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J

Jiřı́ Klı́ma

czech academy of sciences
H指数:29
被引数:2,578

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Molecular features of a Huntington's disease knock-in minipig

亨廷顿病基因敲入小型猪的分子特征

2026-05-010
PRE
Widespread and sustained target engagement in Huntington's disease minipigs upon intrastriatal microRNA-based gene therapy
2021-04-0729
PRE
AAV5-MIHTT GENE THERAPY DEMONSTRATES BROAD DISTRIBUTION AND STRONG HUMAN MUTANT HUNTINGTIN LOWERING IN A HUNTINGTON DISEASE MINIPIG MODEL
2018-09-010
PREAI
Survival of syngeneic and allogeneic iPSC-derived neural precursors after spinal grafting in minipigs
2018-05-0947
OAAI