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Nih National Center for Advancing Translational Sciences (Ncats)

Scholars893
Papers500
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Related Papers (499)
Publication Date
Generation and characterization of induced pluripotent stem cell (iPSC) lines from patients affected with Tay-Sachs and Sandhoff disease
err2026-04-01
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PREAI
errJovanovic, Vukasin M.; Chen, Catherine Z.; Toro, Camilo; Hurd, Kerstin A.; Zou, Jizhong; Tifft, Cynthia J.; Zheng, Wei; Henderson, Mark J.; Marugan, Juan; Tristan, Carlos A.
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Development of Scalable and Commercial Synthesis for GS-441524
err2026-03-01
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PREAI
errGajula, Praveen; Vasilev, Maksim; Li, Jiezhen; Gangu, Aravind S.; Lee, Daniel; Tung, Hsien-Hsin; Mamunooru, Manasa; Wang, Zhirui; Chen, Anji; Rana, Jagruti; Yin, Jinya; Regati, Sridhar; Karmakar, Anupam; Ghosh, Angshuman; Chatterjee, Subhadeep; Yadaw, Ajay K.; Roy, Subho; Bandu, Raju; Dissanayake, Kumuduni; Bietsch, Jonathan; Wannere, Chaitanya; Krishnamurthy, Dhileepkumar; Sirasani, Gopal; Achanta, Srinivas; Armstrong III, Joseph D.; Huang, Junfeng; Sanderson, Philip E.; Qu, Bo; Senanayake, Chris H.
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Integrating qHTS and QSAR Models to Identify Safe GPCR-Targeted Compounds: A Focus on hERG-Dependent Cardiotoxicity
err2026-02-01
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PREAI
errLuo, Xi; Zhao, Jinghua; Sakamuru, Srilatha; Xia, Menghang; Xu, Tuan; Travers, Jameson; Klumpp-Thomas, Carleen; Zhu, Hu; Hall, Matthew D.; Ferguson, Stephen S.; Reif, David M.; Huang, Ruili
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Generation and characterization of POMC-tdTomato reporter human pluripotent stem cell lines
err2026-01-01
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errOAAI
errJovanovic, Vukasin M.; Rausch, Rick; Derosa, Maria Caterina; Castellano, David; Mckee, Cody; Sen, Chaitali; Daly, Fiona; Doege, Claudia A.; Tristan, Carlos A.
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CURE ID: A Platform to Collect Real-World Treatment Data for Drug Repurposing in Rare Genetic Disorders
err2026-01-01
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errFarid, Tahsin; Ruzhnikov, Maura R. Z.; Duggal, Mili; Tumas, Keyla C.; Strongin, Shira; Sid, Eric; Fuchs, Sarah R.; Sacks, Leonard; Pichard, Dominique C.; Pilgrim-Grayson, Catherine; Mathe, Ewy A.; Stone, Heather A.
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The Race to Salvage Glucocerebrosidase: Understanding Small-Molecule Therapies for GBA1-Associated Parkinsonism
err2025-12-01
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errHenderson, Mark J.; Chen, Tiffany C.; Glasstetter, Logan M.; Chen, Yu; Marugan, Juan J.; Sidransky, Ellen
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Investigating the HIV epidemic among Black gay and bisexual men in the Southern United States: Results of the HPTN 096 pilot cross-sectional assessment
err2025-10-17
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PREAI
errBeyrer, Chris; Remien, Robert H.; Eshleman, Susan H.; Gamble, Theresa R.; De Dieu Tapsoba, Jean; Labbett, Rita L.; Sullivan, Philip A.; Laeyendecker, Oliver; Anderson, Peter L.; Agravat, Devang; Hughes, James P.; Driffin, Daniel D.; Hutchinson, Craig S.; Hucks-Ortiz, Christopher; Adair, Maurice; Curry, Melissa; Jones, Shakita Brooks; Haddock, Ian L.; Boyd, Donte; Burwen, Dale R.; Johnson, Anna Satcher; Nelson, LaRon E.
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metLinkR: Facilitating Metaanalysis of Human Metabolomics Data through Automated Linking of Metabolite Identifiers
err2025-04-01
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errPatt, Andrew; Pang, Iris; Lee, Fred; Gohel, Chiraag; Fahy, Eoin; Stevens, Vicki; Ruggieri, David; Moore, Steven C.; Mathe, Ewy A.
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A global survey about undiagnosed rare diseases: perspectives, challenges, and solutions
err2025-02-26
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errOAAI
errBaldovino, Simone; Sciascia, Savino; Carta, Claudio; Salvatore, Marco; Cellai, Laura L.; Ferrari, Gianluca; Lumaka, Aime; Groft, Stephen; Alanay, Yasemin; Azam, Maleeha; Baynam, Gareth; Cederroth, Helene; la Paz, Eva Maria Cutiongco-de; Dissanayake, Vajira Harshadeva Weerabaddana; Giugliani, Roberto; Gonzaga-Jauregui, Claudia; Hettiarachchi, Dineshani; Kvlividze, Oleg; Landoure, Guida; Makay, Prince; Melegh, Bela; Ozbek, Ugur; Pagava, Karaman; Puri, Ratna Dua; Romero, Vaness I.; Scaria, Vinod; Jamuar, Saumya S.; Shotelersuk, Vorasuk; Roccatello, Dario; Gahl, William A.; Wiafe, Samuel A.; Bodamer, Olaf; Posada, Manuel; Taruscio, Domenica
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Lessons learned from evaluating defined chemical mixtures in a high-throughput estrogen receptor assay system
err2025-02-20
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PREAI
errParham, Fred; Eccles, Kristin M.; Rider, Cynthia, V; Sakamuru, Srilatha; Xia, Menghang; Huang, Ruili; Tice, Raymond R.; Dinse, Gregg E.; Devito, Michael J.
