Long-term HSC gene therapy in mucopolysaccharidosis type IIIB mice corrects disease with no evidence of insertional mutagenesis despite high vector copy numbersMOLECULAR GENETICS AND METABOLISMIF3.52025-02-010PRE
Systemic immune challenge exacerbates neurodegeneration in a model of neurological lysosomal diseaseEMBO MOLECULAR MEDICINEIF8.32024-06-180OAAI
Systemic inflammation leads to neuronal loss and exacerbates behavioural deficits in a mouse model of MPS IIIAMOLECULAR GENETICS AND METABOLISMIF3.52024-02-010PRE
Overcoming cancer drug resistance with AI-designed RNA epigenetic inhibitorsMOLECULAR CANCER THERAPEUTICSIF5.52023-12-011PRE
Identification of novel peptide sequences to fuse to iduronate-2-sulfatase for the treatment of Hunter syndromeMOLECULAR GENETICS AND METABOLISMIF3.52023-02-010PRE
Delivering gene therapy for mucopolysaccharide diseasesFRONTIERS IN MOLECULAR BIOSCIENCESIF42022-09-1219OAAI
Actinomycin D downregulates Sox2 and improves survival in preclinical models of recurrent glioblastoma放线菌素d在复发性胶质母细胞瘤的临床前模型中下调Sox2并改善生存率NEURO-ONCOLOGYIF13.42020-03-3025OAAI
Delivering Hematopoietic Stem Cell Gene Therapy Treatments for Neurological Lysosomal DiseasesACS CHEMICAL NEUROSCIENCEIF3.92018-08-2310OAAI
Pre-clinical safety and efficacy evaluation of GMP lentiviral vector in preparation for a clinical trial of hematopoietic stem cell gene therapy in MPS IIIAMOLECULAR GENETICS AND METABOLISMIF3.52018-02-011PREAI
个人简介
教育背景
工作经历
荣誉奖项
未登录.png){kind=icon}
未登录个人简介教育背景工作经历荣誉奖项
研究方向