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GMP-Grade Manufacturing and Quality Control of a Non-Virally Engineered Advanced Therapy Medicinal Product for Personalized Treatment of Age-Related Macular Degeneration Kropp, Martina; Harmening, Nina; Bascuas, Thais; Johnen, Sandra; De Clerck, Eline; Fernandez, Veronica; Ronchetti, Mattia; Cadossi, Ruggero; Zanini, Cristina; Scherman, Daniel; Ivics, Zoltan; Marie, Corinne; Izsvak, Zsuzsanna; Thumann, Gabriele 分享 收藏
A Novel Gene Controls a New Structure: PiggyBac Transposable Element-Derived 1, Unique to Mammals, Controls Mammal-Specific Neuronal Paraspeckles Rasko, Tamas; Pande, Amit; Radscheit, Kathrin; Zink, Annika; Singh, Manvendra; Sommer, Christian; Wachtl, Gerda; Kolacsek, Orsolya; Inak, Gizem; Szvetnik, Attila; Petrakis, Spyros; Bunse, Mario; Bansal, Vikas; Selbach, Matthias; Orban, Tamas, I; Prigione, Alessandro; Hurst, Laurence D.; Izsvak, Zsuzsanna 分享 收藏
Recapitulating early human development with 8C-like cells 用8c样细胞重述人类早期发育 Yu, Xiu; Liang, Shiqi; Chen, Manqi; Yu, Hanwen; Li, Ruiqi; Qu, Yuliang; Kong, Xuhui; Guo, Ruirui; Zheng, Rongyan; Izsvak, Zsuzsanna; Sun, Chuanbo; Yang, Mingzhu; Wang, Jichang 分享 收藏
Naive-like pluripotency to pave the way for saving the northern white rhinoceros from extinction Zywitza, Vera; Rusha, Ejona; Shaposhnikov, Dmitry; Ruiz-Orera, Jorge; Telugu, Narasimha; Rishko, Valentyna; Hayashi, Masafumi; Michel, Geert; Wittler, Lars; Stejskal, Jan; Holtze, Susanne; Goeritz, Frank; Hermes, Robert; Wang, Jichang; Izsvak, Zsuzsanna; Colleoni, Silvia; Lazzari, Giovanna; Galli, Cesare; Hildebrandt, Thomas B.; Hayashi, Katsuhiko; Diecke, Sebastian; Drukker, Micha 分享 收藏
Efficient generation of osteoclasts from human induced pluripotent stem cells and functional investigations of lethal CLCN7-related osteopetrosis Roessler, Uta; Hennig, Anna Floriane; Stelzer, Nina; Bose, Shroddha; Kopp, Johannes; Soe, Kent; Cyganek, Lukas; Zifarelli, Giovanni; Ali, Salaheddine; von der Hagen, Maja; Straessler, Elisabeth Tamara; Hahn, Gabriele; Pusch, Michael; Stauber, Tobias; Izsvak, Zsuzsanna; Gossen, Manfred; Stachelscheid, Harald; Kornak, Uwe 分享 收藏
Single-dose MGTA-145/plerixafor leads to efficient mobilization and in vivo transduction of HSCs with thalassemia correction in mice Li, Chang; Goncalves, Kevin A.; Rasko, Tamas; Pande, Amit; Gil, Sucheol; Liu, Zhinan; Izsvak, Zsuzsanna; Papayannopoulou, Thalia; Davis, John C.; Kiem, Hans-Peter; Lieber, Andre 分享 收藏
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CLINICAL-GRADE MANUFACTURING OF ROR1 CAR T CELLS USING A NOVEL VIRUS-FREE PROTOCOL Mestermann, K.; Eichler, M.; Machwirth, M.; Kebbel, K.; Koehl, U.; Einsele, H.; Mueller, C.; Lehmann, J.; Rasko, T.; Lundberg, F.; Izsvak, Z.; Schmiedeknecht, G.; Hudecek, M. 分享 收藏
Targeting CD33 in Chemoresistant AML Patient-Derived Xenografts by CAR-CIK Cells Modified with an Improved SB Transposon System Rotiroti, Maria Caterina; Buracchi, Chiara; Arcangeli, Silvia; Galimberti, Stefania; Valsecchi, Maria Grazia; Perriello, Vincenzo Maria; Rasko, Tamas; Alberti, Gaia; Magnani, Chiara Francesca; Cappuzzello, Claudia; Lundberg, Felix; Pande, Amit; Dastoli, Giuseppe; Introna, Martino; Serafini, Marta; Biagi, Ettore; Izsvak, Zsuzsanna; Biondi, Andrea; Tettamanti, Sarah 分享 收藏
Curative in vivo hematopoietic stem cell gene therapy of murine thalassemia using large regulatory elements Wang, Hongjie; Georgakopoulou, Aphrodite; Li, Chang; Liu, Zhinan; Gil, Sucheol; Bashyam, Ashvin; Yannaki, Evangelia; Anagnostopoulos, Achilles; Pande, Amit; Izsvak, Zsuzsanna; Papayannopoulou, Thalia; Lieber, Andre 分享 收藏
Human endogenous retrovirus HERV-K(HML-2) RNA causes neurodegeneration through Toll-like receptors Dembny, Paul; Newman, Andrew G.; Singh, Manvendra; Hinz, Michael; Szczepek, Michal; Krueger, Christina; Adalbert, Robert; Dzaye, Omar; Trimbuch, Thorsten; Wallach, Thomas; Kleinau, Gunnar; Derkow, Katja; Richard, Bernhard C.; Schipke, Carola; Scheidereit, Claus; Stachelscheid, Harald; Golenbock, Douglas; Peters, Oliver; Coleman, Michael; Heppner, Frank L.; Scheerer, Patrick; Tarabykin, Victor; Ruprecht, Klemens; Izsvak, Zsuzsanna; Mayer, Jens; Lehnardt, Seija 分享 收藏
Human somatic cell mutagenesis creates genetically tractable sarcomas (vol 46, pg 964, 2014) Molyneux, Sam D.; Waterhouse, Paul D.; Shelton, Dawne; Shao, Yang W.; Watling, Christopher M.; Tang, Qing-Lian; Harris, Isaac S.; Dickson, Brendan C.; Tharmapalan, Pirashaanthy; Sandve, Geir K.; Zhang, Xiaoyang; Bailey, Swneke D.; Berman, Hal; Wunder, Jay S.; Izsvak, Zsuzsanna; Lupien, Mathieu; Mak, Tak W.; Khokha, Rama 分享 收藏
Retrotransposition creates sloping shores: a graded influence of hypomethylated CpG islands on flanking CpG sites (vol 25, pg 1135, 2015) Grandi, Fiorella C.; Rosser, James M.; Newkirk, Simon J.; Yin, Jun; Jiang, Xiaoling; Xing, Zhuo; Whitmore, Leanne; Bashir, Sanum; Ivics, Zoltan; Izsvak, Zsuzsanna; Ye, Ping; Yu, Y. Eugene; An, Wenfeng 分享 收藏