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Terence R. Flotte

university of massachusetts system

82H指数
428论文数
2.2W被引数
收录论文 144
发表时间
Response to the FDA’s proposed pathway for individualized genetic therapies对FDA提出的个性化基因疗法路径的回应
err2025-12-29
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PREAI
errTimothy W. Yu; Julia Vitarello; Kiran Musunuru; Rebecca C. Ahrens-Nicklas; David R. Liu; Michelle L. Mellion; Fyodor Urnov; Winston Yan; Srinivas Chunduru; David Barrett; Terence R. Flotte; Janet Woodcock
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A Compact Base Editor Rescues AATD-associated Liver and Lung Disease in Mouse Models一种紧凑型碱基编辑器挽救了AATD相关的小鼠肝脏和肺部疾病模型
err2025-08-28
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errOAAI
errnull Jenny Gao; Nathan Bamidele; Debora Pires-Ferreira; Chunwei Zheng; April Destefano; Haoyang Cheng; Qiushi Tang; Yueying Cao; Jun Xie; Guangping Gao; Alisha Gruntman; Erik Sontheimer; Terence R. Flotte; Wen Xue
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In memoriam: Kenneth I. Berns, MD, PhD (1938-2024)
err2024-04-01
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errOAAI
errByrne, Barry J.; Flotte, Terence R.; Herzog, Roland W.; Srivastava, Arun
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Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy杜氏肌营养不良症患者接受大剂量rAAV9基因治疗后死亡
err2023-09-28
err92
errOAAI
errLek, Angela; Wong, Brenda; Keeler, Allison; Blackwood, Meghan; Ma, Kaiyue; Huang, Shushu; Sylvia, Katelyn; Batista, A. Rita; Artinian, Rebecca; Kokoski, Danielle; Parajuli, Shestruma; Putra, Juan; Carreon, C. Katte; Lidov, Hart; Woodman, Keryn; Pajusalu, Sander; Spinazzola, Janelle M.; Gallagher, Thomas; Larovere, Joan; Balderson, Diane; Black, Lauren; Sutton, Keith; Horgan, Richard; Lek, Monkol; Flotte, Terence
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Gene therapy for alpha-1 antitrypsin deficiency: an update
err2023-03-02
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errOAAI
errFerreira, Debora Pires; Gruntman, Alisha M.; Flotte, Terence R.
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Immunogenicity of Recombinant Adeno-Associated Virus (AAV) Vectors for Gene Transfer重组腺相关病毒 (AAV) 基因转移载体的免疫原性
err2023-03-02
err63
errOAAI
errArjomandnejad, Motahareh; Dasgupta, Ishani; Flotte, Terence R.; Keeler, Allison M.
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Nicholas Muzyczka, PhD
err2023-03-01
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errOAAI
errBerns, Kenneth I.; Byrne, Barry J.; Flotte, Terence R.; Samulski, R. Jude; Srivastava, Arun
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Gene-based therapeutics for rare genetic neurodevelopmental psychiatric disorders
err2022-07-01
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errOAAI
errDavidson, Beverly L.; Gao, Guangping; Berry-Kravis, Elizabeth; Bradbury, Allison M.; Bonnemann, Carsten; Buxbaum, Joseph D.; Corcoran, Gavin R.; Gray, Steven J.; Gray-Edwards, Heather; Kleiman, Robin J.; Shaywitz, Adam J.; Wang, Dan; Zoghbi, Huda Y.; Flotte, Terence R.; Tauscher-Wisniewski, Sitra; Tifft, Cynthia J.; Sahin, Mustafa
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Gene Therapy for Rare Neurological Disorders
err2022-02-25
err11
PREAI
errFlotte, Terence R.; Gessler, Dominic J.
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AAV gene therapy for Tay-Sachs disease
err2022-02-10
err67
errOAAI
errFlotte, Terence R.; Cataltepe, Oguz; Puri, Ajit; Batista, Ana Rita; Moser, Richard; McKenna-Yasek, Diane; Douthwright, Catherine; Gernoux, Gwladys; Blackwood, Meghan; Mueller, Christian; Tai, Phillip W. L.; Jiang, Xuntian; Bateman, Scot; Spanakis, Spiro G.; Parzych, Julia; Keeler, Allison M.; Abayazeed, Aly; Rohatgi, Saurabh; Gibson, Laura; Finberg, Robert; Barton, Bruce A.; Vardar, Zeynep; Shazeeb, Mohammed Salman; Gounis, Matthew; Tifft, Cynthia J.; Eichler, Florian S.; Brown, Robert H., Jr.; Martin, Douglas R.; Gray-Edwards, Heather L.; Sena-Esteves, Miguel
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Supporting Families Considering Participation in a Clinical Trial: Parent-Provider Perspectives
err2021-05-01
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errOAAI
errFlotte, Terence R.; Lord, Blyth Taylor; Siedman, Jennifer
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