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收藏Reduced Doses of Factor Concentrates and Bypassing Agents to Treat Breakthrough Bleeds in Patients with Hemophilia A and B on Fitusiran Antithrombin-Based Dosing Regimen: ATLAS-OLE降低因子浓缩物和旁路剂的剂量以治疗接受Fitusiran抗凝血酶基础剂量方案的患者中血友病A和B的突破性出血:ATLAS-OLE
Pipe, Steven W.; Kavakli, Kaan; Matsushita, Tadashi; Tran, Huyen; Zulfikar, Bulent; Menapace, Laurel; Puurunen, Marja; Hu, Wenruo; Shen, Yuqian; Kaddi, Chanchala; Salinas, Vanessa
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收藏Retrospective analysis of hemophilia B in Turkey: identifying main characteristics and treatment options
Zulfikar, Bulent; Koc, Basak; Sahin, Fahri; Sasmaz, Hatice Ilgen; Kavakli, Kaan; Balkan, Can; Antmen, Ali Buelent; Akbayram, Sinan; Guvenc, Birol; Okan, Vahap; Turkkan, Emine; Albayrak, Canan; Albayrak, Davut; Sarper, Nazan; Celkan, Tuelin Tiraje; Ayyildiz, Orhan; Aksu, Salih; Patiroglu, Tuerkan; Salcioglu, Zafer; Gunes, Adalet Meral; Torun, Yasemin Altuner; Caliskan, Umran; Tokgoz, Huseyin; Ay, Yilmaz; Ozdemir, Gul Nihal; Sonmez, Mehmet; Unal, Ekrem; Oner, Ahmet Fayik; Guler, Nil; Kupesiz, Osman Alphan; Oren, Hale; Karaman, Serap; Unuvar, Ayegul; Dagli, Mehmet; Demir, Ahmet Muzaffer; Soker, Murat; Alioglu, Buelent; Kaya, Zuehre; Ayhan, Aylin Canbolat; Bicakci, Zafer; Aral, Yusuf Ziya; Ar, Muhlis Cem
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收藏Efanesoctocog Alfa Prophylaxis for Children with Severe Hemophilia A
Malec, Lynn; Peyvandi, Flora; Chan, Anthony K. C.; Koenigs, Christoph; Zulfikar, Bulent; Yuan, Huixing; Simpson, Mindy; Roman, Maria Teresa Alvarez; Carcao, Manuel; Staber, Janice M.; Dunn, Amy L.; Chou, Sheng-Chieh; d'Oiron, Roseline; Albisetti, Manuela; Demissie, Marek; Santagostino, Elena; Yarramaneni, Abhimanyu; Wong, Nancy; Abad-Franch, Lydia; Gunawardena, Sriya; Fijnvandraat, Karin
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收藏Concizumab prophylaxis in persons with hemophilia A or B with inhibitors: patient-reported outcome results from the phase 3 explorer7 study
Tran, Huyen; von Mackensen, Sylvia; Abraham, Aby; Castaman, Giancarlo; Hampton, Kingsley; Knoebl, Paul; Linari, Silvia; Odgaard-Jensen, Jan; Neergaard, Jesper Skov; Stasyshyn, Oleksandra; Zaw, Jay Jay Thaung; Zulfikar, Bulent; Shapiro, Amy
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收藏Phase 3 Trial of Concizumab in Hemophilia with Inhibitors
Matsushita, Tadashi; Shapiro, Amy; Abraham, Aby; Angchaisuksiri, Pantep; Castaman, Giancarlo; Cepo, Katarina; d'Oiron, Roseline; Frei-Jones, Melissa; Goh, Ai-Sim; Haaning, Jesper; Jacobsen, Sanja Hald; Mahlangu, Johnny; Mathias, Mary; Nogami, Keiji; Rasmussen, Josephine Skovgaard; Stasyshyn, Oleksandra; Huyen Tran; Vilchevska, Kateryna; Villarreal Martinez, Laura; Windyga, Jerzy; You, Chur Woo; Zozulya, Nadezhda; Zulfikar, Bulent; Jimenez-Yuste, Victor
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收藏Gene therapy in haemophilia: literature review and regional perspectives for Turkey
Kavakli, Kaan; Antmen, Bulent; Okan, Vahap; Sahin, Fahri; Aytac, Selin; Balkan, Can; Berber, Ergul; Kaya, Zuhre; Kupesiz, Alphan; Zulfikar, Bulent
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收藏Long-term safety and efficacy results from the phase 3b, open-label, multicentre Continuation study of rurioctocog alfa pegol for prophylaxis in previously treated patients with severe haemophilia ARuriocog alfa pegol用于先前治疗的严重血友病A患者预防的3b期,开放标签,多中心持续研究的长期安全性和有效性结果
Chowdary, Pratima; Mullins, Eric S.; Konkle, Barbara A.; McGuinn, Catherine; Park, Young Shil; Stasyshyn, Oleksandra; Zulfikar, Bulent; Engl, Werner; Tangada, Srilatha
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收藏A Randomized Trial of Factor VIII and Neutralizing Antibodies in Hemophilia A
Peyvandi, F.; Mannucci, P. M.; Garagiola, I.; El-Beshlawy, A.; Elalfy, M.; Ramanan, V.; Eshghi, P.; Hanagavadi, S.; Varadarajan, R.; Karimi, M.; Manglani, M. V.; Ross, C.; Young, G.; Seth, T.; Apte, S.; Nayak, D. M.; Santagostino, E.; Mancuso, M. E.; Sandoval Gonzalez, A. C.; Mahlangu, J. N.; Bonanad Boix, S.; Cerqueira, M.; Ewing, N. P.; Male, C.; Owaidah, T.; Soto Arellano, V.; Kobrinsky, N. L.; Majumdar, S.; Perez Garrido, R.; Sachdeva, A.; Simpson, M.; Thomas, M.; Zanon, E.; Antmen, B.; Kavakli, K.; Manco-Johnson, M. J.; Martinez, M.; Marzouka, E.; Mazzucconi, M. G.; Neme, D.; Palomo Bravo, A.; Paredes Aguilera, R.; Prezotti, A.; Schmitt, K.; Wicklund, B. M.; Zulfikar, B.; Rosendaal, F. R.
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