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Marco A. Ciufolini

nanovation therapeutics

51H-index
309Paper Count
9.9KCitation Count
Published Papers 85
Publication Date
Design and development of lipid nanoparticle formulations for brain gene therapy
err2026-07-20
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errOAAI
errSarah B. Thomson; Alissandra de Moura Gomes; Pardis Kazemian; Daniel Z. Kurek; Jayesh A. Kulkarni; Fariba Sadaati; Pamela K. Wagner; Terri L. Petkau; Marco A. Ciufolini; Pieter R. Cullis; Blair R. Leavitt
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Design of Cationic Ionizable Lipids for the Delivery of Therapeutic Nucleic Acids
err2025-09-02
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errOAAI
errN. D. Prasad Atmuri; Fariba Saadati; Jayesh Kulkarni; Dominik Witzigmann; Pieter R. Cullis; Marco A. Ciufolini
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An Improved Synthesis of Ionizable Lipids D-Lin-KC2-DMA and D-Lin-MC3-DMA
err2025-09-01
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errOAAI
errNabi, Ardalan; Tran, Huy; Saadati, Fariba; Prasad Atmuri, Nagavenkata Durga; Dake, Gregory; Ciufolini, Marco A.
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Chemical optimization and derivatization of micrococcin p2 to target multiple bacterial infections: new antibiotics from thiopeptides
err2024-08-20
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PREAI
errPark, Jiyun; Kim, Dahyun; Son, Young-Jin; Ciufolini, Marco A.; Clovis, Shyaka; Han, Minwoo; Kim, Lee-Han; Shin, Sung Jae; Hwang, Hee-Jong
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Claisen Self-Condensation of Lactones in the Synthesis of Ionizable Lipids
err2024-08-13
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PREAI
errNabi, Ardalan; Atmuri, N. D. Prasad; Arnold, Deaglan; Saadati, Fariba; Tran, Huy; Adak, Taniya; Dake, Gregory R.; Ciufolini, Marco A.
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Losartan and metabolite EXP3179 activate endothelial function without lowering blood pressure in AT2 receptor KO mice
err2024-08-01
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PREAI
errSauge, Elodie; White, Zoe; Lizotte, Farah; Yuen, Christopher; Atmuri, N. D. Prasad; Ciufolini, Marco A.; Geraldes, Pedro; Bernatchez, Pascal
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Quantitative Visualization of Lipid Nanoparticle Fusion as a Function of Formulation and Process Parameters
err2024-07-05
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PREAI
errKamanzi, Albert; Zhang, Yao; Gu, Yifei; Liu, Faith; Berti, Romain; Wang, Benjamin; Saadati, Fariba; Ciufolini, Marco A.; Kulkarni, Jayesh; Cullis, Pieter; Leslie, Sabrina
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Therapies from Thiopeptides
err2023-11-14
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errOAAI
errHwang, Hee-Jong; Ciufolini, Marco A.
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Identification of Micrococcin P2-Derivatives as Antibiotic Candidates against Two Gram-Positive Pathogens
err2023-10-05
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PREAI
errKim, Dahyun; Lee, Jusuk; Shyaka, Clovis; Kwak, Jin-Hwan; Pai, Hyunjoo; Rho, Mina; Ciufolini, Marco A.; Han, Minwoo; Park, Jong-Hwan; Kim, Young-Rok; Jung, Sungji; Jang, Ah-Ra; Kim, Eunjung; Lee, Jee-Young; Lee, Hakyeong; Son, Young-Jin; Hwang, Hee-Jong
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From a drug repositioning to a structure-based drug design approach to tackle acute lymphoblastic leukemia
err2023-05-29
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errOAAI
errSaez-Ayala, Magali; Hoffer, Laurent; Abel, Sebastien; Ben Yaala, Khaoula; Sicard, Benoit; Andrieu, Guillaume P.; Latiri, Mehdi; Davison, Emma K.; Ciufolini, Marco A.; Bremond, Paul; Rebuffet, Etienne; Roche, Philippe; Derviaux, Carine; Voisset, Edwige; Montersino, Camille; Castellano, Remy; Collette, Yves; Asnafi, Vahid; Betzi, Stephane; Dubreuil, Patrice; Combes, Sebastien; Morelli, Xavier
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Losartan metabolite EXP3179 is a unique blood pressure-lowering AT1R antagonist with direct, rapid endothelium-dependent vasoactive properties
err2022-12-01
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PREAI
errSauge, Elodie; Pechkovsky, Dmitri; Atmuri, N. D. Prasad; Tehrani, Arash Y.; White, Zoe; Dong, Ying; Cait, Jessica; Hughes, Michael; Tam, Anthony; Donen, Graham; Yuen, Christopher; Walker, Michael J. A.; McNagny, Kelly M.; Sin, Don D.; Ciufolini, Marco A.; Bernatchez, Pascal
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Micrococcin P2 Targets Clostridioides difficile
err2022-07-11
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PREAI
errSon, Young-Jin; Kim, Young-Rok; Oh, Sang-Hun; Jung, Sungji; Ciufolini, Marco A.; Hwang, Hee-Jong; Kwak, Jin-Hwan; Pai, Hyunjoo
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A Route to Lipid ALC-0315: a Key Component of a COVID-19 mRNA Vaccine
err2022-07-04
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errOAAI
errSaadati, Fariba; Cammarone, Silvia; Ciufolini, Marco A.
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Nitro-Group-Containing Thiopeptide Derivatives as Promising Agents to Target Clostridioides difficile
err2022-05-19
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errOAAI
errKim, Dahyun; Kim, Young-Rok; Hwang, Hee-Jong; Ciufolini, Marco A.; Lee, Jusuk; Lee, Hakyeong; Clovis, Shyaka; Jung, Sungji; Oh, Sang-Hun; Son, Young-Jin; Kwak, Jin-Hwan
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Nitric oxide in the Marfan vasculature: Friend or foe?
err2021-11-01
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PREAI
errTehrani, Arash Y.; Ciufolini, Marco A.; Bernatchez, Pascal
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Modular Lipid Nanoparticle Platform Technology for siRNA and Lipophilic Prodrug Delivery
errSMALL
IF12.1
err2021-08-01
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errOAAI
errvan Der Meel, Roy; Chen, Sam; Zaifman, Josh; Kulkarni, Jayesh A.; Zhang, Xu Ran S.; Tam, Ying K.; Bally, Marcel B.; Schiffelers, Raymond M.; Ciufolini, Marco A.; Cullis, Pieter R.; Tam, Yuen Yi C.
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The Onpattro story and the clinical translation of nanomedicines containing nucleic acid-based drugs
err2019-12-04
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PREAI
errAkinc, Akin; Maier, Martin A.; Manoharan, Muthiah; Fitzgerald, Kevin; Jayaraman, Muthusamy; Barros, Scott; Ansell, Steven; Du, Xinyao; Hope, Michael J.; Madden, Thomas D.; Mui, Barbara L.; Semple, Sean C.; Tam, Ying K.; Ciufolini, Marco; Witzigmann, Dominik; Kulkarni, Jayesh A.; van der Meel, Roy; Cullis, Pieter R.
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Catalyst-Free Synthesis of Polysubstituted 5-Acylamino-1,3-Thiazoles via Hantzsch Cyclization of α-Chloroglycinates
err2019-10-25
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errOAAI
errTomassetti, Mara; Lupidi, Gabriele; Piermattei, Pamela; Rossi, Federico V.; Lillini, Samuele; Bianchini, Gianluca; Aramini, Andrea; Ciufolini, Marco A.; Marcantoni, Enrico
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