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收藏ABE8e adenine base editor precisely and efficiently corrects a recurrent COL7A1 nonsense mutation
Sheriff, Adam; Guri, Ina; Zebrowska, Paulina; Llopis-Hernandez, Virginia; Brooks, Imogen R.; Tekkela, Stavroula; Subramaniam, Kavita; Gebrezgabher, Ruta; Naso, Gaetano; Petrova, Anastasia; Balon, Katarzyna; Onoufriadis, Alexandros; Kujawa, Dorota; Kotulska, Martyna; Newby, Gregory; Laczmanski, Lukasz; Liu, David R.; McGrath, John A.; Jackow, Joanna
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