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Borrelial phosphomannose isomerase as a cell surface localized protein that retains enzymatic activity and promotes host-pathogen interaction
errMBIO
IF4.7
err2025-02-11
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errDutta, Shraboni; Rana, Vipin S.; Backstedt, Brian T.; Shakya, Anil K.; Kitsou, Chrysoula; Yas, Ozlem B.; Smith, Alexis A.; Ronzetti, Michael H.; Lipman, Rachel M.; Araujo-Aris, Sarai; Yang, Xiuli; Rai, Ganesha; Lin, Yi-Pin; Herzberg, Osnat; Pal, Utpal
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Active- and Allosteric-Site Cyclic Peptide Inhibitors of Secreted M. tuberculosis Chorismate Mutase
err2025-02-04
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PREAI
errvan Neer, Renier H. P.; Dranchak, Patricia K.; Aitha, Mahesh; Liu, Lijun; Carlson, Emma K.; Jacobsen, Isabella E.; Battaile, Kevin; Fang, Yuhong; Tao, Dingyin; Rai, Ganesha; Padia, Janak; Lovell, Scott; Suga, Hiroaki; Inglese, James
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Genetic Variants of GBP4: Reduced Risks for Drug-Induced Acute Liver Failure in Non-Finnish European Population
err2025-01-27
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PREAI
errLiao, Tsung-Jen; Xia, Menghang; Hayashi, Paul; Pan, Bohun; Aithal, Guruprasad P.; Lucena, M. Isabel; Andrade, Raul J.; Rule, Jody A.; Lee, William M.; Rakela, Jorge; Huang, Ruili; Chen, Minjun
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Repurposing of lonafarnib as a treatment for SARS-CoV-2 infection
err2025-01-09
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errOAAI
errKhan, Mohsin; Irvin, Parker; Park, Seung Bum; Ivester, Hannah M.; Ricardo-Lax, Inna; Leek, Madeleine; Grieshaber, Ailis; Jang, Eun Sun; Coutermarsh-Ott, Sheryl; Zhang, Qi; Maio, Nunziata; Jiang, Jian-Kang; Li, Bing; Huang, Wenwei; Wang, Amy Q.; Xu, Xin; Hu, Zongyi; Zheng, Wei; Ye, Yihong; Rouault, Tracey; Rice, Charles; Allen, Irving C.; Liang, T. Jake
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Development of immunocompetent full thickness skin tissue constructs to model skin fibrosis for high-throughput drug screening
err2024-12-13
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PREAI
errLim, Yi Wei; Quinn, Russell; Bharti, Kapil; Ferrer, Marc; Zarkoob, Hoda; Song, Min Jae
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Therapeutic development approaches to treat haploinsufficiency diseases: restoring protein levels
err2024-12-01
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errOAAI
errEvans, Elena F.; Shyr, Zeenat A.; Traynor, Bryan J.; Zheng, Wei
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Multi- Component, Time- Course screening to develop combination cancer therapies based on synergistic toxicity
err2024-11-25
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PREAI
errCeribelli, Michele; Tosto, Frances Anne; Zhang, Xiaohu; Melani, Christopher J.; Roschewski, Mark; Beck, Erin; Thomas, Carleen Klumpp -; Peer, Cody J.; Wilson, Kelli M.; Chen, Lu; Mcknight, Crystal; Michael, Sam; Itkin, Zina; Shinn, Paul; Figg Sr, William D.; Wilson, Wyndham H.; Staudt, Louis M.; Thomas, Craig J.
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JAHA at Scientific Sessions 2023: Moving Toward Social Justice in Cardiovascular Health in the United States
err2024-11-19
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errOAAI
errBaker-Smith, Carissa M.; Waddy, Salina P.; Hassani, Sara; Mujahid, Mahasin; Okwuosa, Tochi; Peprah, Emmanuel; Boden-Albala, Bernadette
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The state-of-the-art of N-of-1 therapies and the IRDiRC N-of-1 development roadmap
err2024-11-04
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PREAI
errJonker, Anneliene H.; Tataru, Elena-Alexandra; Graessner, Holm; Dimmock, David; Jaffe, Adam; Baynam, Gareth; Davies, James; Mitkus, Shruti; Iliach, Oxana; Horgan, Rich; Augustine, Erika F.; Bateman-House, Alison; Pasmooij, Anna Maria Gerdina; Yu, Tim; Synofzik, Matthis; Douville, Julie; Lapteva, Larissa; Brooks, Philip John; O'Connor, Daniel; Aartsma-Rus, Annemieke
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Discovery of IRAK1/4/pan-FLT3 Kinase Inhibitors as Treatments for Acute Myeloid Leukemia
err2024-10-23
err1
errOAAI
errHoyt, Scott B.; Finocchio, Chris J.; Croll, Elizabeth; Tawa, Gregory J.; Li, Huixu; Ma, Li; Li, Kaikai; Liu, Li; Li, Ranran; Zhang, Xiaohu; Wilson, Kelli; Xu, Xin; Shah, Pranav; Williams, Jordan; Fang, Yuhong; Bolanos, Lyndsey C.; Gracia-Maldonado, Gabriel; Kolt, Amal; Robinson, Christina; Free, Jessica; Edmondson, Elijah F.; Difilippantonio, Simone; Jones, LaQuita M.; Culver-Cochran, Ashley E.; Rosenbaum, Jan S.; Starczynowski, Daniel T.; Thomas, Craig J.
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