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C

Cary O. Harding

Oregon Health & Science University

43H指数
195论文数
5.9K被引数
收录论文 70
发表时间
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A brief history of gene therapy for ornithine transcarbamylase deficiency鸟氨酸转氨甲酰酶缺乏症的基因治疗简史
errMolecular Genetics and Metabolism
IF3.5
err2026-09-06
err0
PREAI
errMargo Sheck Breilyn; Laura L. Konczal; Cary O. Harding
err分享
err收藏
Advancing variant-agnostic liver-directed gene editing using homology-independent targeted integration利用同源非依赖靶向整合推进不区分变体的肝脏导向基因编辑
errMolecular Therapy
IF12
err2026-08-28
err0
PREAI
errMichael A. Martinez; Cary O. Harding
err分享
err收藏
Enhancement of Therapeutic Transgene Insertion for Treatment of Murine Phenylketonuria增强治疗性转基因插入以治疗小鼠苯丙酮尿症
errMolecular Therapy Nucleic Acids
IF6.1
err2025-12-26
err0
errOAAI
errMichael A. Martinez; Daelyn Y. Richards; Shelley R. Winn; Adrian M. Baris; Anne Vonada; Laura Harper; Cary O. Harding
err分享
err收藏
Measuring dietary intake among participants with a urea cycle disorder using standard diet records or a novel food photography app使用标准膳食记录或一种新型食品摄影应用程序测量尿素循环障碍患者中的膳食摄入量
errMolecular Genetics and Metabolism
IF3.5
err2025-11-12
err0
PREAI
errElaine Sim; Ashley Gregor; Erin Macleod; Rachel Moore; Michele N. Ravelli; Dale Schoeller; Cary O. Harding; Peter Jacobs; Melanie B. Gillingham
err分享
err收藏
D-BHB supplementation before moderate-intensity exercise suppresses lipolysis and selectively blunts exercise-induced long-chain acylcarnitine increase in pilot study of patients with long-chain fatty acid oxidation disorders
errMOLECULAR GENETICS AND METABOLISM
IF3.5
err2025-02-01
err0
PREAI
errGregor, Ashley N.; Delerive, Philippe; Cuenoud, Bernard; Monnard, Irina; Redeuil, Karine; Harding, Cary O.; Gillingham, Melanie B.
err分享
err收藏
Phenylketonuria in adults: we know plenty, but there is much more to learn
errAMERICAN JOURNAL OF CLINICAL NUTRITION
IF6.9
err2025-01-01
err0
PREAI
errHarding, Cary O.; Arnold, Georgianne; Berry, Gerard; Christ, Shawn E.; Grange, Dorothy K.; Jurecki, Elaina; Levy, Harvey; Lichter-Konecki, Uta; Longo, Nicola; Mcnutt, Markey; Meachum, Page; Sacharow, Stephanie; Shayota, Brian; Thomas, Janet; Vucko, Erika
err分享
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iPSC-Derived LCHADD Retinal Pigment Epithelial Cells Are Susceptible to Lipid Peroxidation and Rescued by Transfection of a Wildtype AAV-HADHA Vector
errINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE
IF4.7
err2024-09-16
err0
errOAAI
errDevine, Tiffany; Elizondo, Gabriela; Gaston, Garen; Babcock, Shannon J.; Matern, Dietrich; Shchepinov, Mikhail S.; Pennesi, Mark E.; Harding, Cary O.; Gillingham, Melanie B.
err分享
err收藏
Letter to the editor
errHUMAN GENETICS AND GENOMICS ADVANCES
IF3.6
err2024-07-01
err0
errOAAI
errHarding, Cary O.; Martinez, Michael
err分享
err收藏
JNT-517, a first-in-class SLC6A19 inhibitor for the treatment of phenylketonuria, enhances urinary excretion of phenylalanine in healthy volunteers
errMOLECULAR GENETICS AND METABOLISM
IF3.5
err2024-04-01
err0
PREAI
errViader, Andreu; Throup, John; Wobst, Heike; Blanchette, Heather; Nix, Darrell; Pullen, Nicholas; Brown, Dean; Barrish, Joel; Vaughn, Tobias; Weng, Haoling; Longo, Nicola; Harding, Cary
err分享
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Evaluating change in diet with pegvaliase treatment in adults with phenylketonuria: Analysis of phase 3 clinical trial data
errMOLECULAR GENETICS AND METABOLISM
IF3.5
err2024-03-01
err9
errOAAI
errRohr, Fran; Burton, Barbara; Dee, Anne; Harding, Cary O.; Lilienstein, Joshua; Lindstrom, Kristin; Macleod, Erin; Rose, Sarah; Singh, Rani; van Calcar, Sandra; Whitehall, Kaleigh
err分享
err收藏
Long-term comparative effectiveness of pegvaliase versus medical nutrition therapy with and without sapropterin in adults with phenylketonuria
errMOLECULAR GENETICS AND METABOLISM
IF3.5
err2024-01-01
err4
errOAAI
errBurton, Barbara K.; Clague, Gillian E.; Harding, Cary O.; Kucuksayrac, Ece; Levy, Drew G.; Lindstrom, Kristin; Longo, Nicola; Maillot, Francois; Muntau, Ania C.; Rutsch, Frank; Zori, Roberto T.
