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Tsukasa Ohmori

Jichi Medical University
H指数:32
被引数:4,385

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Non-viral delivery of a base editor enables personalized correction of hemophilia B nonsense variants in a mouse model

非病毒递送碱基编辑器在mouse模型中实现血友病B终止密码子变异的个性化纠正

2026-06-120
OAAI
Engineering a compact high-fidelity Staphylococcus aureus Cas9 variant with broader targeting range and mechanistic insights into its activation

构建一种紧凑型高保真金黄色葡萄球菌Cas9变体,并阐明其扩展靶向范围及活化的机制

2026-04-160
OAAI
Therapeutic base editing to generate a gain-of-function F9 variant for hemophilia B

通过治疗性碱基编辑生成具有获得性功能的F9变体以治疗血友病B

Blood
IF23.1
2025-10-280
OAAI
IL-33-primed NLRP3 inflammasome in basophils drives IL-1β production and initiates atopic dermatitis inflammation

嗜碱性粒细胞中IL-33-primed NLRP3炎性小体驱动IL-1β 产生并引发特应性皮炎炎症

2025-07-270
OAAI
The factor (F)VIII K1693N mutation (FVIII-Nara) in a patient with moderate hemophilia A confers resistance to thrombin-catalyzed cleavage at Arg1689 involving P4ʹ position

中等型血友病A患者中的因子(F)Ⅷ K1693N突变(FVIII-Nara)导致其对凝血酶催化的Arg1689裂解(涉及P4'位点)产生抵抗

2025-05-130
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