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Use of HSALR female mice as a model for the study of myotonic dystrophy type I Carrascosa-Saez, Marc; Colom-Rodrigo, Anna; Gonzalez-Martinez, Irene; Perez-Gomez, Raquel; Garcia-Rey, Andrea; Piqueras-Losilla, Diego; Ballestar, Ana; Llamusi, Beatriz; Cerro-Herreros, Estefania; Artero, Ruben 分享 收藏
Immortalized human myotonic dystrophy type 1 muscle cell lines to address patient heterogeneity (vol 27, 109930, 2024) 永生性人类肌强直性营养不良1型肌细胞系用于解决患者异质性 (vol 27, 109930, 2024) Nunez-Manchon, Judit; Capo, Julia; Martinez-Pineiro, Alicia; Juanola, Eduard; Pesovic, Jovan; Mosqueira-Martin, Laura; Gonzalez-Imaz, Klaudia; Maestre-Mora, Pau; Odria, Renato; Cerro-Herreros, Estefania; Naldaiz-Gastesi, Neia; de Munain, Adolfo Lopez; Artero, Ruben; Savic-Pavicevic, Dusanka; Vallejo-Illarramendi, Ainara; Mamchaoui, Kamel; Bigot, Anne; Mouly, Vincent; Suelves, Monica; Nogales-Gadea, Gisela 分享 收藏
A Novel Class of FKBP12 Ligands Rescues Premature Aging Phenotypes Associated with Myotonic Dystrophy Type 1 Garcia-Puga, Mikel; Gerenu, Gorka; Bargiela, Ariadna; Espinosa-Espinosa, Jorge; Mosqueira-Martin, Laura; Sagartzazu-Aizpurua, Maialen; Aizpurua, Jesus M.; Vallejo-Illarramendi, Ainara; Artero, Ruben; de Munain, Adolfo Lopez; Matheu, Ander 分享 收藏
AntimiR treatment corrects myotonic dystrophy primary cell defects across several CTG repeat expansions with a dual mechanism of action Cerro-Herreros, Estefania; Nunez-Manchon, Judit; Naldaiz-Gastesi, Neia; Carrascosa-Saez, Marc; Garcia-Rey, Andrea; Losilla, Diego Piqueras; Gonzalez-Martinez, Irene; Espinosa-Espinosa, Jorge; Moreno, Kevin; Poyatos-Garcia, Javier; Vilchez, Juan J.; de Munain, Adolfo Lopez; Suelves, Monica; Nogales-Gadea, Gisela; Llamusi, Beatriz; Artero, Ruben 分享 收藏
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Peptide-conjugated antimiRs improve myotonic dystrophy type 1 phenotypes by promoting endogenous MBNL1 expression Gonzalez-Martinez, Irene; Cerro-Herreros, Estefania; Moreno, Nerea; Garcia-Rey, Andrea; Espinosa-Espinosa, Jorge; Carrascosa-Saez, Marc; Piqueras-Losilla, Diego; Arzumanov, Andrey; Seoane-Miraz, David; Jad, Yahya; Raz, Richard; Wood, Matthew J.; Varela, Miguel A.; Llamusi, Beatriz; Artero, Ruben 分享 收藏
BlockmiR AONs as Site-Specific Therapeutic MBNL Modulation in Myotonic Dystrophy 2D and 3D Muscle Cells and HSALR Mice Overby, Sarah J.; Cerro-Herreros, Estefania; Espinosa-Espinosa, Jorge; Gonzalez-Martinez, Irene; Moreno, Nerea; Fernandez-Costa, Juan M.; Balaguer-Trias, Jordina; Ramon-Azcon, Javier; Perez-Alonso, Manuel; Moller, Thorleif; Llamusi, Beatriz; Artero, Ruben 分享 收藏
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Proof of concept of peptide-linked blockmiR-induced MBNL functional rescue in myotonic dystrophy type 1 mouse model Overby, Sarah J.; Cerro-Herreros, Estefania; Gonzalez-Martinez, Irene; Varela, Miguel A.; Seoane-Miraz, David; Jad, Yahya; Raz, Richard; Moller, Thorleif; Perez-Alonso, Manuel; Wood, Matthew J.; Llamusi, Beatriz; Artero, Ruben 分享 收藏
Preclinical characterization of antagomiR-218 as a potential treatment for myotonic dystrophy Cerro-Herreros, Estefania; Gonzalez-Martinez, Irene; Moreno, Nerea; Espinosa-Espinosa, Jorge; Fernandez-Costa, Juan M.; Colom-Rodrigo, Anna; Overby, Sarah J.; Seoane-Miraz, David; Poyatos-Garcia, Javier; Vilchez, Juan J.; de Munain, Adolfo Lopez; Varela, Miguel A.; Wood, Matthew J.; Perez-Alonso, Manuel; Llamusi, Beatriz; Artero, Ruben 分享 收藏
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