err分享
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Complete correction of murine phenylketonuria by selection-enhanced hepatocyte transplantation
errHEPATOLOGY
IF15.8
err2023-10-12
err3
errOAAI
errVonada, Anne; Wakefield, Leslie; Martinez, Michael; Harding, Cary O.; Grompe, Markus; Tiyaboonchai, Amita
err分享
err收藏
Efficacy and safety of a synthetic biotic for treatment of phenylketonuria: a phase 2 clinical trial
errNATURE METABOLISM
IF20.8
err2023-09-28
err15
PREAI
errVockley, Jerry; Sondheimer, Neal; Puurunen, Marja; Diaz, George A.; Ginevic, Ilona; Grange, Dorothy K.; Harding, Cary; Northrup, Hope; Phillips III, John A.; Searle, Shawn; Thomas, Janet A.; Zori, Roberto; Denney, William S.; Ernst, Sharon L.; Humphreys, Kristina; McWhorter, Nicole; Kurtz, Caroline; Brennan, Aoife M.
err分享
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ACMG STATEMENT Contributions from medical geneticists in clinical trials of genetic therapies: A points to consider statement of the American College of Medical Genetics and Genomics (ACMG)
errGENETICS IN MEDICINE
IF6.2
err2023-06-01
err1
errOAAI
errPena, Loren D. M.; Burrage, Lindsay C.; Enns, Gregory M.; Esplin, Edward D.; Harding, Cary; Mendell, Jerry R.; Niu, Zhiyv (Neal); Scharfe, Curt; Yu, Timothy; Koeberl, Dwight D.
err分享
err收藏
Resting and total energy expenditure of patients with long-chain fatty acid oxidation disorders (LC-FAODs)
errMOLECULAR GENETICS AND METABOLISM
IF3.5
err2023-03-01
err3
PREAI
errDeLany, James P.; Horgan, Angela; Gregor, Ashley; Vockley, Jerry; Harding, Cary O.; Gillingham, Melanie B.
err分享
err收藏
Biochemical and behavioural profile of NTBC treated Tyrosinemie type 1 mice
errMOLECULAR GENETICS AND METABOLISM
IF3.5
err2022-09-01
err1
errOAAI
errvan Ginkel, Willem G.; Winn, Shelley R.; Dudley, Sandra; Krenik, Destine; Perez, Ruby; Rimann, Nicole; Thony, Beat; Raber, Jacob; Harding, Cary O.
err分享
err收藏
Management of early treated adolescents and young adults with phenylketonuria: Development of international consensus recommendations using a modified Delphi approach
errMOLECULAR GENETICS AND METABOLISM
IF3.5
err2022-09-01
err11
errOAAI
errBurton, Barbara K.; Hermida, Alvaro; Belanger-Quintana, Amaya; Bell, Heather; Bjoraker, Kendra J.; Christ, Shawn E.; Grant, Mitzie L.; Harding, Cary O.; Huijbregts, Stephan C. J.; Longo, Nicola; McNutt, Markey C. I. I. I. I.; Nguyen-Driver, Mina D.; Pessoa, Andre L. Santos; Rocha, Julio Cesar; Sacharow, Stephanie; Sanchez-Valle, Amarilis; Sivri, H. Serap; Vockley, Jerry; Walterfang, Mark; Whittle, Sarah; Muntau, Ania C.
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Modeling the cognitive effects of diet discontinuation in adults with phenylketonuria (PKU) using pegvaliase therapy in PAH-deficient mice
errMOLECULAR GENETICS AND METABOLISM
IF3.5
err2022-05-01
err4
errOAAI
errWinn, Shelley R.; Dudley, Sandra; Scherer, Tanja; Rimann, Nicole; Thoeny, Beat; Boutros, Sydney; Krenik, Destine; Raber, Jacob; Harding, Cary O.
err分享
err收藏
Therapeutic liver repopulation by transient acetaminophen selection of gene-modified hepatocytes
errSCIENCE TRANSLATIONAL MEDICINE
IF14.6
err2021-06-09
err16
errOAAI
errVonada, Anne; Tiyaboonchai, Amita; Nygaard, Sean; Posey, Jeffrey; Peters, Alexander Mack; Winn, Shelley R.; Cantore, Alessio; Naldini, Luigi; Harding, Cary O.; Grompe, Markus
err分享
err收藏
Pharmacokinetic, pharmacodynamic, and immunogenic rationale for optimal dosing of pegvaliase, a PEGylated bacterial enzyme, in adult patients with phenylketonuria
errCTS-CLINICAL AND TRANSLATIONAL SCIENCE
IF2.8
err2021-05-31
err10
errOAAI
errQi, Yulan; Patel, Gina; Henshaw, Joshua; Gupta, Soumi; Olbertz, Joy; Larimore, Kevin; Harding, Cary O.; Merilainen, Markus; Zori, Roberto; Longo, Nicola; Burton, Barbara K.; Li, Mingjin; Gu, Zhonghua; Zoog, Stephen J.; Weng, Haoling H.; Schweighardt, Becky
err分享
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研究方向

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