未登录Subretinal Injection Volume Correlates to Persistent Outer Retinal Thinning in the Pig Eye
Seitz, Immanuel P.; Nyshchuk, Ruslan; Ellederova, Zdenka; Ardan, Taras; Juhasova, Jana; Nemesh, Yaroslav; Juhas, Stefan; Drutovic, Saskia; Susskind, Daniela; Schnichels, Sven; Motlik, Jan; Klymiuk, Nikolai; Wolfrum, Uwe; DeMott, Kathryn Post; Klein, Jennifer J.; Winslow, Ashley; Fischer, M. Dominik
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收藏Delivery of Human iPSC-Derived RPE Cells in Healthy Minipig Retina Results in Interaction Between Photoreceptors and Transplanted Cells向健康迷你猪视网膜内输送人诱导多能干细胞来源的RPE细胞会导致感光细胞与移植细胞之间的相互作用
Brymová, AM; Rodriguez-Jimenez, FJ; Konrad, A; Nemesh, Y; Thottappali, MA; Artero-Castro, A; Nyshchuk, R; Kolesnikova, A; Müller, B; Studenovska, H; Juhasova, J; Juhas, S; Valekova, I; Lukovic, D; Aleman, C; Ardan, T; Drutovic, S; Motlik, J; Ellederova, Z; Stranák, Z; Veith, M; Lytvynchuk, L; Sharma, R; Bharti, K; Petrovski, G; Jendelova, P; Stieger, K; Erceg, S
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收藏Human iPSC-derived RPE cells implantation into minipig eye: Two weeks follow-up study
Ardan, Taras; Erceg, Slaven; Artero-Castro, Ana; Studenovska, Hana; Mueller, Brigitte; Stieger, Knut; Lytvynchuk, Lyubomyr; Stranak, Zbynek; Ellederova, Zdenka; Juhas, Stefan; Motlik, Jan; Petrovski, Goran
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收藏In vitro and in vivo evaluation of genetically corrected RPE cells for autologous cell therapy of hereditary retinal dystrophies
Rodriguez-Jimenez, F. J.; Brymova, A.; Mueller, B.; Stieger, K.; Jendelova, P.; Ardan, T.; Studenovska, H.; Lytvynchuk, L.; Stranak, Z.; Ellederova, Z.; Juhas, J.; Motlik, J.; Petrovski, G.; Erceg, Lukovic D.
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收藏Retinal Pigment Epithelium Cell Development: Extrapolating Basic Biology to Stem Cell Research
Gupta, Santosh; Lytvynchuk, Lyubomyr; Ardan, Taras; Studenovska, Hana; Faura, Georgina; Eide, Lars; Znaor, Ljubo; Erceg, Slaven; Stieger, Knut; Motlik, Jan; Bharti, Kapil; Petrovski, Goran
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收藏AAV5-MIHTT GENE THERAPY MEDIATES SUSTAINED MUTANT HUNTINGTIN LOWERING IN BRAIN AND CEREBROSPINAL FLUID OF HUNTINGTON DISEASE MINIPIGS UP TO 4 YEARS
Van der Bent, Leontien; Brouwers, Cynthia; Pocornie, Robin; Stam, Anouk; Jonk, Steffi; Klima, Jiri; Juhas, Stefan; Motlik, Jan; Evers, Melvin; Ellederovae, Zdenka; Valles, Astrid
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收藏Precision spinal gene delivery-induced functional switch in nociceptive neurons reverses neuropathic pain
Tadokoro, Takahiro; Bravo-Hernandez, Mariana; Agashkov, Kirill; Kobayashi, Yoshiomi; Platoshyn, Oleksandr; Navarro, Michael; Marsala, Silvia; Miyanohara, Atsushi; Yoshizumi, Tetsuya; Shigyo, Michiko; Krotov, Volodymyr; Juhas, Stefan; Juhasova, Jana; Nguyen, Duong; Skalnikova, Helena Kupcova; Motlik, Jan; Studenovska, Hana; Proks, Vladimir; Reddy, Rajiv; Driscoll, Shawn P.; Glenn, Thomas D.; Kemthong, Taratorn; Malaivijitnond, Suchinda; Tomori, Zoltan; Vanicky, Ivo; Kakinohana, Manabu; Pfaff, Samuel L.; Ciacci, Joseph; Belan, Pavel; Marsala, Martin
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收藏Subretinal Implantation of Human Primary RPE Cells Cultured on Nanofibrous Membranes in Minipigs
Lytvynchuk, Lyubomyr; Ebbert, Annabelle; Studenovska, Hana; Nagymihaly, Richard; Josifovska, Natasha; Rais, David; Popelka, Stepan; Tichotova, Lucie; Nemesh, Yaroslav; Cizkova, Jana; Juhasova, Jana; Juhas, Stefan; Jendelova, Pavla; Franekova, Janka; Kozak, Igor; Erceg, Slaven; Stranak, Zbynek; Mueller, Brigitte; Ellederova, Zdenka; Motlik, Jan; Stieger, Knut; Ardan, Taras; Petrovski, Goran
