Dzeneta; Smith, C. I. Edvard; Zain, Rula 分享 收藏
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Dual role of the miR-146 family in rhinovirus-induced airway inflammation and allergic asthma exacerbation Laanesoo, Anet; Urgard, Egon; Periyasamy, Kapilraj; Laan, Martti; Bochkov, Yury A.; Aab, Alar; Magilnick, Nathaniel; Pooga, Margus; Gern, James E.; Johnston, Sebastian L.; Coquet, Jonathan M.; Boldin, Mark P.; Wengel, Jesper; Altraja, Alan; Bochenek, Grazyna; Jakiela, Bogdan; Rebane, Ana 分享 收藏
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NickFect type of cell-penetrating peptides present enhanced efficiency for microRNA-146a delivery into dendritic cells and during skin inflammation Carreras-Badosa, Gemma; Maslovskaja, Julia; Periyasamy, Kapilraj; Urgard, Egon; Padari, Kart; Vaher, Helen; Tserel, Liina; Gestin, Maxime; Kisand, Kai; Arukuusk, Piret; Lou, Chenguang; Langel, Ulo; Wengel, Jesper; Pooga, Margus; Rebane, Ana 分享 收藏
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