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收藏Early disruption of photoreceptor cell architecture and loss of vision in a humanized pig model of usher syndromes
Grotz, Sophia; Schaefer, Jessica; Wunderlich, Kirsten A.; Ellederova, Zdenka; Auch, Hannah; Baehr, Andrea; Runa-Vochozkova, Petra; Fadl, Janet; Arnold, Vanessa; Ardan, Taras; Veith, Miroslav; Santamaria, Gianluca; Dhom, Georg; Hitzl, Wolfgang; Kessler, Barbara; Eckardt, Christian; Klein, Joshua; Brymova, Anna; Linnert, Joshua; Kurome, Mayuko; Zakharchenko, Valeri; Fischer, Andrea; Blutke, Andreas; Doering, Anna; Suchankova, Stepanka; Popelar, Jiri; Rodriguez-Bocanegra, Eduardo; Dlugaiczyk, Julia; Straka, Hans; May-Simera, Helen; Wang, Weiwei; Laugwitz, Karl-Ludwig; Vandenberghe, Luk H.; Wolf, Eckhard; Nagel-Wolfrum, Kerstin; Peters, Tobias; Motlik, Jan; Fischer, M. Dominik; Wolfrum, Uwe; Klymiuk, Nikolai
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收藏Advantages of nanofibrous membranes for culturing of primary RPE cells compared to commercial scaffolds
Tichotova, Lucie; Studenovska, Hana; Petrovski, Goran; Popelka, Stepan; Nemesh, Yaroslav; Sedlackova, Miroslava; Drutovic, Saskia; Rohiwal, Sonali; Jendelova, Pavla; Erceg, Slaven; Brymova, Anna; Artero-Castro, Ana; Lytvynchuk, Lyubomyr; Stranak, Zbynek; Ellederova, Zdenka; Motlik, Jan; Ardan, Taras
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收藏Widespread and sustained target engagement in Huntington's disease minipigs upon intrastriatal microRNA-based gene therapy
Valles, Astrid; Evers, Melvin M.; Stam, Anouk; Sogorb-Gonzalez, Marina; Brouwers, Cynthia; Vendrell-Tornero, Carlos; Acar-Broekmans, Seyda; Paerels, Lieke; Klima, Jiri; Bohuslavova, Bozena; Pintauro, Roberta; Fodale, Valentina; Bresciani, Alberto; Liscak, Roman; Urgosik, Dusan; Starek, Zdenek; Crha, Michal; Blits, Bas; Petry, Harald; Ellederova, Zdenka; Motlik, Jan; van Deventer, Sander; Konstantinova, Pavlina
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收藏Nanofibrous membranes reveal better properties for culturing of RPE cells in comparison with commercial scaffolds
Ardan, Taras; Zemanova, Lucie; Ellederova, Zdenka; Drutovic, Saskia; Studenovska, Hana; Popelka, Stepan; Kepkova-Vodickova, Katerina; Rohiwal, Sonali; Sedlackova, Miroslava; Motlik, Jan
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收藏Transgenic minipig model of Huntington's disease exhibiting gradually progressing neurodegeneration
Ardan, Taras; Baxa, Monika; Levinska, Bozena; Sedlackova, Miroslava; The Duong Nguyen; Klima, Jiri; Juhas, Stefan; Juhasova, Jana; Smatlikova, Petra; Vochozkova, Petra; Motlik, Jan; Ellederova, Zdenka
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收藏Deterioration of mitochondrial bioenergetics and ultrastructure impairment in skeletal muscle of a transgenic minipig model in the early stages of Huntington's disease
Rodinova, Marie; Krizova, Jana; Stufkova, Hana; Bohuslavova, Bozena; Askeland, Georgina; Dosoudilova, Zaneta; Juhas, Stefan; Juhasova, Jana; Ellederova, Zdenka; Zeman, Jiri; Eide, Lars; Motlik, Jan; Hansikova, Hana
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收藏SUSTAINED MUTANT HUNTINGTIN LOWERING IN THE BRAIN AND CEREBROSPINAL FLUID OF HUNTINGTON DISEASE MINIPIGS MEDIATED BY AAV5-MIHTT GENE THERAPY
Valles, Astrid; Brouwers, Cynthia; Pintauro, Roberta; Snapper, Jolanda; Bohuslavova, Bozena; Sogorb-Gonzalez, Marina; Fodale, Valentina; Bresciani, Alberto; Ellederova, Zdenka; Blits, Bas; Motlik, Jan; van Deventer, Sander; Evers, Melvin; Konstantinova, Paylina
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